Retrovirus-mediated transfer of the human α-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts

Gene Therapy

Volumn 4, Issue 11, 1997, Pages 1150-1159

  Huang, M M ^a   Wong, A ^a   Yu, X ^a   Kakkis, E ^b   Kohn, D B ^a,c  

^a UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^b HARBOR UCLA MEDICAL CENTER   (United States)

^c University of Los Angeles   (United States)

Author keywords

Cross correction; Gene therapy; Hematopoietic cells; Hurler syndrome; Retroviral vectors

Indexed keywords

CD34 ANTIGEN; COMPLEMENTARY DNA; LEVO IDURONIDASE; SOMATOMEDIN B RECEPTOR; VIRUS VECTOR;

ANIMAL CELL; ARTICLE; AUTOLOGOUS BONE MARROW TRANSPLANTATION; BONE MARROW CELL; CONTROLLED STUDY; FIBROBLAST; GENE TRANSFER; HEMATOPOIETIC STEM CELL; HUMAN; HUMAN CELL; HURLER SYNDROME; MOLONEY LEUKEMIA ONCOVIRUS; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; RETROVIRUS;

ANIMALIA; MOLONEY MURINE LEUKEMIA VIRUS; MURINAE; ONCOVIRINAE; UNIDENTIFIED RETROVIRUS;

EID: 0030734644     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300504     Document Type: Article

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