Long-term correction of murine lipoprotein lipase deficiency with AAV1-mediated gene transfer of the naturally occurring LPLS447X beneficial mutation

Human Gene Therapy

Volumn 15, Issue 9, 2004, Pages 906-919

  Ross, Colin J D ^a   Twisk, Jaap ^b   Meulenberg, Janneke M ^b   Liu, Guoqing ^a   Van Den Oever, Karin ^c   Moraal, Ewoud ^b   Hermens, Wim T ^b   Rip, Jaap ^c   Kastelein, John J P ^c   Kuivenhoven, Jan Albert ^c   Hayden, Michael R ^a,d  

^a UNIVERSITY OF BRITISH COLUMBIA   (Canada)

^b Amsterdam Molecular Therapeutics   (Netherlands)

^c UNIVERSITY OF AMSTERDAM   (Netherlands)

^d Centre for Molecular Medicine and Therapeutics   (Canada)

Author keywords

[No Author keywords available]

Indexed keywords

LIPOPROTEIN LIPASE;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BLOOD SAMPLING; CHOLESTEROL BLOOD LEVEL; CONTROLLED STUDY; DOSE RESPONSE; ENZYME ACTIVITY; GENE MUTATION; GENE TRANSFER; HISTOLOGY; HYPERLIPIDEMIA; HYPERLIPOPROTEINEMIA TYPE 1; LIPID BLOOD LEVEL; MALE; MOUSE; MUSCLE DISEASE; NONHUMAN; PROTEIN EXPRESSION; TRIACYLGLYCEROL BLOOD LEVEL;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MURINAE;

EID: 4544326444     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2004.15.906     Document Type: Article

References (40)

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