-
1
-
-
0029914677
-
Gene transfer into the mouse retina mediated by an adeno-associated viral vector
-
Ali, R.R., Reichel, M.B., Thrasher, A.J., Levinsky, R.J., Kinnon, C., Kanuga, N., Hunt, D.M., and Bhattacharya, S.S. (1996). Gene transfer into the mouse retina mediated by an adeno-associated viral vector. Hum. Mol. Genet. 5, 591-594.
-
(1996)
Hum. Mol. Genet
, vol.5
, pp. 591-594
-
-
Ali, R.R.1
Reichel, M.B.2
Thrasher, A.J.3
Levinsky, R.J.4
Kinnon, C.5
Kanuga, N.6
Hunt, D.M.7
Bhattacharya, S.S.8
-
2
-
-
0033947697
-
Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy
-
Ali, R.R., Sarra, G.M., Stephens, C., Alwis, M.D., Bainbridge, J.W., Munro, P.M., Fauser, S., Reichel, M.B., Kinnon, C., Hunt, D.M., Bhattacharya, S.S., and Thrasher, A.J. (2000). Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy. Nat. Genet. 25, 306-310.
-
(2000)
Nat. Genet
, vol.25
, pp. 306-310
-
-
Ali, R.R.1
Sarra, G.M.2
Stephens, C.3
Alwis, M.D.4
Bainbridge, J.W.5
Munro, P.M.6
Fauser, S.7
Reichel, M.B.8
Kinnon, C.9
Hunt, D.M.10
Bhattacharya, S.S.11
Thrasher, A.J.12
-
3
-
-
44249120315
-
Effect of gene therapy on visual function in Leber's congenital amaurosis
-
Bainbridge, J.W., Smith, A.J., Barker, S.S., Robbie, S., Henderson, R., Balaggan, K., Viswanathan, A., Holder, G.E., Stockman, A., Tyler, N., Petersen-Jones, S., Bhattacharya, S.S., Thrasher, A.J., Fitzke, F.W., Carter, B.J., Rubin, G.S., Moore, A.T., and Ali, R.R. (2008). Effect of gene therapy on visual function in Leber's congenital amaurosis. N. Engl. J. Med. 358, 2231-2239.
-
(2008)
N. Engl. J. Med
, vol.358
, pp. 2231-2239
-
-
Bainbridge, J.W.1
Smith, A.J.2
Barker, S.S.3
Robbie, S.4
Henderson, R.5
Balaggan, K.6
Viswanathan, A.7
Holder, G.E.8
Stockman, A.9
Tyler, N.10
Petersen-Jones, S.11
Bhattacharya, S.S.12
Thrasher, A.J.13
Fitzke, F.W.14
Carter, B.J.15
Rubin, G.S.16
Moore, A.T.17
Ali, R.R.18
-
4
-
-
0347651828
-
Pigment epithelium-derived factor in the monkey retinal pigment epithelium and interphotoreceptor matrix: Apical secretion and distribution
-
Becerra, S.P., Fariss, R.N., Wu, Y.Q., Montuenga, L.M., Wong, P., and Pfeffer, B.A. (2004). Pigment epithelium-derived factor in the monkey retinal pigment epithelium and interphotoreceptor matrix: Apical secretion and distribution. Exp. Eye Res. 78, 223-234.
-
(2004)
Exp. Eye Res
, vol.78
, pp. 223-234
-
-
Becerra, S.P.1
Fariss, R.N.2
Wu, Y.Q.3
Montuenga, L.M.4
Wong, P.5
Pfeffer, B.A.6
-
5
-
-
57749093004
-
Pigment epithelium-derived factor binds to hyaluronan: Mapping of a hyaluronan binding site
-
Becerra, S.P., Perez-Mediavilla, L.A., Weldon, J.E., Locatelli-Hoops, S., Senanayake, P., Notari, L., Notario, V., and Hollyfield, J.G. (2008). Pigment epithelium-derived factor binds to hyaluronan: Mapping of a hyaluronan binding site. J. Biol. Chem. 283, 33310-33320.
-
(2008)
J. Biol. Chem
, vol.283
, pp. 33310-33320
-
-
Becerra, S.P.1
Perez-Mediavilla, L.A.2
Weldon, J.E.3
Locatelli-Hoops, S.4
Senanayake, P.5
Notari, L.6
Notario, V.7
Hollyfield, J.G.8
-
6
-
-
0028280660
-
Adenovirus vector-mediated in vivo gene transfer into adult murine retina
-
Bennett, J., Wilson, J., Sun, D., Forbes, B., and Maguire, A. (1994). Adenovirus vector-mediated in vivo gene transfer into adult murine retina. Invest. Ophthalmol. Vis. Sci. 35, 2535-2542.
-
(1994)
Invest. Ophthalmol. Vis. Sci
, vol.35
, pp. 2535-2542
-
-
Bennett, J.1
Wilson, J.2
Sun, D.3
Forbes, B.4
Maguire, A.5
-
7
-
-
13044256410
-
Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina
-
Bennett, J., Maguire, A.M., Cideciyan, A.V., Schnell, M., Glover, E., Anand, V., Aleman, T.S., Chirmule, N., Gupta, A.R., Huang, Y., Gao, G.P., Nyberg, W.C., Tazelaar, J., Hughes, J., Wilson, J.M., and Jacobson, S.G. (1999). Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina. Proc. Natl. Acad. Sci. U.S.A. 96, 9920-9925.
-
(1999)
Proc. Natl. Acad. Sci. U.S.A
, vol.96
, pp. 9920-9925
-
-
Bennett, J.1
Maguire, A.M.2
Cideciyan, A.V.3
Schnell, M.4
Glover, E.5
Anand, V.6
Aleman, T.S.7
Chirmule, N.8
Gupta, A.R.9
Huang, Y.10
Gao, G.P.11
Nyberg, W.C.12
Tazelaar, J.13
Hughes, J.14
Wilson, J.M.15
Jacobson, S.G.16
-
8
-
-
31644447744
-
Response of retinoblastoma with vitreous tumor seeding to adenovirus-mediated delivery of thymidine kinase followed by ganciclovir
-
Chévez-Barrios, P., Chintagumpala, M., Mieler, W., Paysse, E., Boniuk, M., Kozinetz, C., Hurwitz, M.Y., and Hurwitz, R.L. (2005). Response of retinoblastoma with vitreous tumor seeding to adenovirus-mediated delivery of thymidine kinase followed by ganciclovir. J. Clin. Oncol. 23, 7927-7935.
-
(2005)
J. Clin. Oncol
, vol.23
, pp. 7927-7935
-
-
Chévez-Barrios, P.1
Chintagumpala, M.2
Mieler, W.3
Paysse, E.4
Boniuk, M.5
Kozinetz, C.6
Hurwitz, M.Y.7
Hurwitz, R.L.8
-
9
-
-
0036797278
-
Five recombinant simian immunodeficiency virus pseudotypes lead to exclusive transduction of retinal pigmented epithelium in rat
-
Duisit, G., Conrath, H., Saleun, S., Folliot, S., Provost, N., Cosset, F.L., Sandrin, V., Moullier, P., and Rolling, F. (2002). Five recombinant simian immunodeficiency virus pseudotypes lead to exclusive transduction of retinal pigmented epithelium in rat. Mol. Ther. 6, 446-454.
-
(2002)
Mol. Ther
, vol.6
, pp. 446-454
-
-
Duisit, G.1
Conrath, H.2
Saleun, S.3
Folliot, S.4
Provost, N.5
Cosset, F.L.6
Sandrin, V.7
Moullier, P.8
Rolling, F.9
-
10
-
-
0031011667
-
Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus
-
Flannery, J.G., Zolotukhin, S., Vaquero, M.I., LaVail, M.M., Muzyczka, N., and Hauswirth, W.W. (1997). Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus. Proc. Natl. Acad. Sci. U.S.A. 94, 6916-6921.
-
(1997)
Proc. Natl. Acad. Sci. U.S.A
, vol.94
, pp. 6916-6921
-
-
Flannery, J.G.1
Zolotukhin, S.2
Vaquero, M.I.3
LaVail, M.M.4
Muzyczka, N.5
Hauswirth, W.W.6
-
11
-
-
20744444135
-
Lentiviral vector-mediated gene transfer in adult mouse photoreceptors is impaired by the presence of a physical barrier
-
Gruter, O., Kostic, C., Crippa, S.V., Perez, M.T., Zografos, L., Schorderet, D.F., Munier, F.L., and Arsenijevic, Y. (2005). Lentiviral vector-mediated gene transfer in adult mouse photoreceptors is impaired by the presence of a physical barrier. Gene Ther. 12, 942-947.
-
(2005)
Gene Ther
, vol.12
, pp. 942-947
-
-
Gruter, O.1
Kostic, C.2
Crippa, S.V.3
Perez, M.T.4
Zografos, L.5
Schorderet, D.F.6
Munier, F.L.7
Arsenijevic, Y.8
-
12
-
-
0021909758
-
The Japanese Tsukuba Primate Center for Medical Science (TPC): An outline
-
Honjo, S. (1985). The Japanese Tsukuba Primate Center for Medical Science (TPC): An outline. J. Med. Primatol. 14, 75-89.
-
(1985)
J. Med. Primatol
, vol.14
, pp. 75-89
-
-
Honjo, S.1
-
13
-
-
0035996270
-
Recombinant Sendai virus-mediated gene transfer into adult rat retinal tissue: Efficient gene transfer by brief exposure
-
Ikeda, Y., Yonemitsu, Y., Sakamoto, T., Ishibashi, T., Ueno, H., Kato, A., Nagai, Y., Fukumura, M., Inomata, H., Hasegawa, M., and Sueishi, K. (2002). Recombinant Sendai virus-mediated gene transfer into adult rat retinal tissue: Efficient gene transfer by brief exposure. Exp. Eye Res. 75, 39-48.
-
(2002)
Exp. Eye Res
, vol.75
, pp. 39-48
-
-
Ikeda, Y.1
Yonemitsu, Y.2
Sakamoto, T.3
Ishibashi, T.4
Ueno, H.5
Kato, A.6
Nagai, Y.7
Fukumura, M.8
Inomata, H.9
Hasegawa, M.10
Sueishi, K.11
-
14
-
-
0042810885
-
Simian immunodeficiency virus-based lentivirus vector for retinal gene transfer: A preclinical safety study in adult rats
-
Ikeda, Y., Goto, Y., Yonemitsu, Y., Miyazaki, M., Sakamoto, T., Ishibashi, T., Tabata, T., Ueda, Y., Hasegawa, M., Tobimatsu, S., and Sueishi, K. (2003). Simian immunodeficiency virus-based lentivirus vector for retinal gene transfer: A preclinical safety study in adult rats. Gene Ther. 10, 1161-1169.
-
(2003)
Gene Ther
, vol.10
, pp. 1161-1169
-
-
Ikeda, Y.1
Goto, Y.2
Yonemitsu, Y.3
Miyazaki, M.4
Sakamoto, T.5
Ishibashi, T.6
Tabata, T.7
Ueda, Y.8
Hasegawa, M.9
Tobimatsu, S.10
Sueishi, K.11
-
15
-
-
16844385431
-
Postsurgical assessment and long-term safety of recombinant adeno-associated virus-mediated gene transfer into the retinas of dogs and primates
-
Le Meur, G., Weber, M., Péréon, Y., Mendes-Madeira, A., Nivard, D., Deschamps, J.Y., Moullier, P., and Rolling, F. (2005). Postsurgical assessment and long-term safety of recombinant adeno-associated virus-mediated gene transfer into the retinas of dogs and primates. Arch. Ophthalmol. 123, 500-506.
-
(2005)
Arch. Ophthalmol
, vol.123
, pp. 500-506
-
-
Le Meur, G.1
Weber, M.2
Péréon, Y.3
Mendes-Madeira, A.4
Nivard, D.5
Deschamps, J.Y.6
Moullier, P.7
Rolling, F.8
-
16
-
-
0036204263
-
Gene transfer to the nonhuman primate retina with recombinant feline immunodeficiency virus vectors
-
Lotery, A.J., Derksen, T.A., Russell, S.R., Mullins, R.F., Sauter, S., Affatigato, L.M., Stone, E.M., and Davidson, B.L. (2002). Gene transfer to the nonhuman primate retina with recombinant feline immunodeficiency virus vectors. Hum. Gene Ther. 13, 689-696.
-
(2002)
Hum. Gene Ther
, vol.13
, pp. 689-696
-
-
Lotery, A.J.1
Derksen, T.A.2
Russell, S.R.3
Mullins, R.F.4
Sauter, S.5
Affatigato, L.M.6
Stone, E.M.7
Davidson, B.L.8
-
17
-
-
10744225428
-
Adeno-associated virus type 5: Transduction efficiency and cell-type specificity in the primate retina
-
Lotery, A.J., Yang, G.S., Mullins, R.F., Russell, S.R., Schmidt, M., Stone, E.M., Lindbloom, J.D., Chiorini, J.A., Kotin, R.M., and Davidson, B.L. (2003). Adeno-associated virus type 5: Transduction efficiency and cell-type specificity in the primate retina. Hum. Gene Ther. 14, 1663-1671.
-
(2003)
Hum. Gene Ther
, vol.14
, pp. 1663-1671
-
-
Lotery, A.J.1
Yang, G.S.2
Mullins, R.F.3
Russell, S.R.4
Schmidt, M.5
Stone, E.M.6
Lindbloom, J.D.7
Chiorini, J.A.8
Kotin, R.M.9
Davidson, B.L.10
-
18
-
-
85119782536
-
-
Maguire, A.M., Simonelli, F., Pierce, E.A., Pugh, E.N., Jr., Mingozzi, F., Bennicelli, J., Banfi, S., Marshall, K.A., Testa, F., Surace, E.M., Rossi, S., Lyubarsky, A., Arruda, V.R., Konkle, B., Stone, E., Sun, J., Jacobs, J., Dell'Osso, L., Hertle, R., Ma, J.X., Redmond, T.M., Zhu, X., Hauck, B., Zelenaia, O., Shindler, K.S., Maguire, M.G., Wright, J.F., Volpe, N.J., McDonnell, J.W., Auricchio, A., High, K.A., and Bennett, J. (2008). Safety and efficacy of gene transfer for Leber's congenital amaurosis. N. Engl. J. Med. 358, 2240-2248.
-
Maguire, A.M., Simonelli, F., Pierce, E.A., Pugh, E.N., Jr., Mingozzi, F., Bennicelli, J., Banfi, S., Marshall, K.A., Testa, F., Surace, E.M., Rossi, S., Lyubarsky, A., Arruda, V.R., Konkle, B., Stone, E., Sun, J., Jacobs, J., Dell'Osso, L., Hertle, R., Ma, J.X., Redmond, T.M., Zhu, X., Hauck, B., Zelenaia, O., Shindler, K.S., Maguire, M.G., Wright, J.F., Volpe, N.J., McDonnell, J.W., Auricchio, A., High, K.A., and Bennett, J. (2008). Safety and efficacy of gene transfer for Leber's congenital amaurosis. N. Engl. J. Med. 358, 2240-2248.
-
-
-
-
19
-
-
0042025129
-
Simian lentiviral vector-mediated retinal gene transfer of pigment epithelium-derived factor protects retinal degeneration and electrical defect in Royal College of Surgeons rats
-
Miyazaki, M., Ikeda, Y., Yonemitsu, Y., Goto, Y., Sakamoto, T., Tabata, T., Ueda, Y., Hasegawa, M., Tobimatsu, S., Ishibashi, T., and Sueishi, K. (2003). Simian lentiviral vector-mediated retinal gene transfer of pigment epithelium-derived factor protects retinal degeneration and electrical defect in Royal College of Surgeons rats. Gene Ther. 10, 1503-1511.
-
(2003)
Gene Ther
, vol.10
, pp. 1503-1511
-
-
Miyazaki, M.1
Ikeda, Y.2
Yonemitsu, Y.3
Goto, Y.4
Sakamoto, T.5
Tabata, T.6
Ueda, Y.7
Hasegawa, M.8
Tobimatsu, S.9
Ishibashi, T.10
Sueishi, K.11
-
20
-
-
58949084050
-
Synergistic neuroprotective effect via simian lentiviral vector-mediated simultaneous gene transfer of human pigment epithelium-derived factor and human fibroblast growth factor-2 in rodent models of retinitis pigmentosa
-
Miyazaki, M., Ikeda, Y., Yonemitsu, Y., Goto, Y., Kohno, R., Murakami, Y., Inoue, M., Ueda, Y., Hasegawa, M., Tobimatsu, S., Sueishi, K., and Ishibashi, T. (2008). Synergistic neuroprotective effect via simian lentiviral vector-mediated simultaneous gene transfer of human pigment epithelium-derived factor and human fibroblast growth factor-2 in rodent models of retinitis pigmentosa. J. Gene Med. 10, 1273-1381.
-
(2008)
J. Gene Med
, vol.10
, pp. 1273-1381
-
-
Miyazaki, M.1
Ikeda, Y.2
Yonemitsu, Y.3
Goto, Y.4
Kohno, R.5
Murakami, Y.6
Inoue, M.7
Ueda, Y.8
Hasegawa, M.9
Tobimatsu, S.10
Sueishi, K.11
Ishibashi, T.12
-
21
-
-
0030931963
-
Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector
-
Miyoshi, H., Takahashi, M., Gage, F.H., and Verma, I.M. (1997). Stable and efficient gene transfer into the retina using an HIV-based lentiviral vector. Proc. Natl. Acad. Sci. U.S.A. 94, 10319-10323.
-
(1997)
Proc. Natl. Acad. Sci. U.S.A
, vol.94
, pp. 10319-10323
-
-
Miyoshi, H.1
Takahashi, M.2
Gage, F.H.3
Verma, I.M.4
-
22
-
-
55349146967
-
Inhibition of nuclear translocation of apoptosis-inducing factor is an essential mechanism of the neuroprotective activity of pigment epithelium-derived factor in a rat model of retinal degeneration
-
Murakami, Y., Ikeda, Y., Yonemitsu, Y., Onimaru, M., Nakagawa, K., Kohno, R., Miyazaki, M., Hisatomi, T., Nakamura, M., Yabe, T., Hasegawa, M., Ishibashi, T., and Sueishi, K. (2008). Inhibition of nuclear translocation of apoptosis-inducing factor is an essential mechanism of the neuroprotective activity of pigment epithelium-derived factor in a rat model of retinal degeneration. Am. J. Pathol. 173, 1326-1338.
-
(2008)
Am. J. Pathol
, vol.173
, pp. 1326-1338
-
-
Murakami, Y.1
Ikeda, Y.2
Yonemitsu, Y.3
Onimaru, M.4
Nakagawa, K.5
Kohno, R.6
Miyazaki, M.7
Hisatomi, T.8
Nakamura, M.9
Yabe, T.10
Hasegawa, M.11
Ishibashi, T.12
Sueishi, K.13
-
23
-
-
0034283881
-
Development of novel simian immunodeficiency virus vectors carrying a dual gene expression system
-
Nakajima, T., Nakamaru, K., Ido, E., Terao, K., Hayami, M., and Hasegawa, M. (2000). Development of novel simian immunodeficiency virus vectors carrying a dual gene expression system. Hum. Gene Ther. 11, 1863-1874.
-
(2000)
Hum. Gene Ther
, vol.11
, pp. 1863-1874
-
-
Nakajima, T.1
Nakamaru, K.2
Ido, E.3
Terao, K.4
Hayami, M.5
Hasegawa, M.6
-
24
-
-
2942585114
-
Decreased levels of pigment epithelium-derived factor in eyes with neuroretinal dystrophic diseases
-
Ogata, N., Matsuoka, M., Imaizumi, M., Arichi, M., and Matsumura, M. (2004). Decreased levels of pigment epithelium-derived factor in eyes with neuroretinal dystrophic diseases. Am. J. Ophthalmol. 137, 1129-1130.
-
(2004)
Am. J. Ophthalmol
, vol.137
, pp. 1129-1130
-
-
Ogata, N.1
Matsuoka, M.2
Imaizumi, M.3
Arichi, M.4
Matsumura, M.5
-
25
-
-
33845648448
-
Efficient expression of a transgene in platelets using simian immunodeficiency virus-based vector harboring glycoprotein Iba promoter: In vivo model for platelet-targeting gene therapy
-
Ohmori, T., Mimuro, J., Takano, K., Madoiwa, S., Kashiwakura, Y., Ishiwata, A., Niimura, M., Mitomo, K., Tabata, T., Hasegawa, M., Ozawa, K., and Sakata, Y. (2006). Efficient expression of a transgene in platelets using simian immunodeficiency virus-based vector harboring glycoprotein Iba promoter: In vivo model for platelet-targeting gene therapy. FASEB J. 20, 1522-1524.
-
(2006)
FASEB J
, vol.20
, pp. 1522-1524
-
-
Ohmori, T.1
Mimuro, J.2
Takano, K.3
Madoiwa, S.4
Kashiwakura, Y.5
Ishiwata, A.6
Niimura, M.7
Mitomo, K.8
Tabata, T.9
Hasegawa, M.10
Ozawa, K.11
Sakata, Y.12
-
26
-
-
0005197246
-
Guiding principles for animal experiments using nonhuman primates
-
Primate Society of Japan, in Japanese
-
Primate Society of Japan. (1986). Guiding principles for animal experiments using nonhuman primates [in Japanese]. Primate Res. 2, 111-113.
-
(1986)
Primate Res
, vol.2
, pp. 111-113
-
-
-
27
-
-
0035514256
-
Clinical protocol: An open-label, phase I, single administration, dose-escalation study of ADGVPEDF.11D (ADPEDF) in neovascular age-related macular degeneration (AMD)
-
Rasmussen, H., Chu, K.W., Campochiaro, P., Gehlbach, P.L., Haller, J.A., Handa, J.T., Nguyen, Q.D., and Sung, J.U. (2001). Clinical protocol: An open-label, phase I, single administration, dose-escalation study of ADGVPEDF.11D (ADPEDF) in neovascular age-related macular degeneration (AMD). Hum. Gene Ther. 12, 2029-2032.
-
(2001)
Hum. Gene Ther
, vol.12
, pp. 2029-2032
-
-
Rasmussen, H.1
Chu, K.W.2
Campochiaro, P.3
Gehlbach, P.L.4
Haller, J.A.5
Handa, J.T.6
Nguyen, Q.D.7
Sung, J.U.8
-
28
-
-
0032503015
-
Retinal functional change caused by adenoviral vector-mediated transfection of LacZ gene
-
Sakamoto, T., Ueno, H., Goto, Y., Oshima, Y., Yamanaka, I., Ishibashi, T., and Inomata, H. (1998). Retinal functional change caused by adenoviral vector-mediated transfection of LacZ gene. Hum. Gene Ther. 9, 789-799.
-
(1998)
Hum. Gene Ther
, vol.9
, pp. 789-799
-
-
Sakamoto, T.1
Ueno, H.2
Goto, Y.3
Oshima, Y.4
Yamanaka, I.5
Ishibashi, T.6
Inomata, H.7
-
29
-
-
0029025831
-
Expression, secretion, and age-related downregulation of pigment epithelium-derived factor, a serpin with neurotrophic activity
-
Tombran-Tink, J., Shivaram, S.M., Chader, G.J., Johnson, L.V., and Bok, D. (1995). Expression, secretion, and age-related downregulation of pigment epithelium-derived factor, a serpin with neurotrophic activity. J. Neurosci. 15, 4992-5003.
-
(1995)
J. Neurosci
, vol.15
, pp. 4992-5003
-
-
Tombran-Tink, J.1
Shivaram, S.M.2
Chader, G.J.3
Johnson, L.V.4
Bok, D.5
-
30
-
-
0029347070
-
Identification of pigment epithelium-derived factor in the interphotoreceptor matrix of bovine eyes
-
Wu, Y.Q., Notario, V., Chader, G.J., and Becerra, S.P. (1995). Identification of pigment epithelium-derived factor in the interphotoreceptor matrix of bovine eyes. Protein Expr. Purif. 6, 447-456.
-
(1995)
Protein Expr. Purif
, vol.6
, pp. 447-456
-
-
Wu, Y.Q.1
Notario, V.2
Chader, G.J.3
Becerra, S.P.4
|