Therapeutic applications of the PhiC31 integrase system

Current Gene Therapy

Volumn 11, Issue 5, 2011, Pages 375-381

  Chavez, Christopher L ^a   Calos, Michele P ^a  

^a STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Att site; Genetic disease; Genomic integration; Hemophilia; Induced pluripotent stem cells; Liver; Non viral; Phage; Serine recombinase; Site specific; Stem cells

Indexed keywords

INTEGRASE; PHIC31 INTEGRASE; UNCLASSIFIED DRUG;

ARTICLE; CELL BASED GENE THERAPY; DRUG EFFICACY; DRUG SAFETY; EX VIVO STUDY; GENOME; GENOTOXICITY; HEMOPHILIA B; HUMAN; HYDRODYNAMICS BASED TRANSFECTION; IN VIVO GENE TRANSFER; IN VIVO STUDY; LIVER CELL; NONHUMAN; PLURIPOTENT STEM CELL; STEM CELL GENE THERAPY; TARGET CELL;

MAMMALIA;

EID: 80053559028     PISSN: 15665232     EISSN: 18755631     Source Type: Journal    
DOI: 10.2174/156652311797415818     Document Type: Article

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