메뉴 건너뛰기




Volumn 19, Issue 6, 2005, Pages 840-847

Treatment of X-linked childhood cerebral adrenoleukodystrophy by the use of an allogeneic stem cell transplantation with reduced intensity conditioning regimen

Author keywords

Allogeneic stem cell transplantation; Hematopoietic stem cell transplantation; Non myeloablative; X linked childhood cerebral adrenoleukodystrophy

Indexed keywords

BUSULFAN; CYCLOSPORIN A; FLUDARABINE; GANCICLOVIR; LONG CHAIN FATTY ACID; RECOMBINANT GRANULOCYTE COLONY STIMULATING FACTOR; STEROID; THYMOCYTE ANTIBODY;

EID: 28644440640     PISSN: 09020063     EISSN: None     Source Type: Journal    
DOI: 10.1111/j.1399-0012.2005.00411.x     Document Type: Article
Times cited : (18)

References (28)
  • 1
    • 0027532282 scopus 로고
    • Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters
    • Moser J, Douar A-M, Sarde C-O et al. Putative X-linked adrenoleukodystrophy gene shares unexpected homology with ABC transporters. Nature 1993: 361: 726.
    • (1993) Nature , vol.361 , pp. 726
    • Moser, J.1    Douar, A.-M.2    Sarde, C.-O.3
  • 2
    • 0027933788 scopus 로고
    • Genomic organization of the adrenoleukodystrophy gene
    • Sarde C-O, Mosser J, Kioschis P et al. Genomic organization of the adrenoleukodystrophy gene. Genomics 1994: 22: 13.
    • (1994) Genomics , vol.22 , pp. 13
    • Sarde, C.-O.1    Mosser, J.2    Kioschis, P.3
  • 3
    • 0030860131 scopus 로고    scopus 로고
    • Adrenoleukodystrophy: Phenotype, genetics, pathogenesis and therapy
    • Moser HW. Adrenoleukodystrophy: phenotype, genetics, pathogenesis and therapy. Brain 1997: 120: 1485.
    • (1997) Brain , vol.120 , pp. 1485
    • Moser, H.W.1
  • 5
    • 0021211765 scopus 로고
    • Bone marrow transplant in adrenoleukodystrophy
    • Moser HW, Tutschka PJ, Brown FR III et al. Bone marrow transplant in adrenoleukodystrophy. Neurology 1984: 34: 1410.
    • (1984) Neurology , vol.34 , pp. 1410
    • Moser, H.W.1    Tutschka, P.J.2    Brown III, F.R.3
  • 6
    • 0032006125 scopus 로고    scopus 로고
    • Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases
    • Slavin S, Nagler A, Naparstek E et al. Nonmyeloablative stem cell transplantation and cell therapy as an alternative to conventional bone marrow transplantation with lethal cytoreduction for the treatment of malignant and nonmalignant hematologic diseases. Blood 1998: 91: 756.
    • (1998) Blood , vol.91 , pp. 756
    • Slavin, S.1    Nagler, A.2    Naparstek, E.3
  • 7
    • 0035382484 scopus 로고    scopus 로고
    • Non-myeloablative stem cell transplantation and donor lymphocyte infusion for the treatment of cancer and life-threatening non-malignant disorders
    • Slavin S, Nagler A, Aker M, Shapira MY, Cividalli G, Or R. Non-myeloablative stem cell transplantation and donor lymphocyte infusion for the treatment of cancer and life-threatening non-malignant disorders. Rev Clin Exp Hematol 2001: 5: 135.
    • (2001) Rev. Clin. Exp. Hematol. , vol.5 , pp. 135
    • Slavin, S.1    Nagler, A.2    Aker, M.3    Shapira, M.Y.4    Cividalli, G.5    Or, R.6
  • 8
    • 0036329702 scopus 로고    scopus 로고
    • Cerebral X-linked adrenoleukodystrophy in a girl with Xq27-Ter deletion
    • Hershkovitz E, Narkis G, Shorer Z et al. Cerebral X-linked adrenoleukodystrophy in a girl with Xq27-Ter deletion. Ann Neurol 2002: 52: 234.
    • (2002) Ann. Neurol. , vol.52 , pp. 234
    • Hershkovitz, E.1    Narkis, G.2    Shorer, Z.3
  • 9
    • 0016187133 scopus 로고
    • Clinical manifestations of graft-versus-host disease in human recipients of marrow from HL-A-matched sibling donors
    • Glucksberg H, Storb R, Fefer A et al. Clinical manifestations of graft-versus-host disease in human recipients of marrow from HL-A-matched sibling donors. Transplantation 1974: 18: 295.
    • (1974) Transplantation , vol.18 , pp. 295
    • Glucksberg, H.1    Storb, R.2    Fefer, A.3
  • 10
    • 0023104845 scopus 로고
    • Variable number of tandem repeat (VNTR) markers for human gene mapping
    • Nakamura Y, Leppert M, OC P et al. Variable number of tandem repeat (VNTR) markers for human gene mapping. Science 1987: 235: 1616.
    • (1987) Science , vol.235 , pp. 1616
    • Nakamura, Y.1    Leppert, M.2    Oc, P.3
  • 11
    • 0023148109 scopus 로고
    • The adrenoleukodystrophy-adrenomyeloneuropathy complex: Is it treatable?
    • Kolodny EH. The adrenoleukodystrophy-adrenomyeloneuropathy complex: is it treatable? Ann Neurol 1987: 21: 230.
    • (1987) Ann. Neurol. , vol.21 , pp. 230
    • Kolodny, E.H.1
  • 12
    • 0027186364 scopus 로고
    • A two-year trial of oleic and erucic acids (Lorenzo's oil) as treatment for adrenomyeloneuropathy
    • Aubourg P, Adamsbaum C, Lavallard-Rousseau MC et al. A two-year trial of oleic and erucic acids (Lorenzo's oil) as treatment for adrenomyeloneuropathy. N Engl J Med 1993: 329: 745.
    • (1993) N. Engl. J. Med. , vol.329 , pp. 745
    • Aubourg, P.1    Adamsbaum, C.2    Lavallard-Rousseau, M.C.3
  • 13
    • 0028063174 scopus 로고
    • Very long chain fatty acids in X-linked adrenoleukodystrophy brain after treatment with Lorenzo's oil
    • Poulos A, Gibson R, Sharp P, Beckman K, Grattan-Smith P. Very long chain fatty acids in X-linked adrenoleukodystrophy brain after treatment with Lorenzo's oil. Ann Neurol 1994: 36: 741.
    • (1994) Ann. Neurol. , vol.36 , pp. 741
    • Poulos, A.1    Gibson, R.2    Sharp, P.3    Beckman, K.4    Grattan-Smith, P.5
  • 14
    • 0019353202 scopus 로고
    • Adrenoleukodystrophy. Failure of immunosuppression to prevent neurological progression
    • Stumpf DA, Hayward A, Haas R et al. Adrenoleukodystrophy. Failure of immunosuppression to prevent neurological progression. Arch Neurol 1981: 38: 48.
    • (1981) Arch. Neurol. , vol.38 , pp. 48
    • Stumpf, D.A.1    Hayward, A.2    Haas, R.3
  • 15
    • 0023715704 scopus 로고
    • Childhood adrenoleukodystrophy. Failure of intensive immunosuppression to arrest neurologic progression
    • Naidu S, Bresnan MJ, Griffin D et al. Childhood adrenoleukodystrophy. Failure of intensive immunosuppression to arrest neurologic progression. Arch Neurol 1988: 45: 846.
    • (1988) Arch. Neurol. , vol.45 , pp. 846
    • Naidu, S.1    Bresnan, M.J.2    Griffin, D.3
  • 16
    • 0025329012 scopus 로고
    • Reversal of early neurologic and neuroradiologic manifestations of X-linked adrenoleukodystrophy by bone marrow transplantation
    • Auborg P, Blanche S, Jambaque I et al. Reversal of early neurologic and neuroradiologic manifestations of X-linked adrenoleukodystrophy by bone marrow transplantation. N Engl J Med 1990: 322: 1860.
    • (1990) N. Engl. J. Med. , vol.322 , pp. 1860
    • Auborg, P.1    Blanche, S.2    Jambaque, I.3
  • 17
    • 0034718378 scopus 로고    scopus 로고
    • Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-finked adrenoleukodystrophy
    • Shapiro E, Krivit W, Lockman L et al. Long-term effect of bone-marrow transplantation for childhood-onset cerebral X-finked adrenoleukodystrophy. Lancet 2000: 356: 713.
    • (2000) Lancet , vol.356 , pp. 713
    • Shapiro, E.1    Krivit, W.2    Lockman, L.3
  • 18
    • 0034531907 scopus 로고    scopus 로고
    • From marrow to brain: Expression of neuronal phenotypes in adult mice
    • Brazelton TR, Rossi FM, Keshet GI, Blau HM. From marrow to brain: expression of neuronal phenotypes in adult mice. Science 2000: 290: 1775.
    • (2000) Science , vol.290 , pp. 1775
    • Brazelton, T.R.1    Rossi, F.M.2    Keshet, G.I.3    Blau, H.M.4
  • 19
    • 0034532106 scopus 로고    scopus 로고
    • Turning blood into brain: Cells bearing neuronal antigens generated in vivo from bone marrow
    • Mezey E, Chandross KJ, Harta G, Maki RA, McKercher SR. Turning blood into brain: cells bearing neuronal antigens generated in vivo from bone marrow. Science 2000: 290: 1779.
    • (2000) Science , vol.290 , pp. 1779
    • Mezey, E.1    Chandross, K.J.2    Harta, G.3    Maki, R.A.4    McKercher, S.R.5
  • 21
    • 0037041427 scopus 로고    scopus 로고
    • Bone marrow cells adopt the phenotype of other cells by spontaneous cell fusion
    • Terada N, Hamazaki T, Oka M et al. Bone marrow cells adopt the phenotype of other cells by spontaneous cell fusion. Nature 2002: 416: 542.
    • (2002) Nature , vol.416 , pp. 542
    • Terada, N.1    Hamazaki, T.2    Oka, M.3
  • 22
    • 0242584006 scopus 로고    scopus 로고
    • Fusion of bone-marrow-derived cells with Purkinje neurons, cardiomyocytes and hepatocytes
    • Alvarez-Dolado M, Pardal R, Garcia-Verdugo JM et al. Fusion of bone-marrow-derived cells with Purkinje neurons, cardiomyocytes and hepatocytes. Nature 2003: 425: 968.
    • (2003) Nature , vol.425 , pp. 968
    • Alvarez-Dolado, M.1    Pardal, R.2    Garcia-Verdugo, J.M.3
  • 23
    • 0037183884 scopus 로고    scopus 로고
    • Little evidence for developmental plasticity of adult hematopoietic stem cells
    • Wagers AJ, Sherwood RI, Christensen JL, Weissman IL. Little evidence for developmental plasticity of adult hematopoietic stem cells. Science 2002: 297: 2256.
    • (2002) Science , vol.297 , pp. 2256
    • Wagers, A.J.1    Sherwood, R.I.2    Christensen, J.L.3    Weissman, I.L.4
  • 24
    • 0036344648 scopus 로고    scopus 로고
    • Non-myeloablative stem cell transplantation for the treatment of cancer and life-threatening non-malignant disorders; past accomplishments and future goals
    • Slavin S, Aker M, Shapira MY, Panigrahi S, Gabriel C, Or R. Non-myeloablative stem cell transplantation for the treatment of cancer and life-threatening non-malignant disorders; past accomplishments and future goals. Transfus Apheresis Sci 2002: 27: 159.
    • (2002) Transfus Apheresis Sci. , vol.27 , pp. 159
    • Slavin, S.1    Aker, M.2    Shapira, M.Y.3    Panigrahi, S.4    Gabriel, C.5    Or, R.6
  • 25
    • 0344522826 scopus 로고    scopus 로고
    • Non-myeloablative hematopoietic cell transplant for treatment of nonmalignant disorders in children
    • Woolfrey AE, Pulsipher MA, Storb R. Non-myeloablative hematopoietic cell transplant for treatment of nonmalignant disorders in children. Int J Hematol 2002: 76 (Suppl 2): 271.
    • (2002) Int. J. Hematol. , vol.76 , Issue.SUPPL. 2 , pp. 271
    • Woolfrey, A.E.1    Pulsipher, M.A.2    Storb, R.3
  • 26
    • 0029114944 scopus 로고
    • The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome
    • Krivit W, Lockman LA, Watkins PA, Hirsch J, Shapiro EG. The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome. J Inherit Metab Dis 1995: 18: 398.
    • (1995) J. Inherit. Metab. Dis. , vol.398 , pp. 18
    • Krivit, W.1    Lockman, L.A.2    Watkins, P.A.3    Hirsch, J.4    Shapiro, E.G.5
  • 27
    • 0029023990 scopus 로고
    • Clinical and therapeutic aspects of adrenoleukodystrophy and adrenomyeloneuropathy
    • Moser HW. Clinical and therapeutic aspects of adrenoleukodystrophy and adrenomyeloneuropathy. J Neuropathol Exp Neurol 1995: 54: 740.
    • (1995) J. Neuropathol. Exp. Neurol. , vol.54 , pp. 740
    • Moser, H.W.1
  • 28
    • 0029082884 scopus 로고
    • Komrower Lecture. Adrenoleukodystrophy: Natural history, treatment and outcome
    • Moser HW. Komrower Lecture. Adrenoleukodystrophy: natural history, treatment and outcome. J Inherit Metab Dis 1995: 18: 435.
    • (1995) J. Inherit. Metab. Dis. , vol.18 , pp. 435
    • Moser, H.W.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.