Retrovirally mediated correction of bone marrow-derived mesenchymal stem cells from patients with mucopolysaccharidosis type I

Blood

Volumn 99, Issue 5, 2002, Pages 1857-1859

  Baxter, Melissa A ^a,b   Wynn, Robert F ^a,b   Deakin, Jonathan A ^a,b   Bellantuono, Ilaria ^a,b   Edington, Kirsten G ^a,b   Cooper, Alan ^a,b   Besley, Guy T N ^a,b   Church, Heather J ^a,b   Ed Wraith, J ^a,b   Carr, Trevor F ^a,b   Fairbairn, Leslie J ^a,b  

^a ROYAL MANCHESTER CHILDREN S HOSPITAL   (United Kingdom)

^b CHRISTIE HOSPITAL   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

GLYCOSAMINOGLYCAN; GREEN FLUORESCENT PROTEIN; HEPARAN SULFATE; LEVO IDURONIDASE; RETROVIRUS VECTOR;

ARTICLE; AUTOSOMAL RECESSIVE DISORDER; BONE MARROW CELL; BONE MARROW CULTURE; CONTROLLED STUDY; DNA MODIFICATION; FIBROBLAST; GENETIC TRANSDUCTION; HUMAN; HUMAN CELL; HURLER SYNDROME; MESENCHYME CELL; PRIORITY JOURNAL; VIRAL GENE THERAPY;

EID: 0036493929     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: 10.1182/blood.V99.5.1857     Document Type: Article

References (21)

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