Adeno-associated virus-mediated gene transfer of the heart/muscle adenine nucleotide translocator (ANT) in mouse

Gene Therapy

Volumn 12, Issue 7, 2005, Pages 570-578

  Flierl, A ^a,d   Chen, Y ^b   Coskun, P E ^a,d   Samulski, R J ^c   Wallace, D C ^a,d  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b UNIVERSITY OF CHICAGO   (United States)

^c UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^d EMORY UNIVERSITY   (United States)

Author keywords

AAV; Adenine nucleotide translocator (ANT); Mitochondria; Myopathy; Ophthalmoplegia; Oxidative phosphorylation

Indexed keywords

ADENINE NUCLEOTIDE TRANSLOCASE; ADENOSINE DIPHOSPHATE; ADENOSINE TRIPHOSPHATE; COMPLEMENTARY DNA; PARVOVIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL DIFFERENTIATION; CELL TRANSPORT; CONTROLLED STUDY; DISEASE ASSOCIATION; DISORDERS OF MITOCHONDRIAL FUNCTIONS; DRUG MECHANISM; EXTRAOCULAR MUSCLE; GENE EXPRESSION; GENE INSERTION; GENE MUTATION; GENE TARGETING; GENE TRANSFER; GENETIC TRANSDUCTION; HISTOPATHOLOGY; MITOCHONDRIAL MEMBRANE; MITOCHONDRIAL MYOPATHY; MOUSE; MOUSE MUTANT; MUSCLE CELL; NONHUMAN; NUCLEOTIDE SEQUENCE; OPHTHALMOPLEGIA; PARALYSIS; PRIORITY JOURNAL; PTOSIS; STEM CELL; SYMPTOMATOLOGY; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRUS RECOMBINANT;

ADENINE NUCLEOTIDE TRANSLOCATOR 1; ANIMALS; DEPENDOVIRUS; DNA, COMPLEMENTARY; GENE TARGETING; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; MICE; MICE, KNOCKOUT; MITOCHONDRIA, MUSCLE; MITOCHONDRIAL MYOPATHIES; MUSCLE, SKELETAL; OPHTHALMOPLEGIA, CHRONIC PROGRESSIVE EXTERNAL; TRANSGENES;

ADENO-ASSOCIATED VIRUS; FORMICIDAE;

EID: 16344384536     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3302443     Document Type: Article

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