-
1
-
-
0035847075
-
Transgenic monkeys produced by retroviral gene transfer into mature oocytes
-
DOI 10.1126/science.291.5502.309
-
Chan, A. W., Chong, K. Y., Martinovich, C., Simerly, C. & Schatten, G. Transgenic monkeys produced by retroviral gene transfer into mature oocytes. Science 291, 309-312 (2001). (Pubitemid 32096317)
-
(2001)
Science
, vol.291
, Issue.5502
, pp. 309-312
-
-
Chan, A.W.S.1
Chong, K.Y.2
Martinovich, C.3
Simerly, C.4
Schatten, G.5
-
2
-
-
45149105779
-
Towards a transgenic model of Huntington's disease in a nonhuman primate
-
Yang, S. H. et al. Towards a transgenic model of Huntington's disease in a nonhuman primate. Nature 453, 921-924 (2008).
-
(2008)
Nature
, vol.453
, pp. 921-924
-
-
Yang, S.H.1
-
4
-
-
60149106907
-
Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes
-
Foust, K. D. et al. Intravascular AAV9 preferentially targets neonatal neurons and adult astrocytes. Nat Biotechnol 27, 59-65 (2009).
-
(2009)
Nat Biotechnol
, vol.27
, pp. 59-65
-
-
Foust, K.D.1
-
5
-
-
79961032418
-
Several rAAV vectors efficiently cross the blood-brain barrier and transduce neurons and astrocytes in the neonatal mouse central nervous system
-
Zhang, H. et al. Several rAAV vectors efficiently cross the blood-brain barrier and transduce neurons and astrocytes in the neonatal mouse central nervous system. Mol Ther 19, 1440-1448 (2011).
-
(2011)
Mol Ther
, vol.19
, pp. 1440-1448
-
-
Zhang, H.1
-
6
-
-
32944459983
-
Transduction characteristics of adeno-associated virus vectors expressing cap serotypes 7, 8, 9, and Rh10 in the mouse brain
-
DOI 10.1016/j.ymthe.2005.11.015, PII S1525001605017090
-
Cearley, C. N. & Wolfe, J. H. Transduction characteristics of adeno-associated virus vectors expressing cap serotypes 7, 8, 9, and Rh10 in the mouse brain. Mol Ther 13, 528-537 (2006). (Pubitemid 43257620)
-
(2006)
Molecular Therapy
, vol.13
, Issue.3
, pp. 528-537
-
-
Cearley, C.N.1
Wolfe, J.H.2
-
7
-
-
67649861393
-
Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons
-
Duque, S. et al. Intravenous administration of self-complementary AAV9 enables transgene delivery to adult motor neurons. Mol Ther 17, 1187-1196 (2009).
-
(2009)
Mol Ther
, vol.17
, pp. 1187-1196
-
-
Duque, S.1
-
8
-
-
77749249680
-
Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN
-
Foust, K. D. et al. Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN. Nat Biotechnol 28, 271-274 (2010).
-
(2010)
Nat Biotechnol
, vol.28
, pp. 271-274
-
-
Foust, K.D.1
-
9
-
-
78751700314
-
Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice
-
Dominguez, E. et al. Intravenous scAAV9 delivery of a codon-optimized SMN1 sequence rescues SMA mice. Hum Mol Genet 20, 681-693 (2011).
-
(2011)
Hum Mol Genet
, vol.20
, pp. 681-693
-
-
Dominguez, E.1
-
10
-
-
79955574241
-
Efficacy of a combined intracerebral and systemic gene delivery approach for the treatment of a severe lysosomal storage disorder
-
Spampanato, C. et al. Efficacy of a combined intracerebral and systemic gene delivery approach for the treatment of a severe lysosomal storage disorder. Mol Ther 19, 860-869 (2011).
-
(2011)
Mol Ther
, vol.19
, pp. 860-869
-
-
Spampanato, C.1
-
11
-
-
77953459529
-
Animal models for schizophrenia via in utero gene transfer: Understanding roles for genetic susceptibility factors in brain development
-
Kamiya, A. Animal models for schizophrenia via in utero gene transfer: understanding roles for genetic susceptibility factors in brain development. Prog Brain Res 179, 9-15 (2009).
-
(2009)
Prog Brain Res
, vol.179
, pp. 9-15
-
-
Kamiya, A.1
-
12
-
-
80053923197
-
Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to differential targeting of CNS cell types and extensive transduction of the nervous system
-
Rahim, A. A. et al. Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to differential targeting of CNS cell types and extensive transduction of the nervous system. FASEB J 25, 3505-3518 (2011).
-
(2011)
FASEB J
, vol.25
, pp. 3505-3518
-
-
Rahim, A.A.1
-
13
-
-
77649273563
-
Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB)
-
Gray, S. J. et al. Directed evolution of a novel adeno-associated virus (AAV) vector that crosses the seizure-compromised blood-brain barrier (BBB).Mol Ther 18, 570-578 (2010).
-
(2010)
Mol Ther
, vol.18
, pp. 570-578
-
-
Gray, S.J.1
-
14
-
-
32344438754
-
Directed evolution of adeno-associated virus yields enhanced gene delivery vectors
-
DOI 10.1038/nbt1182, PII NBT1182
-
Maheshri, N., Koerber, J. T., Kaspar, B. K. & Schaffer, D. V. Directed evolution of adeno-associated virus yields enhanced gene delivery vectors. Nat Biotechnol 24, 198-204 (2006). (Pubitemid 43221704)
-
(2006)
Nature Biotechnology
, vol.24
, Issue.2
, pp. 198-204
-
-
Maheshri, N.1
Koerber, J.T.2
Kaspar, B.K.3
Schaffer, D.V.4
-
15
-
-
78650753240
-
Inhibition of Ras-guanine nucleotide-releasing factor 1 (Ras-GRF1) signaling in the striatum reverts motor symptoms associated with L-dopa-induced dyskinesia
-
Fasano, S. et al. Inhibition of Ras-guanine nucleotide-releasing factor 1 (Ras-GRF1) signaling in the striatum reverts motor symptoms associated with L-dopa-induced dyskinesia. Proc Natl Acad Sci USA 107, 21824-21829 (2010).
-
(2010)
Proc Natl Acad Sci USA
, vol.107
, pp. 21824-21829
-
-
Fasano, S.1
|