Lentiviral and adeno-associated vector-based therapy for motor neuron disease through RNAi

Methods in Molecular Biology

Volumn 555, Issue , 2009, Pages 87-108

  Towne, Chris ^a   Aebischer, Patrick ^a  

^a EPFL   (Switzerland)

Author keywords

adeno associated virus (AAV); Amyotrophic lateral sclerosis; G93A SOD1; gene therapy; lentivirus; RNA interference (RNAi); superoxide dismutase (SOD1)

Indexed keywords

ADENO-ASSOCIATED VIRUS; LENTIVIRUS;

COPPER ZINC SUPEROXIDE DISMUTASE; RNA; SUPEROXIDE DISMUTASE;

ADENO ASSOCIATED VIRUS; AMYOTROPHIC LATERAL SCLEROSIS; ANIMAL; ARTICLE; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; INTRAMUSCULAR DRUG ADMINISTRATION; INTRASPINAL DRUG ADMINISTRATION; INVERTED REPEAT; LENTIVIRINAE; METABOLISM; MOUSE; PATHOLOGY; RNA INTERFERENCE; SPINAL CORD;

AMYOTROPHIC LATERAL SCLEROSIS; ANIMALS; DEPENDOVIRUS; GENE THERAPY; GENETIC VECTORS; HUMANS; INJECTIONS, INTRAMUSCULAR; INJECTIONS, SPINAL; INVERTED REPEAT SEQUENCES; LENTIVIRUS; MICE; RNA; RNA INTERFERENCE; SPINAL CORD; SUPEROXIDE DISMUTASE;

EID: 70349319824     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-60327-295-7_7     Document Type: Article

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