Phenotypic rescue after adeno-associated virus-mediated delivery of 4-sulfatase to the retinal pigment epithelium of feline mucopolysaccharidosis VI

Journal of Gene Medicine

Volumn 4, Issue 6, 2002, Pages 613-621

  Ho, Thucanh T ^a   Maguire, Albert M ^a   Aguirre, Gustavo D ^b   Surace, Enrico M ^a   Anand, Vibha ^a   Zeng, Yong ^a   Salvetti, Anna ^c   Hopwood, John J ^d   Haskins, Mark E ^e   Bennett, Jean ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b Department of Obstetrics Gynecology   (United States)

^c Universite de Nantes   (France)

^d WOMEN S AND CHILDREN S HOSPITAL   (Australia)

^e UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

Adeno associated virus; Cat; Gene therapy; Lysosomal storage; Mucopolysaccharidosis VI; Retinal pigment epithelium

Indexed keywords

ANTIBIOTIC AGENT; COMPLEMENTARY DNA; CORTICOSTEROID; CYCLOPENTOLATE; DERMATAN SULFATE; GREEN FLUORESCENT PROTEIN; PARVOVIRUS VECTOR; PHENYLEPHRINE; SULFATASE; TROPICAMIDE; VIRUS VECTOR; PHOTOPROTEIN;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BIOACCUMULATION; CAT; CELL INCLUSION; CONJUNCTIVITIS; CONTROLLED STUDY; DISEASE SEVERITY; DOSE TIME EFFECT RELATION; DRUG TARGETING; HISTOPATHOLOGY; HYPERTROPHY; IMMUNE RESPONSE; IN SITU HYBRIDIZATION; LYSOSOME MEMBRANE; LYSOSOME STORAGE DISEASE; MAROTEAUX LAMY SYNDROME; NEUTROPHILIA; NONHUMAN; OPHTHALMOSCOPY; PATHOLOGY; PHENOTYPE; PIGMENT EPITHELIUM; PRIORITY JOURNAL; REPORTER GENE; RETINA CELL; RETINA DISEASE; SCAR FORMATION; TIME; VIRAL GENE DELIVERY SYSTEM; VIRUS RECOMBINANT; ADENO ASSOCIATED VIRUS; ANIMAL; ANIMAL DISEASE; ANTIBODY PRODUCTION; ENZYMOLOGY; GENE THERAPY; GENETIC RECOMBINATION; GENETICS;

ADENO-ASSOCIATED VIRUS; FELIDAE; FELIS CATUS;

ANIMALS; ANTIBODY FORMATION; CATS; DEPENDOVIRUS; GENE THERAPY; GREEN FLUORESCENT PROTEINS; IN SITU HYBRIDIZATION; LUMINESCENT PROTEINS; MUCOPOLYSACCHARIDOSIS VI; PHENOTYPE; PIGMENT EPITHELIUM OF EYE; RECOMBINATION, GENETIC; SULFATASES;

EID: 14044270228     PISSN: 1099498X     EISSN: None     Source Type: Journal    
DOI: 10.1002/jgm.302     Document Type: Article

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