Treatment of the immune dysregulation, polyendoccrinopathy, enteropathy, X-linked syndrome (IPEX) by allogeneic bone marrow transplantation

New England Journal of Medicine

Volumn 344, Issue 23, 2001, Pages 1758-1762

  Baud, Olivier ^a   Goulet, Olivier ^a   Canioni, Danielle ^a   Le Deist, Françoise ^a   Radford, Isabelle ^a   Rieu, Daniel ^c   Dupuis Girod, Sophie ^a   Cerf Bensussan, Nadine ^a   Cavazzana Calvo, Marina ^a   Brousse, Nicole ^a   Fisher, Alain ^a   Casanova, Jean Laurent ^a,b  

^a HÔPITAL NECKER ENFANTS MALADES   (France)

^b UNIVERSITÉ PARIS DESCARTES   (France)

^c HÔPITAL ARNAUD DE VILLENEUVE   (France)

Author keywords

[No Author keywords available]

Indexed keywords

ADOLESCENT; ADULT; ARTICLE; AUTOIMMUNE DISEASE; AUTOSOMAL RECESSIVE DISORDER; BONE MARROW TRANSPLANTATION; CASE REPORT; CLINICAL FEATURE; DISEASE COURSE; ENTEROPATHY; FEMALE; HUMAN; IMMUNOPATHOLOGY; IPEX SYNDROME; PEDIGREE; PRIORITY JOURNAL; SCHOOL CHILD; TREATMENT INDICATION; X CHROMOSOME LINKED DISORDER;

ANEMIA, HEMOLYTIC; AUTOIMMUNE DISEASES; BONE MARROW TRANSPLANTATION; DIABETES MELLITUS, TYPE 1; DIARRHEA; DNA-BINDING PROTEINS; FATAL OUTCOME; FEMALE; FORKHEAD TRANSCRIPTION FACTORS; HUMANS; INFANT; LINKAGE (GENETICS); MALE; PEDIGREE; POINT MUTATION; POLYENDOCRINOPATHIES, AUTOIMMUNE; SYNDROME; TRANSPLANTATION, HOMOLOGOUS; X CHROMOSOME;

EID: 0035821985     PISSN: 00284793     EISSN: None     Source Type: Journal    
DOI: 10.1056/NEJM200106073442304     Document Type: Article

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