Characterization of a transgenic short hairpin RNA-induced murine model of tafazzin deficiency

Human Gene Therapy

Volumn 22, Issue 7, 2011, Pages 865-871

  Soustek, Meghan S ^a,b   Falk, Darin J ^a,b   Mah, Cathryn S ^a,b   Toth, Matthew J ^c   Schlame, Michael ^c,d   Lewin, Alfred S ^b   Byrne, Barry J ^a,b,c  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^b UNIVERSITY OF FLORIDA   (United States)

^c Barth Syndrome Foundation   (United States)

^d NEW YORK UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ACYLTRANSFERASE; CARDIOLIPIN; MESSENGER RNA; SHORT HAIRPIN RNA;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BARTH SYNDROME; BIOACCUMULATION; CONTROLLED STUDY; FEMALE; GENE; GENE INDUCTION; GENE MUTATION; HEART LEFT VENTRICLE EJECTION FRACTION; HEART MITOCHONDRION; HEART MUSCLE; IN VIVO STUDY; MITOCHONDRIAL MEMBRANE; MORPHOLOGY; MUSCLE CONTRACTILITY; MUSCLE FIBRIL; MUSCLE MITOCHONDRION; MUSCLE STRENGTH; NONHUMAN; SEQUENCE HOMOLOGY; SKELETAL MUSCLE; SOLEUS MUSCLE; TAFAZZIN GENE; TRANSGENE; TRANSGENIC MOUSE;

ANIMALS; ANIMALS, GENETICALLY MODIFIED; BARTH SYNDROME; DISEASE MODELS, ANIMAL; ELECTROCARDIOGRAPHY; FEMALE; GENE KNOCKDOWN TECHNIQUES; GENETIC LOCI; GENOTYPE; MAGNETIC RESONANCE IMAGING; MICE; MICROSCOPY, ELECTRON; MITOCHONDRIA; MUSCLE, SKELETAL; MUTATION; MYOCARDIUM; RNA, MESSENGER; RNA, SMALL INTERFERING; TRANSCRIPTION FACTORS;

ANIMALIA; DANIO RERIO; MAMMALIA; MURINAE; MUS; MUS MUSCULUS;

EID: 79960343132     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2010.199     Document Type: Article

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