Axons mediate the distribution of arylsulfatase a within the mouse hippocampus upon gene delivery

Molecular Therapy

Volumn 12, Issue 4, 2005, Pages 669-679

  Luca, Tonia ^a   Givogri, Maria I ^a   Perani, Laura ^a   Galbiati, Francesca ^a   Follenzi, Antonia ^a   Naldini, Luigi ^a,b   Bongarzone, Ernesto R ^a  

^a SAN RAFFAELE SCIENTIFIC INSTITUTE   (Italy)

^b VITA SALUTE SAN RAFFAELE UNIVERSITY   (Italy)

Author keywords

Axonal transport; Hippocampus; Lentiviral vector; Leukodystrophy; Myelin

Indexed keywords

CEREBROSIDE SULFATASE; COMPLEMENTARY DNA; GREEN FLUORESCENT PROTEIN; HEMAGGLUTININ; LENTIVIRUS VECTOR; LYSOSOME ENZYME; SULFATIDE;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BRAIN COMMISSURE; BRAIN NERVE CELL; CELL COMPARTMENTALIZATION; CLINICAL OBSERVATION; CONTROLLED STUDY; DENDRITE; ENZYME LOCALIZATION; GENE TRANSFER; GENETIC TRANSDUCTION; GRANULE CELL; HIPPOCAMPUS; IN VIVO STUDY; LYSOSOME; MAMMAL; METACHROMATIC LEUKODYSTROPHY; MOUSE; NERVE FIBER TRANSPORT; NEUROPROTECTION; NONHUMAN; PROTEIN EXPRESSION; PROTEIN TRANSPORT; PYRAMIDAL TRACT; SYNAPSE VESICLE; VIRAL GENE DELIVERY SYSTEM;

ANIMALS; AXONAL TRANSPORT; CELL MOVEMENT; CEREBROSIDE-SULFATASE; DISEASE MODELS, ANIMAL; DNA, COMPLEMENTARY; GENE THERAPY; GENETIC VECTORS; GREEN FLUORESCENT PROTEINS; HEMAGGLUTININS; HIPPOCAMPUS; LENTIVIRUS; LEUKODYSTROPHY, METACHROMATIC; MICE; MICE, MUTANT STRAINS; RECOMBINANT PROTEINS; TRANSDUCTION, GENETIC;

ANIMALIA; MAMMALIA;

EID: 25144474418     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymthe.2005.06.438     Document Type: Article

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