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Volumn 11, Issue 8, 2002, Pages 759-767

Autotransplantation in mdx mice of mdx myoblasts genetically corrected by an HSV-1 amplicon vector

Author keywords

Autologous transplantation; Duchene muscular dystrophy (DMD); Dystrophin positive fibers; Full length dystrophin cDNA; HSV 1 amplicons

Indexed keywords

BASIC FIBROBLAST GROWTH FACTOR; BETA GALACTOSIDASE; COMPLEMENTARY DNA; DIHYDROFOLATE REDUCTASE; DYSTROPHIN; GREEN FLUORESCENT PROTEIN; IMMUNOSUPPRESSIVE AGENT; NEOMYCIN; NITRIC OXIDE SYNTHASE; SOMATOMEDIN C; TACROLIMUS; VIRUS DNA; VIRUS VECTOR;

EID: 0036980730     PISSN: 09636897     EISSN: None     Source Type: Journal    
DOI: 10.3727/000000002783985297     Document Type: Article
Times cited : (25)

References (61)
  • 1
    • 0028500191 scopus 로고
    • Cultured human myoblasts and myotubes show markedly different transducibility by replication-defective adenovirus recombinants
    • Acsadi, G.; Jani, A.; Huard, J.; Blaschuk, K.; Massie, B.; Holland, P.; Lochmuller, H.; Karpati, G. Cultured human myoblasts and myotubes show markedly different transducibility by replication-defective adenovirus recombinants. Gene Ther. 1:338-340; 1994.
    • (1994) Gene Ther. , vol.1 , pp. 338-340
    • Acsadi, G.1    Jani, A.2    Huard, J.3    Blaschuk, K.4    Massie, B.5    Holland, P.6    Lochmuller, H.7    Karpati, G.8
  • 2
    • 0028346944 scopus 로고
    • A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity
    • Acsadi, G.; Jani, A.; Massie, B.; Simoneau, M.; Holland, P.; Blaschuk, K.; Karpati, G. A differential efficiency of adenovirus-mediated in vivo gene transfer into skeletal muscle cells of different maturity. Hum. Mol. Genet. 3:579-584; 1994.
    • (1994) Hum. Mol. Genet. , vol.3 , pp. 579-584
    • Acsadi, G.1    Jani, A.2    Massie, B.3    Simoneau, M.4    Holland, P.5    Blaschuk, K.6    Karpati, G.7
  • 4
    • 0036544519 scopus 로고    scopus 로고
    • Muscle-specific expression of insulin-like growth factor I counters muscle decline in mdx mice
    • Barton, E. R.; Morris, L.; Musaro, A.; Rosenthal, N.; Sweeney, H. L. Muscle-specific expression of insulin-like growth factor I counters muscle decline in mdx mice. J. Cell Biol. 157:137-148; 2002.
    • (2002) J. Cell Biol. , vol.157 , pp. 137-148
    • Barton, E.R.1    Morris, L.2    Musaro, A.3    Rosenthal, N.4    Sweeney, H.L.5
  • 6
    • 0032573203 scopus 로고    scopus 로고
    • Management of posttransplant lymphoproliferative disease in pediatric liver transplant recipients receiving primary tacrolimus (FK506) therapy
    • Cacciarelli, T. V.; Green, M.; Jaffe, R.; Mazariegos, G. V.; Jain, A.; Fung, J. J.; Reyes, J. Management of posttransplant lymphoproliferative disease in pediatric liver transplant recipients receiving primary tacrolimus (FK506) therapy. Transplantation 66:1047-1052; 1998.
    • (1998) Transplantation , vol.66 , pp. 1047-1052
    • Cacciarelli, T.V.1    Green, M.2    Jaffe, R.3    Mazariegos, G.V.4    Jain, A.5    Fung, J.J.6    Reyes, J.7
  • 7
    • 0028934815 scopus 로고
    • Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression
    • Dai, Y.; Schwarz, E. M.; Gu, D.; Zhang, W. W.; Sarvetnick, N.; Verma, I. M. Cellular and humoral immune responses to adenoviral vectors containing factor IX gene: Tolerization of factor IX and vector antigens allows for long-term expression. Proc. Natl. Acad. Sci. USA 92:1401-1405; 1995.
    • (1995) Proc. Natl. Acad. Sci. USA , vol.92 , pp. 1401-1405
    • Dai, Y.1    Schwarz, E.M.2    Gu, D.3    Zhang, W.W.4    Sarvetnick, N.5    Verma, I.M.6
  • 8
    • 0029849257 scopus 로고    scopus 로고
    • Quantitative analysis of the packaging capacity of recombinant adeno-associated virus
    • Dong, J. Y.; Fan, P. D.; Frizzell, R. A. Quantitative analysis of the packaging capacity of recombinant adeno-associated virus. Hum. Gene Ther. 7:2101-2112; 1996.
    • (1996) Hum. Gene Ther. , vol.7 , pp. 2101-2112
    • Dong, J.Y.1    Fan, P.D.2    Frizzell, R.A.3
  • 9
    • 0026570486 scopus 로고
    • Retroviral-mediated transfer of a dystrophin minigene into mdx mouse myoblasts in vitro
    • Dunckley, M. G.; Love, D. R.; Davies, K. E.; Walsh, F. S.; Morris, G. E.; Dickson, G. Retroviral-mediated transfer of a dystrophin minigene into mdx mouse myoblasts in vitro. FEBS Lett. 296:128-134; 1992.
    • (1992) FEBS Lett. , vol.296 , pp. 128-134
    • Dunckley, M.G.1    Love, D.R.2    Davies, K.E.3    Walsh, F.S.4    Morris, G.E.5    Dickson, G.6
  • 10
    • 0027174251 scopus 로고
    • Direct retroviral-mediated transfer of a dystrophin minigene into mdx mouse muscle in vivo
    • Dunckley, M. G.; Wells, D. J.; Walsh, F. S.; Dickson, G. Direct retroviral-mediated transfer of a dystrophin minigene into mdx mouse muscle in vivo. Hum. Mol. Genet. 2:717-723; 1993.
    • (1993) Hum. Mol. Genet. , vol.2 , pp. 717-723
    • Dunckley, M.G.1    Wells, D.J.2    Walsh, F.S.3    Dickson, G.4
  • 11
    • 0027490860 scopus 로고
    • Duchenne muscular dystrophy-Meryon's disease
    • Emery, A. E. Duchenne muscular dystrophy-Meryon's disease. Neuromusc. Disord. 3:263-266; 1993.
    • (1993) Neuromusc. Disord. , vol.3 , pp. 263-266
    • Emery, A.E.1
  • 15
    • 0029844849 scopus 로고    scopus 로고
    • Helper virus-free transfer of herpes simplex virus type 1 plasmid vectors into neural cells
    • Fraefel, C.; Song, S.; Lim, F.; Lang, P.; Yu, L.; Wang, Y.; Wild, P.; Geller, A. I. Helper virus-free transfer of herpes simplex virus type 1 plasmid vectors into neural cells. J. Virol. 70:7190-7197; 1996.
    • (1996) J. Virol. , vol.70 , pp. 7190-7197
    • Fraefel, C.1    Song, S.2    Lim, F.3    Lang, P.4    Yu, L.5    Wang, Y.6    Wild, P.7    Geller, A.I.8
  • 16
    • 0026502646 scopus 로고
    • MyoD and myogenin are coexpressed in regenerating skeletal muscle of the mouse
    • Fuchtbauer, E. M.; Westphal, H. MyoD and myogenin are coexpressed in regenerating skeletal muscle of the mouse. Dev. Dyn. 193:34-39; 1992.
    • (1992) Dev. Dyn. , vol.193 , pp. 34-39
    • Fuchtbauer, E.M.1    Westphal, H.2
  • 17
    • 0026805782 scopus 로고
    • Identification of skeletal muscle precursor cells in vivo by use of MyoD1 and myogenin probes
    • Grounds, M. D.; Garrett, K. K.; Lai, M. C.; Wright, W. E.; Beilharz, M. W. Identification of skeletal muscle precursor cells in vivo by use of MyoD1 and myogenin probes. Cell Tissue Res. 267:99-104; 1992.
    • (1992) Cell Tissue Res. , vol.267 , pp. 99-104
    • Grounds, M.D.1    Garrett, K.K.2    Lai, M.C.3    Wright, W.E.4    Beilharz, M.W.5
  • 18
    • 0026560260 scopus 로고
    • Normal dystrophin transcripts detected in Duchenne muscular dystrophy patients after myoblast transplantation
    • Gussoni, E.; Pavlath, G. K.; Lanctot, A. M.; Sharma, K. R.; Miller, R. G.; Steinman, L.; Blau, H. M. Normal dystrophin transcripts detected in Duchenne muscular dystrophy patients after myoblast transplantation. Nature 356:435-438; 1992.
    • (1992) Nature , vol.356 , pp. 435-438
    • Gussoni, E.1    Pavlath, G.K.2    Lanctot, A.M.3    Sharma, K.R.4    Miller, R.G.5    Steinman, L.6    Blau, H.M.7
  • 19
    • 0018218652 scopus 로고
    • Further observations on the pathological responses of rat skeletal muscle to toxins isolated from the venom of the Australian tiger snake, Notechis scutatus scutatus
    • Harris, J. B.; Johnson, M. A. Further observations on the pathological responses of rat skeletal muscle to toxins isolated from the venom of the Australian tiger snake, Notechis scutatus scutatus. Clin. Exp. Pharmacol. Physiol. 5:587-600; 1978.
    • (1978) Clin. Exp. Pharmacol. Physiol. , vol.5 , pp. 587-600
    • Harris, J.B.1    Johnson, M.A.2
  • 20
    • 0023614188 scopus 로고
    • Dystrophin: The protein product of the Duchenne muscular dystrophy locus
    • Hoffman, E. P.; Brown, R. H., Jr.; Kunkel, L. M. Dystrophin: The protein product of the Duchenne muscular dystrophy locus. Cell 51:919-928; 1987.
    • (1987) Cell , vol.51 , pp. 919-928
    • Hoffman, E.P.1    Brown R.H., Jr.2    Kunkel, L.M.3
  • 22
    • 0027080543 scopus 로고
    • Human myoblast transplantation between immunohistocompatible donors and recipients produces immune reactions
    • Huard, J.; Roy, R.; Bouchard, J. P.; Malouin, F.; Richards, C. L.; Tremblay, J. P. Human myoblast transplantation between immunohistocompatible donors and recipients produces immune reactions. Transplant. Proc. 24:3049-3051; 1992.
    • (1992) Transplant. Proc. , vol.24 , pp. 3049-3051
    • Huard, J.1    Roy, R.2    Bouchard, J.P.3    Malouin, F.4    Richards, C.L.5    Tremblay, J.P.6
  • 25
    • 0028029771 scopus 로고
    • Very efficient myoblast allotransplantation in mice under FK506 immunosuppression
    • Kinoshita, I.; Vilquin, J. T.; Guerette, B.; Asselin, I.; Roy, R.; Tremblay, J. P. Very efficient myoblast allotransplantation in mice under FK506 immunosuppression. Muscle Nerve 17:1407-1415; 1994.
    • (1994) Muscle Nerve , vol.17 , pp. 1407-1415
    • Kinoshita, I.1    Vilquin, J.T.2    Guerette, B.3    Asselin, I.4    Roy, R.5    Tremblay, J.P.6
  • 26
    • 0023614271 scopus 로고
    • Complete cloning of the Duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals
    • Koenig, M.; Hoffman, E. P.; Bertelson, J. C.; Monaco, A. P.; Feener, C.; Kunkel, L. M. Complete cloning of the Duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals. Cell 50:509-517; 1987.
    • (1987) Cell , vol.50 , pp. 509-517
    • Koenig, M.1    Hoffman, E.P.2    Bertelson, J.C.3    Monaco, A.P.4    Feener, C.5    Kunkel, L.M.6
  • 27
    • 0025954579 scopus 로고
    • Infection and inhibition of differentiation of human fetal skeletal myoblasts by adenovirus
    • Kohtz, D. S.; Cole, F.; Wong, M. L.; Hsu, M. T. Infection and inhibition of differentiation of human fetal skeletal myoblasts by adenovirus. Virology 184:569-579; 1991.
    • (1991) Virology , vol.184 , pp. 569-579
    • Kohtz, D.S.1    Cole, F.2    Wong, M.L.3    Hsu, M.T.4
  • 28
    • 0014949207 scopus 로고
    • Cleavage of structural proteins during the assembly of the head of bacteriophage T4
    • Laemmli, U. K. Cleavage of structural proteins during the assembly of the head of bacteriophage T4. Nature 227:680-685; 1970.
    • (1970) Nature , vol.227 , pp. 680-685
    • Laemmli, U.K.1
  • 30
    • 0028047235 scopus 로고
    • Dystrophin-glycoprotein complex: Its role in the molecular pathogenesis of muscular dystrophies
    • Matsumura, K.; Campbell, K. P. Dystrophin-glycoprotein complex: Its role in the molecular pathogenesis of muscular dystrophies. Muscle Nerve 17:2-15; 1994.
    • (1994) Muscle Nerve , vol.17 , pp. 2-15
    • Matsumura, K.1    Campbell, K.P.2
  • 31
    • 0026621608 scopus 로고
    • Association of dystrophin-related protein with dystrophin-associated proteins in mdx mouse muscle
    • Matsumura, K.; Ervasti, J. M.; Ohlendieck, K.; Kahl, S. D.; Campbell, K. P. Association of dystrophin-related protein with dystrophin-associated proteins in mdx mouse muscle. Nature 360:588-591; 1992.
    • (1992) Nature , vol.360 , pp. 588-591
    • Matsumura, K.1    Ervasti, J.M.2    Ohlendieck, K.3    Kahl, S.D.4    Campbell, K.P.5
  • 34
    • 0025279872 scopus 로고
    • Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection
    • Miller, D. G.; Adam, M.A.; Miller, A. D. Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection. Mol. Cell. Biol. 10:4239-4242; 1990.
    • (1990) Mol. Cell. Biol. , vol.10 , pp. 4239-4242
    • Miller, D.G.1    Adam, M.A.2    Miller, A.D.3
  • 35
    • 0031788860 scopus 로고    scopus 로고
    • Expression of human dystrophin following the transplantation of genetically modified mdx myoblasts
    • Moisset, P. A.; Gagnon, Y.; Karpati, G.; Tremblay, J. P. Expression of human dystrophin following the transplantation of genetically modified mdx myoblasts. Gene Ther. 5:1340-1346; 1998.
    • (1998) Gene Ther. , vol.5 , pp. 1340-1346
    • Moisset, P.A.1    Gagnon, Y.2    Karpati, G.3    Tremblay, J.P.4
  • 36
    • 0025633198 scopus 로고
    • Normal myogenic cells from newborn mice restore normal histology to degenerating muscles of the mdx mouse
    • Morgan, J. E.; Hoffman, E. P.; Partridge, T. A. Normal myogenic cells from newborn mice restore normal histology to degenerating muscles of the mdx mouse. J. Cell Biol. 111:2437-2449; 1990.
    • (1990) J. Cell Biol. , vol.111 , pp. 2437-2449
    • Morgan, J.E.1    Hoffman, E.P.2    Partridge, T.A.3
  • 37
    • 0027466562 scopus 로고
    • Long-term persistence and migration of myogenic cells injected into pre-irradiated muscles of mdx mice
    • Morgan, J. E.; Pagel, C. N.; Sherratt, T.; Partridge, T. A. Long-term persistence and migration of myogenic cells injected into pre-irradiated muscles of mdx mice. J. Neurol. Sci. 115:191-200; 1993.
    • (1993) J. Neurol. Sci. , vol.115 , pp. 191-200
    • Morgan, J.E.1    Pagel, C.N.2    Sherratt, T.3    Partridge, T.A.4
  • 39
    • 0032080573 scopus 로고    scopus 로고
    • Dystrophin acts as a transplantation rejection antigen in dystrophin-deficient mice: Implication for gene therapy
    • Ohtsuka, Y.; Udaka, K.; Yamashiro, Y.; Yagita, H.; Okumura, K. Dystrophin acts as a transplantation rejection antigen in dystrophin-deficient mice: Implication for gene therapy. J. Immunol. 160:4635-4640; 1998.
    • (1998) J. Immunol. , vol.160 , pp. 4635-4640
    • Ohtsuka, Y.1    Udaka, K.2    Yamashiro, Y.3    Yagita, H.4    Okumura, K.5
  • 41
    • 0024540879 scopus 로고
    • Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts
    • Partridge, T. A.; Morgan, J. E.; Coulton, G. R.; Hoffman, E. P.; Kunkel, L. M. Conversion of mdx myofibres from dystrophin-negative to -positive by injection of normal myoblasts. Nature 337:176-179; 1989.
    • (1989) Nature , vol.337 , pp. 176-179
    • Partridge, T.A.1    Morgan, J.E.2    Coulton, G.R.3    Hoffman, E.P.4    Kunkel, L.M.5
  • 42
    • 0028566996 scopus 로고
    • Transient immunosuppressive treatment leads to long-term retention of allogeneic myoblasts in hybrid myofibers
    • Pavlath, G. K.; Rando, T. A.; Blau, H. M. Transient immunosuppressive treatment leads to long-term retention of allogeneic myoblasts in hybrid myofibers. J. Cell Biol. 127:1923-1932; 1994.
    • (1994) J. Cell Biol. , vol.127 , pp. 1923-1932
    • Pavlath, G.K.1    Rando, T.A.2    Blau, H.M.3
  • 47
    • 0033045270 scopus 로고    scopus 로고
    • Successful myoblast transplantation in primates depends on appropriate cell delivery and induction of regeneration in the host muscle
    • Skuk, D.; Roy, B.; Goulet, M.; Tremblay, J. P. Successful myoblast transplantation in primates depends on appropriate cell delivery and induction of regeneration in the host muscle. Exp. Neurol. 155:22-30; 1999.
    • (1999) Exp. Neurol. , vol.155 , pp. 22-30
    • Skuk, D.1    Roy, B.2    Goulet, M.3    Tremblay, J.P.4
  • 48
    • 0020451027 scopus 로고
    • The herpes simplex virus amplicon: A new eucaryotic defective-virus cloning-amplifying vector
    • Spaete, R. R.; Frenkel, N. The herpes simplex virus amplicon: A new eucaryotic defective-virus cloning-amplifying vector. Cell 30:295-304; 1982.
    • (1982) Cell , vol.30 , pp. 295-304
    • Spaete, R.R.1    Frenkel, N.2
  • 49
    • 0031870243 scopus 로고    scopus 로고
    • An enhanced packaging system for helper-dependent herpes simplex virus vectors
    • Stavropoulos, T. A.; Strathdee, C. A. An enhanced packaging system for helper-dependent herpes simplex virus vectors. J. Virol. 72:7137-7143; 1998.
    • (1998) J. Virol. , vol.72 , pp. 7137-7143
    • Stavropoulos, T.A.1    Strathdee, C.A.2
  • 50
    • 0034181045 scopus 로고    scopus 로고
    • A modular set of helper-dependent herpes simplex virus expression vectors
    • Strathdee, C. A.; McLeod, M. R. A modular set of helper-dependent herpes simplex virus expression vectors. Mol. Ther. 1:479-485; 2000.
    • (2000) Mol. Ther. , vol.1 , pp. 479-485
    • Strathdee, C.A.1    McLeod, M.R.2
  • 51
    • 0027166930 scopus 로고
    • Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy
    • Tremblay, J. P.; Malouin, F.; Roy, R.; Huard, J.; Bouchard, J. P.; Satoh, A.; Richards, C. L. Results of a triple blind clinical study of myoblast transplantations without immunosuppressive treatment in young boys with Duchenne muscular dystrophy. Cell Transplant. 2:99-112; 1993.
    • (1993) Cell Transplant. , vol.2 , pp. 99-112
    • Tremblay, J.P.1    Malouin, F.2    Roy, R.3    Huard, J.4    Bouchard, J.P.5    Satoh, A.6    Richards, C.L.7
  • 53
    • 0028807696 scopus 로고
    • FK506 immunosuppression to control the immune reactions triggered by first-generation adenovirus-mediated gene transfer
    • Vilquin, J. T.; Guerette, B.; Kinoshita, I.; Roy, B.; Goulet, M.; Gravel, C.; Roy, R.; Tremblay, J. P. FK506 immunosuppression to control the immune reactions triggered by first-generation adenovirus-mediated gene transfer. Hum. Gene Ther. 6:1391-1401; 1995.
    • (1995) Hum. Gene Ther. , vol.6 , pp. 1391-1401
    • Vilquin, J.T.1    Guerette, B.2    Kinoshita, I.3    Roy, B.4    Goulet, M.5    Gravel, C.6    Roy, R.7    Tremblay, J.P.8
  • 54
    • 0028824881 scopus 로고
    • Successful histocompatible myoblast transplantation in dystrophin-deficient mdx mouse despite the production of antibodies against dystrophin
    • Vilquin, J. T.; Wagner, E.; Kinoshita, I.; Roy, R.; Tremblay, J. P. Successful histocompatible myoblast transplantation in dystrophin-deficient mdx mouse despite the production of antibodies against dystrophin. J. Cell Biol. 131:975-988; 1995.
    • (1995) J. Cell Biol. , vol.131 , pp. 975-988
    • Vilquin, J.T.1    Wagner, E.2    Kinoshita, I.3    Roy, R.4    Tremblay, J.P.5
  • 56
    • 0034756520 scopus 로고    scopus 로고
    • An infectious transfer and expression system for genomic DNA loci in human and mouse cells
    • Wade-Martins, R.; Smith, E. R.; Tyminski, E.; Chiocca, E. A.; Saeki, Y. An infectious transfer and expression system for genomic DNA loci in human and mouse cells. Nat. Biotechnol. 19:1067-1070; 2001.
    • (2001) Nat. Biotechnol. , vol.19 , pp. 1067-1070
    • Wade-Martins, R.1    Smith, E.R.2    Tyminski, E.3    Chiocca, E.A.4    Saeki, Y.5
  • 59
    • 0036173625 scopus 로고    scopus 로고
    • Herpes simplex virus type 1 amplicon vector-mediated gene transfer to muscle
    • Wang, Y.; Mukherjee, S.; Fraefel, C.; Breakefield, X. O.; Allen, P. D. Herpes simplex virus type 1 amplicon vector-mediated gene transfer to muscle. Hum. Gene Ther. 13:261-273; 2002.
    • (2002) Hum. Gene Ther. , vol.13 , pp. 261-273
    • Wang, Y.1    Mukherjee, S.2    Fraefel, C.3    Breakefield, X.O.4    Allen, P.D.5
  • 60
    • 0035494438 scopus 로고    scopus 로고
    • A nitric oxide synthase transgene ameliorates muscular dystrophy in mdx mice
    • Wehling, M.; Spencer, M. J.; Tidball, J. G. A nitric oxide synthase transgene ameliorates muscular dystrophy in mdx mice. J. Cell Biol. 155:123-131; 2001.
    • (2001) J. Cell Biol. , vol.155 , pp. 123-131
    • Wehling, M.1    Spencer, M.J.2    Tidball, J.G.3
  • 61
    • 0020463763 scopus 로고
    • Effects of irradiation on regeneration in dystrophic mouse leg muscles
    • Wirtz, P.; Loermans, H.; Rutten, E. Effects of irradiation on regeneration in dystrophic mouse leg muscles. Br. J. Exp. Pathol. 63:671-679; 1982.
    • (1982) Br. J. Exp. Pathol. , vol.63 , pp. 671-679
    • Wirtz, P.1    Loermans, H.2    Rutten, E.3


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