Transduction of myogenic cells by retargeted dual high-capacity hybrid viral vectors: robust dystrophin synthesis in duchenne muscular dystrophy muscle cells

Molecular Therapy

Volumn 13, Issue 5, 2006, Pages 976-986

  Gonçalves, Manuel A F V ^a   Holkers, Maarten ^a   Cudré Mauroux, Christophe ^b   van Nierop, Gijsbert P ^a   Knaän Shanzer, Shoshan ^a   van der Velde, Ietje ^a   Valerio, Dinko ^a   de Vries, Antoine A F ^a  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b UNIVERSITY OF GENEVA   (Switzerland)

Author keywords

adeno associated virus; adenovirus; CAR; CD46; Duchenne muscular dystrophy; full length dystrophin; high capacity vector; human muscle cells; myoblast; retargeting

Indexed keywords

ADENOVIRUS VECTOR; BETA DYSTROGLYCAN; COXSACKIE VIRUS AND ADENOVIRUS RECEPTOR; DYSTROPHIN; GLYCOPROTEIN; PARVOVIRUS VECTOR; VIRUS VECTOR;

ARTICLE; CONTROLLED STUDY; COXSACKIE VIRUS B; DUCHENNE MUSCULAR DYSTROPHY; GENE TRANSFER; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; IMMUNOPHENOTYPING; MUSCLE CELL; MYOBLAST; MYOTUBE; SEROTYPE; SOUTHERN BLOTTING; VIRAL GENE DELIVERY SYSTEM;

ADENOVIRIDAE; DEPENDOVIRUS; DNA, RECOMBINANT; DYSTROPHIN; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HELA CELLS; HUMANS; MUSCLE CELLS; MUSCULAR DYSTROPHY, DUCHENNE; SEROTYPING; TRANSDUCTION, GENETIC; VIRUS INTEGRATION;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; COXSACKIEVIRUS; HUMAN ENTEROVIRUS B; PARVOVIRUS;

EID: 33645886040     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymthe.2005.11.018     Document Type: Article

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