-
1
-
-
33646418438
-
The ocular features of the mucopolysaccharidoses
-
Ashworth JL, Biswas S, Wraith E, Lloyd IC. The ocular features of the mucopolysaccharidoses. Eye 2006, 20:553-63.
-
(2006)
Eye
, vol.20
, pp. 553-563
-
-
Ashworth, J.L.1
Biswas, S.2
Wraith, E.3
Lloyd, I.C.4
-
2
-
-
33747066706
-
Genetics of corneal dystrophies: the evolving landscape
-
Pieramici SF, Afshari NA. Genetics of corneal dystrophies: the evolving landscape. Curr Opin Ophthalmol 2006, 17:361-6.
-
(2006)
Curr Opin Ophthalmol
, vol.17
, pp. 361-366
-
-
Pieramici, S.F.1
Afshari, N.A.2
-
3
-
-
38549095458
-
Genetics of anterior and stromal corneal dystrophies
-
Poulaki V, Colby K. Genetics of anterior and stromal corneal dystrophies. Semin Ophthalmol 2008, 23:9-17.
-
(2008)
Semin Ophthalmol
, vol.23
, pp. 9-17
-
-
Poulaki, V.1
Colby, K.2
-
4
-
-
0034887136
-
Corneal neovascularization
-
Chang JH, Gabison EE, Kato T, Azar DT. Corneal neovascularization. Curr Opin Ophthalmol 2001, 12:242-9.
-
(2001)
Curr Opin Ophthalmol
, vol.12
, pp. 242-249
-
-
Chang, J.H.1
Gabison, E.E.2
Kato, T.3
Azar, D.T.4
-
5
-
-
40249088145
-
Fibrotic disorders in the eye: targets of gene therapy
-
Saika S, Yamanaka O, Sumioka T. Fibrotic disorders in the eye: targets of gene therapy. Prog Retin Eye Res 2008, 27:177-96.
-
(2008)
Prog Retin Eye Res
, vol.27
, pp. 177-196
-
-
Saika, S.1
Yamanaka, O.2
Sumioka, T.3
-
6
-
-
3142779846
-
Gene therapy approaches to prolonging corneal allograft survival
-
Williams KA, Jessup CF, Coster DJ. Gene therapy approaches to prolonging corneal allograft survival. Expert Opin Biol Ther 2004, 4:1059-71.
-
(2004)
Expert Opin Biol Ther
, vol.4
, pp. 1059-1071
-
-
Williams, K.A.1
Jessup, C.F.2
Coster, D.J.3
-
7
-
-
32944473806
-
Induction of replication in human corneal endothelial cells by E2F2 transcription factor cDNA transfer
-
McAlister JC, Joyce NC, Harris DL, Ali RR, Larkin DF. Induction of replication in human corneal endothelial cells by E2F2 transcription factor cDNA transfer. Invest Ophthalmol Vis Sci 2005, 46:3597-603.
-
(2005)
Invest Ophthalmol Vis Sci
, vol.46
, pp. 3597-3603
-
-
McAlister, J.C.1
Joyce, N.C.2
Harris, D.L.3
Ali, R.R.4
Larkin, D.F.5
-
8
-
-
44649125943
-
Maroteaux-Lamy syndrome: functional characterization of pathogenic mutations and polymorphisms in the arylsulfatase B gene
-
Garrido E, Cormand B, Hopwood JJ, Chabás A, Grinberg D, Vilageliu L. Maroteaux-Lamy syndrome: functional characterization of pathogenic mutations and polymorphisms in the arylsulfatase B gene. Mol Genet Metab 2008, 94:305-12.
-
(2008)
Mol Genet Metab
, vol.94
, pp. 305-312
-
-
Garrido, E.1
Cormand, B.2
Hopwood, J.J.3
Chabás, A.4
Grinberg, D.5
Vilageliu, L.6
-
9
-
-
63749116578
-
Mutations and polymorphisms in GUSB gene in mucopolysaccharidosis VII (Sly Syndrome)
-
Tomatsu S, Montaño AM, Dung VC, Grubb JH, Sly WS. Mutations and polymorphisms in GUSB gene in mucopolysaccharidosis VII (Sly Syndrome). Hum Mutat 2009, 30:511-9.
-
(2009)
Hum Mutat
, vol.30
, pp. 511-519
-
-
Tomatsu, S.1
Montaño, A.M.2
Dung, V.C.3
Grubb, J.H.4
Sly, W.S.5
-
10
-
-
33846958072
-
Elucidating the molecular genetic basis of the corneal dystrophies: are we there yet?
-
Aldave AJ, Sonmez B. Elucidating the molecular genetic basis of the corneal dystrophies: are we there yet? Arch Ophthalmol 2007, 125:177-86.
-
(2007)
Arch Ophthalmol
, vol.125
, pp. 177-186
-
-
Aldave, A.J.1
Sonmez, B.2
-
11
-
-
0008206775
-
-
eds, Adelaide, Flinders University Press
-
Williams KA, Lowe MT, Bartlett CM, Kelly L, Coster DJ. The Australian Corneal Graft Registry Report 2007 2008, 1-194. eds, Adelaide, Flinders University Press
-
(2008)
The Australian Corneal Graft Registry Report 2007
, pp. 1-194
-
-
Williams, K.A.1
Lowe, M.T.2
Bartlett, C.M.3
Kelly, L.4
Coster, D.J.5
-
12
-
-
33750430869
-
Corneal avascularity is due to soluble VEGF receptor-1
-
Ambati BK, Nozaki M, Singh N. Corneal avascularity is due to soluble VEGF receptor-1. Nature 2006, 443:993-7.
-
(2006)
Nature
, vol.443
, pp. 993-997
-
-
Ambati, B.K.1
Nozaki, M.2
Singh, N.3
-
13
-
-
38349081535
-
Promotion of graft survival by vascular endothelial growth factor A neutralization after high-risk corneal transplantation
-
Bachmann BO, Bock F, Wiegand SJ. Promotion of graft survival by vascular endothelial growth factor A neutralization after high-risk corneal transplantation. Arch Ophthalmol 2008, 126:71-7.
-
(2008)
Arch Ophthalmol
, vol.126
, pp. 71-77
-
-
Bachmann, B.O.1
Bock, F.2
Wiegand, S.J.3
-
15
-
-
20944448800
-
Expression of Smad7 in mouse eyes accelerates healing of corneal tissue following exposure to alkali
-
Saika S, Ikeda K, Yamanaka O. Expression of Smad7 in mouse eyes accelerates healing of corneal tissue following exposure to alkali. Am J Pathol 2005, 166:1405-18.
-
(2005)
Am J Pathol
, vol.166
, pp. 1405-1418
-
-
Saika, S.1
Ikeda, K.2
Yamanaka, O.3
-
16
-
-
29244455283
-
The impact of corneal allograft rejection on the long-term outcome of corneal transplantation
-
Coster DJ, Williams KA. The impact of corneal allograft rejection on the long-term outcome of corneal transplantation. Am J Ophthalmol 2005, 140:1112-22.
-
(2005)
Am J Ophthalmol
, vol.140
, pp. 1112-1122
-
-
Coster, D.J.1
Williams, K.A.2
-
17
-
-
65349179021
-
The potential of viral vector- mediated gene transfer to prolong corneal allograft survival
-
Parker DG, Brereton HM, Coster DJ, Williams KA. The potential of viral vector- mediated gene transfer to prolong corneal allograft survival. Curr Gene Ther 2009, 9:33-44.
-
(2009)
Curr Gene Ther
, vol.9
, pp. 33-44
-
-
Parker, D.G.1
Brereton, H.M.2
Coster, D.J.3
Williams, K.A.4
-
18
-
-
0035872802
-
Prolongation of sheep corneal allograft survival by ex vivo transfer of the gene encoding interleukin-10
-
Klebe S, Sykes PJ, Coster DJ, Krishnan R, Williams KA. Prolongation of sheep corneal allograft survival by ex vivo transfer of the gene encoding interleukin-10. Transplantation 2001, 71:1214-20.
-
(2001)
Transplantation
, vol.71
, pp. 1214-1220
-
-
Klebe, S.1
Sykes, P.J.2
Coster, D.J.3
Krishnan, R.4
Williams, K.A.5
-
19
-
-
0036938746
-
Influence of ballistic gene transfer on antigen-presenting cells in murine corneas
-
Muller A, Zhang EP, Schroff M, Wittig B, Hoffmann F. Influence of ballistic gene transfer on antigen-presenting cells in murine corneas. Graefes Arch Clin Exp Ophthalmol 2002, 240:851-9.
-
(2002)
Graefes Arch Clin Exp Ophthalmol
, vol.240
, pp. 851-859
-
-
Muller, A.1
Zhang, E.P.2
Schroff, M.3
Wittig, B.4
Hoffmann, F.5
-
20
-
-
0036202821
-
Effect of administration of CTLA4-Ig as protein or cDNA on corneal allograft survival
-
Comer RM, King WJ, Ardjomand N, Theoharis S, George AJ, Larkin DF. Effect of administration of CTLA4-Ig as protein or cDNA on corneal allograft survival. Invest Ophthalmol Vis Sci 2002, 43:1095-103.
-
(2002)
Invest Ophthalmol Vis Sci
, vol.43
, pp. 1095-1103
-
-
Comer, R.M.1
King, W.J.2
Ardjomand, N.3
Theoharis, S.4
George, A.J.5
Larkin, D.F.6
-
21
-
-
0347531772
-
Ballistic CTLA4 and IL-4 gene transfer into the lower lid prolongs orthotopic corneal graft survival in mice
-
Zhang EP, Franke J, Schroff M, Junghans C, Wittig B, Hoffmann F. Ballistic CTLA4 and IL-4 gene transfer into the lower lid prolongs orthotopic corneal graft survival in mice. Graefes Arch Clin Exp Ophthalmol 2003, 241:921-6.
-
(2003)
Graefes Arch Clin Exp Ophthalmol
, vol.241
, pp. 921-926
-
-
Zhang, E.P.1
Franke, J.2
Schroff, M.3
Junghans, C.4
Wittig, B.5
Hoffmann, F.6
-
22
-
-
23444461955
-
Prolongation of sheep corneal allograft survival by transfer of the gene encoding ovine IL-12-p40 but not IL-4 to donor corneal endothelium
-
Klebe S, Coster DJ, Sykes PJ. Prolongation of sheep corneal allograft survival by transfer of the gene encoding ovine IL-12-p40 but not IL-4 to donor corneal endothelium. J Immunol 2005, 175:2219-26.
-
(2005)
J Immunol
, vol.175
, pp. 2219-2226
-
-
Klebe, S.1
Coster, D.J.2
Sykes, P.J.3
-
23
-
-
33646239375
-
Influence of local and systemic CTLA4Ig gene transfer on corneal allograft survival
-
Gong N, Pleyer U, Yang J. Influence of local and systemic CTLA4Ig gene transfer on corneal allograft survival. J Gene Med 2006, 8:459-67.
-
(2006)
J Gene Med
, vol.8
, pp. 459-467
-
-
Gong, N.1
Pleyer, U.2
Yang, J.3
-
24
-
-
33644955010
-
Function of indoleamine 2,3-dioxygenase in corneal allograft rejection and prolongation of allograft survival by over-expression
-
Beutelspacher SC, Pillai R, Watson MP. Function of indoleamine 2,3-dioxygenase in corneal allograft rejection and prolongation of allograft survival by over-expression. Eur J Immunol 2006, 36:690-700.
-
(2006)
Eur J Immunol
, vol.36
, pp. 690-700
-
-
Beutelspacher, S.C.1
Pillai, R.2
Watson, M.P.3
-
25
-
-
33847776096
-
Effects of local and systemic viral interleukin-10 gene transfer on corneal allograft survival
-
Gong N, Pleyer U, Volk HD, Ritter T. Effects of local and systemic viral interleukin-10 gene transfer on corneal allograft survival. Gene Ther 2007, 14:484-90.
-
(2007)
Gene Ther
, vol.14
, pp. 484-490
-
-
Gong, N.1
Pleyer, U.2
Volk, H.D.3
Ritter, T.4
-
26
-
-
47049101220
-
Expression of the chemokine antagonist vMIP II using a non-viral vector can prolong corneal allograft survival
-
Pillai RG, Beutelspacher SC, Larkin DF, George AJ. Expression of the chemokine antagonist vMIP II using a non-viral vector can prolong corneal allograft survival. Transplantation 2008, 85:1640-7.
-
(2008)
Transplantation
, vol.85
, pp. 1640-1647
-
-
Pillai, R.G.1
Beutelspacher, S.C.2
Larkin, D.F.3
George, A.J.4
-
27
-
-
34047252855
-
Local overexpression of nerve growth factor in rat corneal transplants improves allograft survival
-
Gong N, Pleyer U, Vogt K. Local overexpression of nerve growth factor in rat corneal transplants improves allograft survival. Invest Ophthalmol Vis Sci 2007, 48:1043-52.
-
(2007)
Invest Ophthalmol Vis Sci
, vol.48
, pp. 1043-1052
-
-
Gong, N.1
Pleyer, U.2
Vogt, K.3
-
28
-
-
34547829459
-
Corneal graft rejection is accompanied by apoptosis of the endothelium and is prevented by gene therapy with Bcl-xL
-
Barcia RN, Dana MR, Kazlauskas A. Corneal graft rejection is accompanied by apoptosis of the endothelium and is prevented by gene therapy with Bcl-xL. Am J Transplant 2007, 7:2082-9.
-
(2007)
Am J Transplant
, vol.7
, pp. 2082-2089
-
-
Barcia, R.N.1
Dana, M.R.2
Kazlauskas, A.3
-
29
-
-
53249145658
-
Therapeutic approaches in glycogen storage disease type II/Pompe disease
-
Schoser B, Hill V, Raben N. Therapeutic approaches in glycogen storage disease type II/Pompe disease. Neurotherapeutics 2008, 5:569-78.
-
(2008)
Neurotherapeutics
, vol.5
, pp. 569-578
-
-
Schoser, B.1
Hill, V.2
Raben, N.3
-
30
-
-
45749120846
-
The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update
-
Suppl
-
Rovelli AM. The controversial and changing role of haematopoietic cell transplantation for lysosomal storage disorders: an update. Bone Marrow Transplant 2008, 41(2):S87-9. Suppl
-
(2008)
Bone Marrow Transplant
, vol.41
, Issue.2
-
-
Rovelli, A.M.1
-
31
-
-
67349280926
-
Does enzyme replacement therapy influence the ocular changes in type VI mucopolysaccharidosis?
-
Pitz S, Ogun O, Arash L, Miebach E, Beck M. Does enzyme replacement therapy influence the ocular changes in type VI mucopolysaccharidosis? Graefes Arch Clin Exp Ophthalmol 2009, 247:975-80.
-
(2009)
Graefes Arch Clin Exp Ophthalmol
, vol.247
, pp. 975-980
-
-
Pitz, S.1
Ogun, O.2
Arash, L.3
Miebach, E.4
Beck, M.5
-
32
-
-
0033866381
-
Corneal transplantation in a patient with mucopolysaccharidosis type VII (Sly disease)
-
Bergwerk KE, Falk RE, Glasgow BJ, Rabinowitz YS. Corneal transplantation in a patient with mucopolysaccharidosis type VII (Sly disease). Ophthalmic Genet 2000, 21:17-20.
-
(2000)
Ophthalmic Genet
, vol.21
, pp. 17-20
-
-
Bergwerk, K.E.1
Falk, R.E.2
Glasgow, B.J.3
Rabinowitz, Y.S.4
-
33
-
-
0034758482
-
Long-term follow-up of corneal graft survival following bone marrow transplantation in the Maroteaux-Lamy syndrome
-
Uçakhan OO, Brodie SE, Desnick R, Willner J, Asbell PA. Long-term follow-up of corneal graft survival following bone marrow transplantation in the Maroteaux-Lamy syndrome. CLAO J 2001, 27:234-7.
-
(2001)
CLAO J
, vol.27
, pp. 234-237
-
-
Uçakhan, O.O.1
Brodie, S.E.2
Desnick, R.3
Willner, J.4
Asbell, P.A.5
-
34
-
-
0030892231
-
Corneal transplantation in Maroteaux-Lamy syndrome
-
Varssano D, Cohen EJ, Nelson LB, Eagle RC. Corneal transplantation in Maroteaux-Lamy syndrome. Arch Ophthalmol 1997, 115:428-9.
-
(1997)
Arch Ophthalmol
, vol.115
, pp. 428-429
-
-
Varssano, D.1
Cohen, E.J.2
Nelson, L.B.3
Eagle, R.C.4
-
35
-
-
0037344452
-
Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII
-
Kamata Y, Tanabe A, Kanaji A. Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII. Gene Ther 2003, 10:406-14.
-
(2003)
Gene Ther
, vol.10
, pp. 406-414
-
-
Kamata, Y.1
Tanabe, A.2
Kanaji, A.3
-
36
-
-
0027051181
-
Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer
-
Wolfe JH, Sands MS, Barker JE. Reversal of pathology in murine mucopolysaccharidosis type VII by somatic cell gene transfer. Nature 1992, 360:749-53.
-
(1992)
Nature
, vol.360
, pp. 749-753
-
-
Wolfe, J.H.1
Sands, M.S.2
Barker, J.E.3
-
37
-
-
0034567124
-
Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII
-
Wolfe JH, Sands MS, Harel N. Gene transfer of low levels of beta-glucuronidase corrects hepatic lysosomal storage in a large animal model of mucopolysaccharidosis VII. Mol Ther 2000, 2:552-61.
-
(2000)
Mol Ther
, vol.2
, pp. 552-561
-
-
Wolfe, J.H.1
Sands, M.S.2
Harel, N.3
-
38
-
-
0034756448
-
Adenovirus-mediated gene therapy for corneal clouding in mice with mucopolysaccharidosis type VII
-
Kamata Y, Okuyama T, Kosuga M. Adenovirus-mediated gene therapy for corneal clouding in mice with mucopolysaccharidosis type VII. Mol Ther 2001, 4:307-12.
-
(2001)
Mol Ther
, vol.4
, pp. 307-312
-
-
Kamata, Y.1
Okuyama, T.2
Kosuga, M.3
-
39
-
-
0346957021
-
Prospects for gene therapy in corneal disease
-
Jun AS, Larkin DF. Prospects for gene therapy in corneal disease. Eye 2003, 17:906-11.
-
(2003)
Eye
, vol.17
, pp. 906-911
-
-
Jun, A.S.1
Larkin, D.F.2
-
40
-
-
21744461301
-
Gene therapy in the cornea
-
Mohan RR, Sharma A, Netto MV, Sinha S, Wilson SE. Gene therapy in the cornea. Prog Retin Eye Res 2005, 24:537-59.
-
(2005)
Prog Retin Eye Res
, vol.24
, pp. 537-559
-
-
Mohan, R.R.1
Sharma, A.2
Netto, M.V.3
Sinha, S.4
Wilson, S.E.5
-
42
-
-
0031571331
-
Suppression of ongoing ocular inflammatory disease by topical administration of plasmid DNA encoding IL-10
-
Daheshia M, Kuklin N, Kanangat S, Manickan E, Rouse BT. Suppression of ongoing ocular inflammatory disease by topical administration of plasmid DNA encoding IL-10. J Immunol 1997, 159:1945-52.
-
(1997)
J Immunol
, vol.159
, pp. 1945-1952
-
-
Daheshia, M.1
Kuklin, N.2
Kanangat, S.3
Manickan, E.4
Rouse, B.T.5
-
44
-
-
69249213481
-
Subconjunctival gene delivery of the transcription factor GA-binding protein delays corneal neovascularization in a mouse model
-
Yoon KC, Bae JA, Park HJ. Subconjunctival gene delivery of the transcription factor GA-binding protein delays corneal neovascularization in a mouse model. Gene Ther 2009, 16:973-81.
-
(2009)
Gene Ther
, vol.16
, pp. 973-981
-
-
Yoon, K.C.1
Bae, J.A.2
Park, H.J.3
-
45
-
-
0030930701
-
Controlled gene gun delivery and expression of DNA within the cornea
-
Tanelian DL, Barry MA, Johnston SA, Le T, Smith G. Controlled gene gun delivery and expression of DNA within the cornea. Biotechniques 1997, 23:484-8.
-
(1997)
Biotechniques
, vol.23
, pp. 484-488
-
-
Tanelian, D.L.1
Barry, M.A.2
Johnston, S.A.3
Le, T.4
Smith, G.5
-
46
-
-
0033935828
-
Corneal endothelial cell nuclei are damaged after DNA transfer using a gene gun
-
Klebe S, Stirling JW, Williams KA. Corneal endothelial cell nuclei are damaged after DNA transfer using a gene gun. Clin Experiment Ophthalmol 2000, 28:58-9.
-
(2000)
Clin Experiment Ophthalmol
, vol.28
, pp. 58-59
-
-
Klebe, S.1
Stirling, J.W.2
Williams, K.A.3
-
47
-
-
61449442375
-
Nanosecond electroporation: another look
-
Sundararajan R. Nanosecond electroporation: another look. Mol Biotechnol 2009, 41:69-82.
-
(2009)
Mol Biotechnol
, vol.41
, pp. 69-82
-
-
Sundararajan, R.1
-
48
-
-
39149121847
-
Current and future ophthalmic drug delivery systems. A shift to the posterior segment
-
Del Amo EM, Urtti A. Current and future ophthalmic drug delivery systems. A shift to the posterior segment. Drug Discov Today 2008, 13:135-43.
-
(2008)
Drug Discov Today
, vol.13
, pp. 135-143
-
-
Del Amo, E.M.1
Urtti, A.2
-
49
-
-
0033016739
-
Activated polyamidoamine dendrimers, a non- viral vector for gene transfer to the corneal endothelium
-
Hudde T, Rayner SA, Comer RM. Activated polyamidoamine dendrimers, a non- viral vector for gene transfer to the corneal endothelium. Gene Ther 1999, 6:939-43.
-
(1999)
Gene Ther
, vol.6
, pp. 939-943
-
-
Hudde, T.1
Rayner, S.A.2
Comer, R.M.3
-
50
-
-
64549134676
-
Nonviral vectors for gene delivery
-
Mintzer MA, Simanek EE. Nonviral vectors for gene delivery. Chem Rev 2009, 109:259-302.
-
(2009)
Chem Rev
, vol.109
, pp. 259-302
-
-
Mintzer, M.A.1
Simanek, E.E.2
-
51
-
-
0642336863
-
Antibody targeted gene transfer to endothelium
-
Tan PH, Manunta M, Ardjomand N. Antibody targeted gene transfer to endothelium. J Gene Med 2003, 5:311-23.
-
(2003)
J Gene Med
, vol.5
, pp. 311-323
-
-
Tan, P.H.1
Manunta, M.2
Ardjomand, N.3
-
52
-
-
29744464073
-
Exploration of peptide motifs for potent non-viral gene delivery highly selective for dividing cells
-
Parker AL, Collins L, Zhang X, Fabre JW. Exploration of peptide motifs for potent non-viral gene delivery highly selective for dividing cells. J Gene Med 2005, 7:1545-54.
-
(2005)
J Gene Med
, vol.7
, pp. 1545-1554
-
-
Parker, A.L.1
Collins, L.2
Zhang, X.3
Fabre, J.W.4
-
53
-
-
42149116854
-
Bioadhesive hyaluronan-chitosan nanoparticles can transport genes across the ocular mucosa and transfect ocular tissue
-
de la Fuente M, Seijo B, Alonso MJ. Bioadhesive hyaluronan-chitosan nanoparticles can transport genes across the ocular mucosa and transfect ocular tissue. Gene Ther 2008, 15:668-76.
-
(2008)
Gene Ther
, vol.15
, pp. 668-676
-
-
de la Fuente, M.1
Seijo, B.2
Alonso, M.J.3
-
54
-
-
67749113177
-
Efficient lentiviral gene transfer into corneal stroma cells using a femtosecond laser: Gene Ther
-
Bemelmans AP, Arsenijevic Y, Majo F. Efficient lentiviral gene transfer into corneal stroma cells using a femtosecond laser: Gene Ther. 2009
-
(2009)
-
-
Bemelmans, A.P.1
Arsenijevic, Y.2
Majo, F.3
-
55
-
-
34547865358
-
(LYS)(16)-based reducible polycations provide stable polyplexes with anionic fusogenic peptides and efficient gene delivery to post mitotic cells
-
Parker AL, Eckley L, Singh S, Preece JA, Collins L, Fabre JW. (LYS)(16)-based reducible polycations provide stable polyplexes with anionic fusogenic peptides and efficient gene delivery to post mitotic cells. Biochim Biophys Acta 2007, 1770:1331-7.
-
(2007)
Biochim Biophys Acta
, vol.1770
, pp. 1331-1337
-
-
Parker, A.L.1
Eckley, L.2
Singh, S.3
Preece, J.A.4
Collins, L.5
Fabre, J.W.6
-
56
-
-
0036942665
-
Minimizing side effects of ballistic gene transfer into the murine corneal epithelium
-
Zhang EP, Muller A, Schulte F. Minimizing side effects of ballistic gene transfer into the murine corneal epithelium. Graefes Arch Clin Exp Ophthalmol 2002, 240:114-9.
-
(2002)
Graefes Arch Clin Exp Ophthalmol
, vol.240
, pp. 114-119
-
-
Zhang, E.P.1
Muller, A.2
Schulte, F.3
-
57
-
-
33750997296
-
Regulation of corneal repair by particle-mediated gene transfer of opioid growth factor receptor complementary DNA
-
Zagon IS, Sassani JW, Malefyt KJ, McLaughlin PJ. Regulation of corneal repair by particle-mediated gene transfer of opioid growth factor receptor complementary DNA. Arch Ophthalmol 2006, 124:1620-4.
-
(2006)
Arch Ophthalmol
, vol.124
, pp. 1620-1624
-
-
Zagon, I.S.1
Sassani, J.W.2
Malefyt, K.J.3
McLaughlin, P.J.4
-
58
-
-
0031787123
-
Targeted gene transfer to corneal endothelium in vivo by electric pulse
-
Oshima Y, Sakamoto T, Yamanaka I, Nishi T, Ishibashi T, Inomata H. Targeted gene transfer to corneal endothelium in vivo by electric pulse. Gene Ther 1998, 51:1347-54.
-
(1998)
Gene Ther
, vol.51
, pp. 1347-1354
-
-
Oshima, Y.1
Sakamoto, T.2
Yamanaka, I.3
Nishi, T.4
Ishibashi, T.5
Inomata, H.6
-
59
-
-
0036353346
-
Targeted gene transfer to corneal stroma in vivo by electric pulses
-
Oshima Y, Sakamoto T, Hisatomi T. Targeted gene transfer to corneal stroma in vivo by electric pulses. Exp Eye Res 2002, 74:191-8.
-
(2002)
Exp Eye Res
, vol.74
, pp. 191-198
-
-
Oshima, Y.1
Sakamoto, T.2
Hisatomi, T.3
-
61
-
-
0346039142
-
Delivery of several forms of DNA, DNA-RNA hybrids, and dyes across human sclera by electrical fields
-
Davies JB, Ciavatta VT, Boatright JH, Nickerson JM. Delivery of several forms of DNA, DNA-RNA hybrids, and dyes across human sclera by electrical fields. Mol Vis 2003, 9:569-78.
-
(2003)
Mol Vis
, vol.9
, pp. 569-578
-
-
Davies, J.B.1
Ciavatta, V.T.2
Boatright, J.H.3
Nickerson, J.M.4
-
62
-
-
0034774810
-
Efficiency and toxicity of liposome-mediated gene transfer to corneal endothelial cells
-
Pleyer U, Groth D, Hinz B. Efficiency and toxicity of liposome-mediated gene transfer to corneal endothelial cells. Exp Eye Res 2001, 73:1-7.
-
(2001)
Exp Eye Res
, vol.73
, pp. 1-7
-
-
Pleyer, U.1
Groth, D.2
Hinz, B.3
-
63
-
-
0034765449
-
Gene transfer to ovine corneal endothelium
-
Klebe S, Sykes PJ, Coster DJ, Bloom DC, Williams KA. Gene transfer to ovine corneal endothelium. Clin Experiment Ophthalmol 2001, 29:316-22.
-
(2001)
Clin Experiment Ophthalmol
, vol.29
, pp. 316-322
-
-
Klebe, S.1
Sykes, P.J.2
Coster, D.J.3
Bloom, D.C.4
Williams, K.A.5
-
64
-
-
36448984350
-
A novel bubble liposome and ultrasound- mediated gene transfer to ocular surface: RC-1 cells in vitro and conjunctiva in vivo
-
Yamashita T, Sonoda S, Suzuki R. A novel bubble liposome and ultrasound- mediated gene transfer to ocular surface: RC-1 cells in vitro and conjunctiva in vivo. Exp Eye Res 2007, 85:741-8.
-
(2007)
Exp Eye Res
, vol.85
, pp. 741-748
-
-
Yamashita, T.1
Sonoda, S.2
Suzuki, R.3
-
65
-
-
3142773814
-
A synthetic peptide vector system for optimal gene delivery to corneal endothelium
-
Collins L, Fabre JW. A synthetic peptide vector system for optimal gene delivery to corneal endothelium. J Gene Med 2004, 6:185-94.
-
(2004)
J Gene Med
, vol.6
, pp. 185-194
-
-
Collins, L.1
Fabre, J.W.2
-
66
-
-
44649113307
-
Novel hyaluronic acid-chitosan nanoparticles for ocular gene therapy
-
de la Fuente M, Seijo B, Alonso MJ. Novel hyaluronic acid-chitosan nanoparticles for ocular gene therapy. Invest Ophthalmol Vis Sci 2008, 49:2016-24.
-
(2008)
Invest Ophthalmol Vis Sci
, vol.49
, pp. 2016-2024
-
-
de la Fuente, M.1
Seijo, B.2
Alonso, M.J.3
-
67
-
-
34249692487
-
Nanoparticles sustain expression of Flt intraceptors in the cornea and inhibit injury-induced corneal angiogenesis
-
Jani PD, Singh N, Jenkins C. Nanoparticles sustain expression of Flt intraceptors in the cornea and inhibit injury-induced corneal angiogenesis. Invest Ophthalmol Vis Sci 2007, 48:2030-6.
-
(2007)
Invest Ophthalmol Vis Sci
, vol.48
, pp. 2030-2036
-
-
Jani, P.D.1
Singh, N.2
Jenkins, C.3
-
68
-
-
0030025064
-
Adenovirus-mediated gene delivery to the corneal endothelium
-
Larkin DF, Oral HB, Ring CJ, Lemoine NR, George AJ. Adenovirus-mediated gene delivery to the corneal endothelium. Transplantation 1996, 61:363-70.
-
(1996)
Transplantation
, vol.61
, pp. 363-370
-
-
Larkin, D.F.1
Oral, H.B.2
Ring, C.J.3
Lemoine, N.R.4
George, A.J.5
-
69
-
-
20344388074
-
Is ex vivo adenovirus mediated gene transfer a therapeutic option for the treatment of corneal diseases?
-
Ritter T, Gong N, Pleyer U. Is ex vivo adenovirus mediated gene transfer a therapeutic option for the treatment of corneal diseases? Br J Ophthalmol 2005, 89:648-9.
-
(2005)
Br J Ophthalmol
, vol.89
, pp. 648-649
-
-
Ritter, T.1
Gong, N.2
Pleyer, U.3
-
70
-
-
0038128347
-
Immune response following intraocular delivery of recombinant viral vectors
-
Bennett J. Immune response following intraocular delivery of recombinant viral vectors. Gene Ther 2003, 10:977-82.
-
(2003)
Gene Ther
, vol.10
, pp. 977-982
-
-
Bennett, J.1
-
71
-
-
36249015420
-
Gene delivery by lentivirus vectors
-
Cockrell AS, Kafri T. Gene delivery by lentivirus vectors. Mol Biotechnol 2007, 36:184-204.
-
(2007)
Mol Biotechnol
, vol.36
, pp. 184-204
-
-
Cockrell, A.S.1
Kafri, T.2
-
73
-
-
34547691354
-
Retroviral integration and human gene therapy
-
Bushman FD. Retroviral integration and human gene therapy. J Clin Invest 2007, 117:2083-6.
-
(2007)
J Clin Invest
, vol.117
, pp. 2083-2086
-
-
Bushman, F.D.1
-
74
-
-
60649092964
-
Non-integrating lentiviral vectors
-
Sarkis C, Philippe S, Mallet J, Serguera C. Non-integrating lentiviral vectors. Curr Gene Ther 2008, 8:430-7.
-
(2008)
Curr Gene Ther
, vol.8
, pp. 430-437
-
-
Sarkis, C.1
Philippe, S.2
Mallet, J.3
Serguera, C.4
-
76
-
-
33845345920
-
AAV-mediated gene transfer for retinal diseases
-
Allocca M, Tessitore A, Cotugno G, Auricchio A. AAV-mediated gene transfer for retinal diseases. Expert Opin Biol Ther 2006, 6:1279-94.
-
(2006)
Expert Opin Biol Ther
, vol.6
, pp. 1279-1294
-
-
Allocca, M.1
Tessitore, A.2
Cotugno, G.3
Auricchio, A.4
-
77
-
-
1942423120
-
Hammerhead ribozyme targeting connective tissue growth factor mRNA blocks transforming growth factor-beta mediated cell proliferation
-
Blalock TD, Yuan R, Lewin AS, Schultz GS. Hammerhead ribozyme targeting connective tissue growth factor mRNA blocks transforming growth factor-beta mediated cell proliferation. Exp Eye Res 2004, 78:1127-36.
-
(2004)
Exp Eye Res
, vol.78
, pp. 1127-1136
-
-
Blalock, T.D.1
Yuan, R.2
Lewin, A.S.3
Schultz, G.S.4
-
78
-
-
0041464740
-
Transcription factor Egr-1 supports FGF-dependent angiogenesis during neovascularization and tumor growth
-
Fahmy RG, Dass CR, Sun LQ, Chesterman CN, Khachigian LM. Transcription factor Egr-1 supports FGF-dependent angiogenesis during neovascularization and tumor growth. Nat Med 2003, 9:1026-32.
-
(2003)
Nat Med
, vol.9
, pp. 1026-1032
-
-
Fahmy, R.G.1
Dass, C.R.2
Sun, L.Q.3
Chesterman, C.N.4
Khachigian, L.M.5
-
79
-
-
39049183025
-
In vitro optimization of antisense oligodeoxynucleotide design: an example using the connexin gene family
-
Law LY, Zhang WV, Stott NS, Becker DL, Green CR. In vitro optimization of antisense oligodeoxynucleotide design: an example using the connexin gene family. J Biomol Tech 2006, 17:270-82.
-
(2006)
J Biomol Tech
, vol.17
, pp. 270-282
-
-
Law, L.Y.1
Zhang, W.V.2
Stott, N.S.3
Becker, D.L.4
Green, C.R.5
-
80
-
-
61349086011
-
Antisense down regulation of connexin31.1 reduces apoptosis and increases thickness of human and animal corneal epithelia
-
Chang CY, Laux-Fenton WT, Law LY, Becker DL, Sherwin T, Green CR. Antisense down regulation of connexin31.1 reduces apoptosis and increases thickness of human and animal corneal epithelia. Cell Biol Int 2009, 33:376-85.
-
(2009)
Cell Biol Int
, vol.33
, pp. 376-385
-
-
Chang, C.Y.1
Laux-Fenton, W.T.2
Law, L.Y.3
Becker, D.L.4
Sherwin, T.5
Green, C.R.6
-
81
-
-
3242891755
-
Bves is expressed in the epithelial components of the retina, lens, and cornea
-
Ripley AN, Chang MS, Bader DM. Bves is expressed in the epithelial components of the retina, lens, and cornea. Invest Ophthalmol Vis Sci 2004, 45:2475-83.
-
(2004)
Invest Ophthalmol Vis Sci
, vol.45
, pp. 2475-2483
-
-
Ripley, A.N.1
Chang, M.S.2
Bader, D.M.3
-
82
-
-
35649027831
-
Inhibition of VEGF expression and corneal neovascularization by siRNA targeting cytochrome P450 4B1
-
Seta F, Patil K, Bellner L. Inhibition of VEGF expression and corneal neovascularization by siRNA targeting cytochrome P450 4B1. Prostaglandins Other Lipid Mediat 2007, 84:116-27.
-
(2007)
Prostaglandins Other Lipid Mediat
, vol.84
, pp. 116-127
-
-
Seta, F.1
Patil, K.2
Bellner, L.3
-
83
-
-
0037966956
-
Inhibition of rat corneal angiogenesis by a nuclease-resistant RNA aptamer specific for angiopoietin-2
-
White RR, Shan S, Rusconi CP. Inhibition of rat corneal angiogenesis by a nuclease-resistant RNA aptamer specific for angiopoietin-2. Proc Natl Acad Sci USA 2003, 100:5028-33.
-
(2003)
Proc Natl Acad Sci USA
, vol.100
, pp. 5028-5033
-
-
White, R.R.1
Shan, S.2
Rusconi, C.P.3
-
84
-
-
0034212434
-
US gene therapy in crisis
-
Teichler Zallen D. US gene therapy in crisis. Trends Genet 2000, 16:272-5.
-
(2000)
Trends Genet
, vol.16
, pp. 272-275
-
-
Teichler Zallen, D.1
-
85
-
-
61849121315
-
Lessons learned from the gene therapy trial for ornithine transcarbamylase deficiency
-
Wilson JM. Lessons learned from the gene therapy trial for ornithine transcarbamylase deficiency. Mol Genet Metab 2009, 96:151-7.
-
(2009)
Mol Genet Metab
, vol.96
, pp. 151-157
-
-
Wilson, J.M.1
-
86
-
-
63449137940
-
Public trust and research a decade later: what have we learned since Jesse Gelsinger's death?
-
Yarborough M, Sharp RR. Public trust and research a decade later: what have we learned since Jesse Gelsinger's death? Mol Genet Metab 2009, 97:4-5.
-
(2009)
Mol Genet Metab
, vol.97
, pp. 4-5
-
-
Yarborough, M.1
Sharp, R.R.2
-
87
-
-
39849105679
-
NIH recombinant DNA Advisory Committee continues to ponder adverse event associated with AAV gene therapy trial
-
Williams DA. NIH recombinant DNA Advisory Committee continues to ponder adverse event associated with AAV gene therapy trial. Mol Ther 2008, 16:427-8.
-
(2008)
Mol Ther
, vol.16
, pp. 427-428
-
-
Williams, D.A.1
-
88
-
-
51349090473
-
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1
-
Hacein-Bey-Abina S, Garrigue A, Wang GP. Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1. J Clin Invest 2008, 118:3132-42.
-
(2008)
J Clin Invest
, vol.118
, pp. 3132-3142
-
-
Hacein-Bey-Abina, S.1
Garrigue, A.2
Wang, G.P.3
-
89
-
-
65249101260
-
The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy
-
Montini E, Cesana D, Schmidt M. The genotoxic potential of retroviral vectors is strongly modulated by vector design and integration site selection in a mouse model of HSC gene therapy. J Clin Invest 2009, 119:964-75.
-
(2009)
J Clin Invest
, vol.119
, pp. 964-975
-
-
Montini, E.1
Cesana, D.2
Schmidt, M.3
-
90
-
-
65249108107
-
Preventing and exploiting the oncogenic potential of integrating gene vectors
-
Modlich U, Baum C. Preventing and exploiting the oncogenic potential of integrating gene vectors. J Clin Invest 2009, 119:755-8.
-
(2009)
J Clin Invest
, vol.119
, pp. 755-758
-
-
Modlich, U.1
Baum, C.2
-
91
-
-
33644820684
-
Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response
-
Manno CS, Pierce GF, Arruda VR. Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response. Nat Med 2006, 12:342-7.
-
(2006)
Nat Med
, vol.12
, pp. 342-347
-
-
Manno, C.S.1
Pierce, G.F.2
Arruda, V.R.3
-
92
-
-
44049108096
-
Manufacturing and characterizing AAV-based vectors for use in clinical studies
-
Wright JF. Manufacturing and characterizing AAV-based vectors for use in clinical studies. Gene Ther 2008, 15:840-8.
-
(2008)
Gene Ther
, vol.15
, pp. 840-848
-
-
Wright, J.F.1
-
93
-
-
77952025832
-
-
The Journal of Gene Medicine Clinical Trial website, updated March 2009. Accessed 12 May 2009. Available from:
-
http://www.wiley.co.uk/genetherapy/clinical/, The Journal of Gene Medicine Clinical Trial website, updated March 2009. Accessed 12 May 2009. Available from:
-
-
-
-
94
-
-
44249120315
-
Effect of gene therapy on visual function in Leber's congenital amaurosis
-
Bainbridge JW, Smith AJ, Barker SS. Effect of gene therapy on visual function in Leber's congenital amaurosis. N Engl J Med 2008, 358:2231-9.
-
(2008)
N Engl J Med
, vol.358
, pp. 2231-2239
-
-
Bainbridge, J.W.1
Smith, A.J.2
Barker, S.S.3
-
95
-
-
44249085878
-
Safety and efficacy of gene transfer for Leber's congenital amaurosis
-
Maguire AM, Simonelli F, Pierce EA. Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med 2008, 358:2240-8.
-
(2008)
N Engl J Med
, vol.358
, pp. 2240-2248
-
-
Maguire, A.M.1
Simonelli, F.2
Pierce, E.A.3
-
96
-
-
54949104686
-
Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial
-
Hauswirth WW, Aleman TS, Kaushal S. Treatment of leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: short-term results of a phase I trial. Hum Gene Ther 2008, 19:979-90.
-
(2008)
Hum Gene Ther
, vol.19
, pp. 979-990
-
-
Hauswirth, W.W.1
Aleman, T.S.2
Kaushal, S.3
-
97
-
-
36048975465
-
Corneal gene therapy
-
Klausner EA, Peer D, Chapman RL, Multack RF, Andurkar SV. Corneal gene therapy. J Control Release 2007, 124:107-33.
-
(2007)
J Control Release
, vol.124
, pp. 107-133
-
-
Klausner, E.A.1
Peer, D.2
Chapman, R.L.3
Multack, R.F.4
Andurkar, S.V.5
|