메뉴 건너뛰기




Volumn 15, Issue 6, 2007, Pages 1079-1085

Erratum: Retraction to metabolic basis of sexual dimorphism in PKU mice after genome-targeted PAH gene therapy (Molecular Therapy (2007) 15:6 (1079-1085) DOI: 10.1038/sj.mt.6300137);Metabolic basis of sexual dimorphism in PKU mice after genome-targeted PAH gene therapy

Author keywords

[No Author keywords available]

Indexed keywords

ANDROSTANOLONE; ESTRADIOL; PHENYLALANINE; PHENYLALANINE 4 MONOOXYGENASE; TETRAHYDROBIOPTERIN;

EID: 34249290419     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2010.198     Document Type: Erratum
Times cited : (11)

References (39)
  • 1
    • 0028888322 scopus 로고
    • Molecular genetics of phenylketonuria: From molecular anthropology to gene therapy
    • Eisensmith, RC and Woo, SL (1995). Molecular genetics of phenylketonuria: From molecular anthropology to gene therapy. Adv Genet 32: 199-271.
    • (1995) Adv Genet , vol.32 , pp. 199-271
    • Eisensmith, R.C.1    Woo, S.L.2
  • 2
    • 0028464358 scopus 로고
    • Gene therapy for phenylketonuria: Phenotypic correction in a genetically deficient mouse model by adenovirus-mediated hepatic gene transfer
    • Fang, B, Eisensmith, RC, Li, XH, Finegold, MJ, Shedlovsky, A, Dove, W et al. (1994). Gene therapy for phenylketonuria: Phenotypic correction in a genetically deficient mouse model by adenovirus-mediated hepatic gene transfer. Gene Ther 1: 247-254.
    • (1994) Gene Ther , vol.1 , pp. 247-254
    • Fang, B.1    Eisensmith, R.C.2    Li, X.H.3    Finegold, M.J.4    Shedlovsky, A.5    Dove, W.6
  • 3
    • 0023787380 scopus 로고
    • Retroviral-mediated gene transfer and expression of human phenylalanine hydroxylase in primary mouse hepatocytes
    • Peng, H, Armentano, D, MacKenzie-Graham, L, Shen, RF, Darlington, G, Ledley, FD et al. (1988). Retroviral-mediated gene transfer and expression of human phenylalanine hydroxylase in primary mouse hepatocytes. Proc Natl Acad Sci USA 85: 8146-8150.
    • (1988) Proc Natl Acad Sci USA , vol.85 , pp. 8146-8150
    • Peng, H.1    Armentano, D.2    MacKenzie-Graham, L.3    Shen, R.F.4    Darlington, G.5    Ledley, F.D.6
  • 4
    • 0034012174 scopus 로고    scopus 로고
    • A heteroallelic mutant mouse model: A new orthologue for human hyperphenylalaninemia
    • Sarkissian, CN, Boulais, DM, McDonald, JD and Scriver, CR (2000). A heteroallelic mutant mouse model: A new orthologue for human hyperphenylalaninemia. Mol Genet Metab 69: 188-194.
    • (2000) Mol Genet Metab , vol.69 , pp. 188-194
    • Sarkissian, C.N.1    Boulais, D.M.2    McDonald, J.D.3    Scriver, C.R.4
  • 5
    • 33645098770 scopus 로고    scopus 로고
    • Administration-route and gender-independent long-term therapeutic correction of phenylketonuria (PKU) in a mouse model by recombinant adeno-associated virus 8 pseudotyped vector-mediated gene transfer
    • Ding, Z, Georgiev, P and Thony, B (2006). Administration-route and gender-independent long-term therapeutic correction of phenylketonuria (PKU) in a mouse model by recombinant adeno-associated virus 8 pseudotyped vector-mediated gene transfer. Gene Ther 13: 587-593.
    • (2006) Gene Ther , vol.13 , pp. 587-593
    • Ding, Z.1    Georgiev, P.2    Thony, B.3
  • 6
    • 3242766095 scopus 로고    scopus 로고
    • Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice
    • Mochizuki, S, Mizukami, H, Ogura, T, Kure, S, Ichinohe, A, Kojima, K et al. (2004). Long-term correction of hyperphenylalaninemia by AAV-mediated gene transfer leads to behavioral recovery in phenylketonuria mice. Gene Ther 11: 1081-1086.
    • (2004) Gene Ther , vol.11 , pp. 1081-1086
    • Mochizuki, S.1    Mizukami, H.2    Ogura, T.3    Kure, S.4    Ichinohe, A.5    Kojima, K.6
  • 7
    • 3242778717 scopus 로고    scopus 로고
    • Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer
    • Oh, HJ, Park, ES, Kang, S, Jo, I and Jung, SC (2004). Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer. Pediatr Res 56: 278-284.
    • (2004) Pediatr Res , vol.56 , pp. 278-284
    • Oh, H.J.1    Park, E.S.2    Kang, S.3    Jo, I.4    Jung, S.C.5
  • 8
    • 27344439351 scopus 로고    scopus 로고
    • Complete and persistent phenotypic correction of phenylketonuria in mice by site-specific genome integration of murine phenylalanine hydroxylase cDNA
    • Chen, L and Woo, SL (2005). Complete and persistent phenotypic correction of phenylketonuria in mice by site-specific genome integration of murine phenylalanine hydroxylase cDNA. Proc Natl Acad Sci USA 102: 15581-15586.
    • (2005) Proc Natl Acad Sci USA , vol.102 , pp. 15581-15586
    • Chen, L.1    Woo, S.L.2
  • 9
    • 0032510752 scopus 로고    scopus 로고
    • In vitro site-specific integration of bacteriophage DNA catalyzed by a recombinase of the resolvase/invertase family
    • Thorpe, HM and Smith, MC (1998). In vitro site-specific integration of bacteriophage DNA catalyzed by a recombinase of the resolvase/invertase family. Proc Natl Acad Sci USA 95: 5505-5510.
    • (1998) Proc Natl Acad Sci USA , vol.95 , pp. 5505-5510
    • Thorpe, H.M.1    Smith, M.C.2
  • 10
    • 0035008830 scopus 로고    scopus 로고
    • Site-specific genomic integration in mammalian cells mediated by phage phiC31 integrase
    • Thyagarajan, B, Olivares, EC, Hollis, RP, Ginsburg, DS and Calos, MP (2001). Site-specific genomic integration in mammalian cells mediated by phage phiC31 integrase. Mol Cell Biol 21: 3926-3934.
    • (2001) Mol Cell Biol , vol.21 , pp. 3926-3934
    • Thyagarajan, B.1    Olivares, E.C.2    Hollis, R.P.3    Ginsburg, D.S.4    Calos, M.P.5
  • 11
    • 0036283336 scopus 로고    scopus 로고
    • Phage TP901-1 site-specific integrase functions in human cells
    • Stoll, SM, Ginsburg, DS and Calos, MP (2002). Phage TP901-1 site-specific integrase functions in human cells. J Bacteriol 184: 3657-3663.
    • (2002) J Bacteriol , vol.184 , pp. 3657-3663
    • Stoll, S.M.1    Ginsburg, D.S.2    Calos, M.P.3
  • 12
    • 0035980679 scopus 로고    scopus 로고
    • Phage R4 integrase mediates site-specific integration in human cells
    • Olivares, EC, Hollis, RP and Calos, MP (2001). Phage R4 integrase mediates site-specific integration in human cells. Gene 278: 167-176.
    • (2001) Gene , vol.278 , pp. 167-176
    • Olivares, E.C.1    Hollis, R.P.2    Calos, M.P.3
  • 13
    • 0036209004 scopus 로고    scopus 로고
    • Construction of an integration-proficient vector based on the site-specific recombination mechanism of enterococcal temperate phage phiFC1
    • Yang, HY, Kim, YW and Chang, HI (2002). Construction of an integration-proficient vector based on the site-specific recombination mechanism of enterococcal temperate phage phiFC1. J Bacteriol 184: 1859-1864.
    • (2002) J Bacteriol , vol.184 , pp. 1859-1864
    • Yang, H.Y.1    Kim, Y.W.2    Chang, H.I.3
  • 14
    • 30944462461 scopus 로고    scopus 로고
    • Transgenic Xenopus laevis embryos can be generated using phiC31 integrase
    • Allen, BG and Weeks, DL (2005). Transgenic Xenopus laevis embryos can be generated using phiC31 integrase. Nat Methods 2: 975-979.
    • (2005) Nat Methods , vol.2 , pp. 975-979
    • Allen, B.G.1    Weeks, D.L.2
  • 15
    • 0037337299 scopus 로고    scopus 로고
    • Site-specific cassette exchange and germline transmission with mouse ES cells expressing phiC31 integrase
    • Belteki, G, Gertsenstein, M, Ow, DW and Nagy, A (2003). Site-specific cassette exchange and germline transmission with mouse ES cells expressing phiC31 integrase. Nat Biotechnol 21: 321-324.
    • (2003) Nat Biotechnol , vol.21 , pp. 321-324
    • Belteki, G.1    Gertsenstein, M.2    Ow, D.W.3    Nagy, A.4
  • 16
    • 22144464502 scopus 로고    scopus 로고
    • phiC31 integrase confers genomic integration and long-term transgene expression in rat retina
    • Chalberg, TW, Genise, HL, Vollrath, D and Calos, MP (2005). phiC31 integrase confers genomic integration and long-term transgene expression in rat retina. Invest Ophthalmol Vis Sci 46: 2140-2146.
    • (2005) Invest Ophthalmol Vis Sci , vol.46 , pp. 2140-2146
    • Chalberg, T.W.1    Genise, H.L.2    Vollrath, D.3    Calos, M.P.4
  • 18
    • 31144443605 scopus 로고    scopus 로고
    • Iterative in vivo assembly of large and complex transgenes by combining the activities of phiC31 integrase and Cre recombinase
    • Dafhnis-Calas, F, Xu, Z, Hanines, S, Malla, SK, Smith, MC and Brown, WR (2005). Iterative in vivo assembly of large and complex transgenes by combining the activities of phiC31 integrase and Cre recombinase. Nucleic Acids Res 33: E189.
    • (2005) Nucleic Acids Res , vol.33
    • Dafhnis-Calas, F.1    Xu, Z.2    Hanines, S.3    Malla, S.K.4    Smith, M.C.5    Brown, W.R.6
  • 19
    • 17644425657 scopus 로고    scopus 로고
    • A direct comparison of two nonviral gene therapy vectors for somatic integration: In vivo evaluation of the bacteriophage integrase phiC31 and the sleeping beauty transposase
    • Ehrhardt A, Xu, H, Huang, Z, Engler, JA and Kay, MA (2005). A direct comparison of two nonviral gene therapy vectors for somatic integration: in vivo evaluation of the bacteriophage integrase phiC31 and the sleeping beauty transposase. Mol Ther 11: 695-706.
    • (2005) Mol Ther , vol.11 , pp. 695-706
    • Ehrhardt, A.1    Xu, H.2    Huang, Z.3    Engler, J.A.4    Kay, M.A.5
  • 20
    • 25144432005 scopus 로고    scopus 로고
    • Site-specific integration with phiC31 integrase for prolonged expression of therapeutic genes
    • Ginsburg, DS and Calos, MP (2005). Site-specific integration with phiC31 integrase for prolonged expression of therapeutic genes. Adv Genet 54: 179-187.
    • (2005) Adv Genet , vol.54 , pp. 179-187
    • Ginsburg, D.S.1    Calos, M.P.2
  • 21
    • 2442458847 scopus 로고    scopus 로고
    • Construction of transgenic drosophila by using the site-specific integrase from phage phiC31
    • Groth, AC, Fish, M, Nusse, R and Calos, MP (2004). Construction of transgenic drosophila by using the site-specific integrase from phage phiC31. Genetics 166: 1775-1782.
    • (2004) Genetics , vol.166 , pp. 1775-1782
    • Groth, A.C.1    Fish, M.2    Nusse, R.3    Calos, M.P.4
  • 22
    • 14044257947 scopus 로고    scopus 로고
    • In vivo correction of murine hereditary tyrosinemia type I by phiC31 integrase-mediated gene delivery
    • Held, PK, Olivares, EC, Aguilar, CP, Finegold, M, Calos, MP and Grompe, M (2005). In vivo correction of murine hereditary tyrosinemia type I by phiC31 integrase-mediated gene delivery. Mol Ther 11: 399-408.
    • (2005) Mol Ther , vol.11 , pp. 399-408
    • Held, P.K.1    Olivares, E.C.2    Aguilar, C.P.3    Finegold, M.4    Calos, M.P.5    Grompe, M.6
  • 23
    • 33744786230 scopus 로고    scopus 로고
    • Phage phiC31 integrase-mediated genomic integration of the common cytokine receptor gamma chain in human T-cell lines
    • Ishikawa, Y, Tanaka, N, Murakami, K, Uchiyama, T, Kumaki, S, Tsuchiya, S et al. (2006). Phage phiC31 integrase-mediated genomic integration of the common cytokine receptor gamma chain in human T-cell lines. J Gene Med 8: 646-653.
    • (2006) J Gene Med , vol.8 , pp. 646-653
    • Ishikawa, Y.1    Tanaka, N.2    Murakami, K.3    Uchiyama, T.4    Kumaki, S.5    Tsuchiya, S.6
  • 24
    • 11844256340 scopus 로고    scopus 로고
    • Phage phiC31 integrase: A new tool in plastid genome engineering
    • Khan, MS, Khalid, AM and Malik KA (2005). Phage phiC31 integrase: A new tool in plastid genome engineering. Trends Plant Sci 10: 1-3.
    • (2005) Trends Plant Sci , vol.10 , pp. 1-3
    • Khan, M.S.1    Khalid, A.M.2    Malik, K.A.3
  • 25
    • 1642268398 scopus 로고    scopus 로고
    • A novel approach to plastid transformation utilizes the phiC31 phage integrase
    • Lutz, KA, Corneille, S, Azhagiri, AK, Svab, Z and Maliga, P (2004). A novel approach to plastid transformation utilizes the phiC31 phage integrase. Plant J 37: 906-913.
    • (2004) Plant J , vol.37 , pp. 906-913
    • Lutz, K.A.1    Corneille, S.2    Azhagiri, A.K.3    Svab, Z.4    Maliga, P.5
  • 27
    • 30044438781 scopus 로고    scopus 로고
    • Site-specific gene integration in cultured silkworm cells mediated by phiC31 integrase
    • Nakayama, G, Kawaguchi, Y, Koga, K and Kusakabe, T (2006). Site-specific gene integration in cultured silkworm cells mediated by phiC31 integrase. Mol Genet Genomics 275: 1-8.
    • (2006) Mol Genet Genomics , vol.275 , pp. 1-8
    • Nakayama, G.1    Kawaguchi, Y.2    Koga, K.3    Kusakabe, T.4
  • 28
    • 0038618975 scopus 로고    scopus 로고
    • PhiC31 integrase-mediated nonviral genetic correction of junctional epidermolysis bullosa
    • Ortiz-Urda, S, Thyagarajan, B, Keene, DR, Lin, Q, Calos, MP and Khavari, PA (2003). PhiC31 integrase-mediated nonviral genetic correction of junctional epidermolysis bullosa. Hum Gene Ther 14: 923-928.
    • (2003) Hum Gene Ther , vol.14 , pp. 923-928
    • Ortiz-Urda, S.1    Thyagarajan, B.2    Keene, D.R.3    Lin, Q.4    Calos, M.P.5    Khavari, P.A.6
  • 29
    • 4644292834 scopus 로고    scopus 로고
    • Nucleofection of muscle-derived stem cells and myoblasts with phiC31 integrase: Stable expression of a full-length-dystrophin fusion gene by human myoblasts
    • Quenneville, SP, Chapdelaine, P, Rousseau, J, Beaulieu, J, Caron, NJ, Skuk D et al. (2004). Nucleofection of muscle-derived stem cells and myoblasts with phiC31 integrase: Stable expression of a full-length-dystrophin fusion gene by human myoblasts. Mol Ther 10: 679-687.
    • (2004) Mol Ther , vol.10 , pp. 679-687
    • Quenneville, S.P.1    Chapdelaine, P.2    Rousseau, J.3    Beaulieu, J.4    Caron, N.J.5    Skuk, D.6
  • 30
    • 3042525132 scopus 로고    scopus 로고
    • Synapsis and DNA cleavage in phiC31 integrase-mediated site-specific recombination
    • Smith, MC, Till, R, Brady, K, Soultanas, P and Thorpe, H (2004). Synapsis and DNA cleavage in phiC31 integrase-mediated site-specific recombination. Nucleic Acids Res 32: 2607-2617.
    • (2004) Nucleic Acids Res , vol.32 , pp. 2607-2617
    • Smith, M.C.1    Till, R.2    Brady, K.3    Soultanas, P.4    Thorpe, H.5
  • 31
    • 0034924880 scopus 로고    scopus 로고
    • Gene insertion and replacement in Schizosaccharomyces pombe mediated by the Streptomyces bacteriophage phiC31 site-specific recombination system
    • Thomason, LC, Calendar, R and Ow, DW (2001). Gene insertion and replacement in Schizosaccharomyces pombe mediated by the Streptomyces bacteriophage phiC31 site-specific recombination system. Mol Genet Genomics 265: 1031-1038.
    • (2001) Mol Genet Genomics , vol.265 , pp. 1031-1038
    • Thomason, L.C.1    Calendar, R.2    Ow, D.W.3
  • 32
    • 0032805251 scopus 로고    scopus 로고
    • Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA
    • Liu, F, Song, Y and Liu, D (1999). Hydrodynamics-based transfection in animals by systemic administration of plasmid DNA. Gene Ther 6 1258-1266.
    • (1999) Gene Ther , vol.6 , pp. 1258-1266
    • Liu, F.1    Song, Y.2    Liu, D.3
  • 33
    • 0037818636 scopus 로고    scopus 로고
    • Sex significantly influences transduction of murine liver by recombinant adeno-associated viral vectors through an androgen-dependent pathway
    • Davidoff, AM, Ng, CY, Zhou, J, Spence, Y and Nathwani, AC (2003). Sex significantly influences transduction of murine liver by recombinant adeno-associated viral vectors through an androgen-dependent pathway. Blood 102: 480-488.
    • (2003) Blood , vol.102 , pp. 480-488
    • Davidoff, A.M.1    Ng, C.Y.2    Zhou, J.3    Spence, Y.4    Nathwani, A.C.5
  • 34
    • 33645161455 scopus 로고    scopus 로고
    • Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria
    • Harding, CO, Gillingham, MB, Hamman, K, Clark, H, Goebel-Daghighi, E, Bird, A et al. (2006). Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria. Gene Ther 13: 457-462.
    • (2006) Gene Ther , vol.13 , pp. 457-462
    • Harding, C.O.1    Gillingham, M.B.2    Hamman, K.3    Clark, H.4    Goebel-Daghighi, E.5    Bird, A.6
  • 35
    • 28844479023 scopus 로고    scopus 로고
    • Tetrahydrobiopterin and maternal PKU
    • Koch, R, Moseley, K and Guttler, F (2005). Tetrahydrobiopterin and maternal PKU. Mol Genet Metab 86 (suppl. 1): S139-S141.
    • (2005) Mol Genet Metab , vol.86 , Issue.SUPPL. 1
    • Koch, R.1    Moseley, K.2    Guttler, F.3
  • 37
    • 0041915626 scopus 로고    scopus 로고
    • Gene transfer of human guanosine 5′-triphosphate cyclohydrolase I restores vascular tetrahydrobiopterin level and endothelial function in low renin hypertension
    • Zheng, JS, Yang, XQ, Lookingland, KJ, Fink, GD, Hessliger, C and Kapatos, G (2003). Gene transfer of human guanosine 5′-triphosphate cyclohydrolase I restores vascular tetrahydrobiopterin level and endothelial function in low renin hypertension. Circulation 108 1238-1245.
    • (2003) Circulation , vol.108 , pp. 1238-1245
    • Zheng, J.S.1    Yang, X.Q.2    Lookingland, K.J.3    Fink, G.D.4    Hessliger, C.5    Kapatos, G.6
  • 38
    • 0037420705 scopus 로고    scopus 로고
    • Simultaneous measurement of phenylalanine and tyrosine in phenylketonuric plasma and dried blood by high-performance liquid chromatography
    • Dale, Y, Mackey, V, Mushi, R, Nyanda, A, Maleque, M and Ike, J (2003). Simultaneous measurement of phenylalanine and tyrosine in phenylketonuric plasma and dried blood by high-performance liquid chromatography. J Chromatogr B Analyt Technol Biomed Life Sci 788: 1-8.
    • (2003) J Chromatogr B Analyt Technol Biomed Life Sci , vol.788 , pp. 1-8
    • Dale, Y.1    Mackey, V.2    Mushi, R.3    Nyanda, A.4    Maleque, M.5    Ike, J.6
  • 39
    • 0041888245 scopus 로고    scopus 로고
    • Integration site for Streptomyces phage phiBT1 and development of site-specific integrating vectors
    • Gregory, MA, Till, R and Smith, MC (2003). Integration site for Streptomyces phage phiBT1 and development of site-specific integrating vectors. J Bacteriol 185: 5320-5323.
    • (2003) J Bacteriol , vol.185 , pp. 5320-5323
    • Gregory, M.A.1    Till, R.2    Smith, M.C.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.