Stable hematopoietic cell engraftment after low-intensity nonmyeloablative conditioning in patients with immune dysregulation, polyendocrinopathy, enteropathy, X-linked syndrome

Journal of Allergy and Clinical Immunology

Volumn 126, Issue 5, 2010, Pages 1000-1005

  Burroughs, Lauri M ^a,b   Torgerson, Troy R ^b,c   Storb, Rainer ^a,b   Carpenter, Paul A ^a,b   Rawlings, David J ^b,c   Sanders, Jean ^a,b   Scharenberg, Andrew M ^b,c   Skoda Smith, Suzanne ^b,c   Englund, Janet ^b   Ochs, Hans D ^b,c   Woolfrey, Ann E ^a,b  

^a Fred Hutchinson Cancer Research Center   (United States)

^b UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

^c SEATTLE CHILDREN S RESEARCH INSTITUTE   (United States)

Author keywords

Autoimmunity; Hematopoietic cell transplantation; Immune dysregulation; Immune reconstitution; Immunodeficiency; Nonmyeloablative conditioning regimen; Regulatory T cells

Indexed keywords

CYCLOSPORIN; FLUDARABINE; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; TRANSCRIPTION FACTOR FOXP3;

ARTICLE; CASE REPORT; CHILD; CHIMERA; CLINICAL FEATURE; COMORBIDITY; ENGRAFTMENT; FOLLOW UP; GENE EXPRESSION; HUMAN; IMMUNOSUPPRESSIVE TREATMENT; INFANT; IPEX SYNDROME; LYMPHOCYTE SUBPOPULATION; NONMYELOABLATIVE CONDITIONING; PERIPHERAL BLOOD STEM CELL; PRIORITY JOURNAL; PROTEIN EXPRESSION; REGULATORY T LYMPHOCYTE; RISK FACTOR; SCHOOL CHILD; SYMPTOM; WHOLE BODY RADIATION;

ADOLESCENT; CELL SEPARATION; CHILD; CYCLOSPORINE; FLOW CYTOMETRY; FORKHEAD TRANSCRIPTION FACTORS; GENETIC DISEASES, X-LINKED; GRAFT VS HOST DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; IMMUNOLOGIC DEFICIENCY SYNDROMES; IMMUNOSUPPRESSIVE AGENTS; INFANT; MALE; MYCOPHENOLIC ACID; MYELOABLATIVE AGONISTS; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; SYNDROME; TRANSPLANTATION CONDITIONING; VIDARABINE; WHOLE-BODY IRRADIATION;

EID: 78049461165     PISSN: 00916749     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.jaci.2010.05.021     Document Type: Article

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