Prevention of oculopharyngeal muscular dystrophy by muscular expression of Llama single-chain intrabodies in vivo

Human Molecular Genetics

Volumn 18, Issue 10, 2009, Pages 1849-1859

  Chartier, Aymeric ^a   Raz, Vered ^b   Sterrenburg, Ellen ^b   Verrips, C Theo ^c   van der Maarel, Silvère M ^b   Simonelig, Martine ^a  

^a INSTITUTE OF HUMAN GENETICS   (France)

^b LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^c UTRECHT UNIVERSITY   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

BINDING PROTEIN; CELL ANTIBODY; LLAMA ANTIBODY; POLYADENYLIC ACID BINDING PROTEIN NUCLEAR 1; UNCLASSIFIED DRUG;

ARTICLE; CONTROLLED STUDY; DROSOPHILA; GENE REPRESSION; GENETIC IDENTIFICATION; IN VIVO STUDY; NONHUMAN; OCULOPHARYNGEAL MUSCULAR DYSTROPHY; PATHOGENESIS; PRIORITY JOURNAL; PROTEIN AGGREGATION; PROTEIN EXPRESSION; PROTEIN FUNCTION;

ANIMALS; ANTIBODIES, MONOCLONAL; CAMELIDS, NEW WORLD; DISEASE MODELS, ANIMAL; DROSOPHILA; FEMALE; GENE THERAPY; HUMANS; IMMUNOTHERAPY; MALE; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, OCULOPHARYNGEAL; POLY(A)-BINDING PROTEIN II; PROTEIN TRANSPORT;

ANIMALIA; CAMELIDAE; LAMA (MAMMAL);

EID: 65449169579     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddp101     Document Type: Article

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