Gene therapy of x-linked adrenoleukodystrophy using hematopoietic stem cells and a lentiviral vector;Thérapie génique de l'adrénoleucodystrophie liée à l'X par transfert du gène dans les cellules souches hématopoïétiques à l'aide d'un vecteur lentiviral

Bulletin de l'Academie Nationale de Medecine

Volumn 194, Issue 2, 2010, Pages 255-268

  Cartier, Nathalie ^a   Hacein Bey Abina, Salima ^a   Von Kalle, Christof ^a   Bougnères, Pierre ^a   Fischer, Alain ^a   Cavazzana Calvo, Marina ^a   Aubourg, Patrick ^a  

^a INSERM   (France)

Author keywords

Adrenoleukodystrophy; Gene Therapy; Hematopoietic Stem Cells; Lentivirus

Indexed keywords

EID: 77955564990     PISSN: 00014079     EISSN: None     Source Type: Journal    
DOI: 10.1016/s0001-4079(19)32319-2     Document Type: Conference Paper

References (12)

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9. BENHAMIDA S., PFLUMIO F, DUBART-KUPPERSCHMITT A et al. - Transduced CD34+ cells from adrenoleukodystrophy patients with HIV-derived vector mediate long-term engraftment of NOD/SCID mice.Mol. Ther., 2003, 7, 317.
10. ASHEUER M., PFLUMIO F., BENHAMIDA S., DUBART-KUPPERSCHMITT A et al. - Human CD34+ cells differentiate into microglia and express recombinant therapeutic protein. Proc. Natl. Acad. Sci. U.S.A., 2005, 101, 3557.
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