Using 5′-PTMs to repair mutant β-globin transcripts

RNA

Volumn 13, Issue 8, 2007, Pages 1317-1327

  Kierlin Duncan, Monique N ^a,b   Sullenger, Bruce A ^a,b  

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

^b DUKE UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Hemoglobinopathies; Trans splicing

Indexed keywords

BETA GLOBIN; RNA; GLOBIN; MESSENGER RNA;

5' PRE TRANS SPLICING MOLECULE; ARTICLE; BETA THALASSEMIA; CONTROLLED STUDY; EMBRYO; EXON; GENE MUTATION; HUMAN; HUMAN CELL; INTRON; MAMMAL CELL; MOLECULE; MUTANT; PRIORITY JOURNAL; RNA REPAIR; RNA SPLICING; RNA TRANSCRIPTION; SICKLE CELL ANEMIA; TRANS SPLICING; CELL LINE; GENETICS; METABOLISM; MUTATION; SPLICEOSOME;

MAMMALIA;

CELL LINE; EXONS; GLOBINS; HUMANS; INTRONS; MUTATION; RNA, MESSENGER; SPLICEOSOMES; TRANS-SPLICING;

EID: 34447542621     PISSN: 13558382     EISSN: 14699001     Source Type: Journal    
DOI: 10.1261/rna.525607     Document Type: Article

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