메뉴 건너뛰기




Volumn 99, Issue 4, 2002, Pages 259-265

Progress in the somatic gene therapy of retinal dystrophies in animal models;Fortschritte in der somatischen gentherapie von netzhautdegenerationen am tiermodell

Author keywords

Adeno associated virus; Animal model; Retinal dystrophies; Somatic gene therapy

Indexed keywords

ADENOVIRUS VECTOR;

EID: 0346665723     PISSN: 0941293X     EISSN: None     Source Type: Journal    
DOI: 10.1007/s00347-002-0633-x     Document Type: Article
Times cited : (3)

References (20)
  • 1
    • 0035032662 scopus 로고    scopus 로고
    • Gene therapy restores vision in a canine model of childhood blindness
    • Acland GM, Aguirre GD, Ray J et al. (2001) Gene therapy restores vision in a canine model of childhood blindness. Nat Genet 28:92-95
    • (2001) Nat Genet , vol.28 , pp. 92-95
    • Acland, G.M.1    Aguirre, G.D.2    Ray, J.3
  • 2
    • 0034779927 scopus 로고    scopus 로고
    • A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease
    • Aitken ML, Moss RB, Waltz DA et al. (2001) A phase I study of aerosolized administration of tgAAVCF to cystic fibrosis subjects with mild lung disease. Hum Gene Ther 12:1907-1916
    • (2001) Hum Gene Ther , vol.12 , pp. 1907-1916
    • Aitken, M.L.1    Moss, R.B.2    Waltz, D.A.3
  • 3
    • 0033947697 scopus 로고    scopus 로고
    • Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy
    • Ali RR, Sarra GM, Stephens C et al. (2000) Restoration of photoreceptor ultrastructure and function in retinal degeneration slow mice by gene therapy [see comments]. Nat Genet 25:306-310
    • (2000) Nat Genet , vol.25 , pp. 306-310
    • Ali, R.R.1    Sarra, G.M.2    Stephens, C.3
  • 4
    • 13044256410 scopus 로고    scopus 로고
    • Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina
    • Bennett J, Maguire AM, Cideciyan AV et al. (1999) Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina. Proc Natl Acad Sci USA 96:9920-9925
    • (1999) Proc Natl Acad Sci USA , vol.96 , pp. 9920-9925
    • Bennett, J.1    Maguire, A.M.2    Cideciyan, A.V.3
  • 5
    • 0035371211 scopus 로고    scopus 로고
    • Molecular genetics and prospects for therapy of the inherited retinal dystrophies
    • Bessant DA, Ali RR, Bhattacharya SS (2001) Molecular genetics and prospects for therapy of the inherited retinal dystrophies. Curr Opin Genet Dev 11:307-316
    • (2001) Curr Opin Genet Dev , vol.11 , pp. 307-316
    • Bessant, D.A.1    Ali, R.R.2    Bhattacharya, S.S.3
  • 6
    • 0035989763 scopus 로고    scopus 로고
    • Gene therapy for Parkinson's disease
    • Frim DM, Le HN (2002) Gene therapy for Parkinson's disease. Expert Opin Biol Ther 2:151-161
    • (2002) Expert Opin Biol Ther , vol.2 , pp. 151-161
    • Frim, D.M.1    Le, H.N.2
  • 7
    • 0028969746 scopus 로고
    • Cell loss in retinal dystrophies by apoptosis - Death by informed consent!
    • Gregory CY, Bird AC (1995) Cell loss in retinal dystrophies by apoptosis - death by informed consent! Br J Ophthalmol 79:186-190
    • (1995) Br J Ophthalmol , vol.79 , pp. 186-190
    • Gregory, C.Y.1    Bird, A.C.2
  • 8
    • 0031966698 scopus 로고    scopus 로고
    • Genetic blindness: Current concepts in the pathogenesis of human outer retinal dystrophies
    • Gregory-Evans K, Bhattacharya SS (1998) Genetic blindness: current concepts in the pathogenesis of human outer retinal dystrophies. Trends Genet 14:103-108
    • (1998) Trends Genet , vol.14 , pp. 103-108
    • Gregory-Evans, K.1    Bhattacharya, S.S.2
  • 9
    • 0034050904 scopus 로고    scopus 로고
    • Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
    • Kay MA, Manno CS, Ragni MV et al. (2000) Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nat Genet 24:257-261
    • (2000) Nat Genet , vol.24 , pp. 257-261
    • Kay, M.A.1    Manno, C.S.2    Ragni, M.V.3
  • 10
    • 0033862099 scopus 로고    scopus 로고
    • Early-onset severe rod-cone dystrophy in young children with RPE65 mutations
    • Lorenz B, Gyurus P, Preising M et al. (2000) Early-onset severe rod-cone dystrophy in young children with RPE65 mutations. Invest Ophthalmol Vis Sci 41:2735-2742
    • (2000) Invest Ophthalmol Vis Sci , vol.41 , pp. 2735-2742
    • Lorenz, B.1    Gyurus, P.2    Preising, M.3
  • 11
    • 0036478954 scopus 로고    scopus 로고
    • Chromosomal effects of adeno-associated virus vector integration
    • Miller DG, Rutledge EA, Russell DW (2002) Chromosomal effects of adeno-associated virus vector integration. Nat Genet 30:147-148
    • (2002) Nat Genet , vol.30 , pp. 147-148
    • Miller, D.G.1    Rutledge, E.A.2    Russell, D.W.3
  • 12
    • 0034622122 scopus 로고    scopus 로고
    • A brief review of retinitis pigmentosa and the identified retinitis pigmentosa genes
    • Phelan J, Bok KD (2000) A brief review of retinitis pigmentosa and the identified retinitis pigmentosa genes. Mol Vis 6:116-124
    • (2000) Mol Vis , vol.6 , pp. 116-124
    • Phelan, J.1    Bok, K.D.2
  • 13
    • 0347815878 scopus 로고    scopus 로고
    • Molekulare genetik
    • Augustin AJ (Hrsg). Springer, Berlin Heidelberg New York Tokyo
    • Reichel MB (2000) Molekulare Genetik. In Augustin AJ (Hrsg) Augenheilkunde. Springer, Berlin Heidelberg New York Tokyo, S 1175-1186
    • (2000) Augenheilkunde , pp. 1175-1186
    • Reichel, M.B.1
  • 14
    • 0035086987 scopus 로고    scopus 로고
    • An immune response after intraocular administration of an adenoviral vector containing a beta galactosidase reporter gene slows retinal degeneration in the rd mouse
    • Reichel MB, Bainbridge J, Baker D, Thrasher AJ, Bhattacharya SS, Ali RR (2001) An immune response after intraocular administration of an adenoviral vector containing a beta galactosidase reporter gene slows retinal degeneration in the rd mouse. Br J Ophthalmol 85:341-344
    • (2001) Br J Ophthalmol , vol.85 , pp. 341-344
    • Reichel, M.B.1    Bainbridge, J.2    Baker, D.3    Thrasher, A.J.4    Bhattacharya, S.S.5    Ali, R.R.6
  • 16
    • 0035083297 scopus 로고    scopus 로고
    • Retinal degeneration. Apoptosis as pathomechanism and therapy strategy
    • Reichel MB, Schlichtenbrede F, Paul D, Wiedemann P (2001) Retinal degeneration. Apoptosis as pathomechanism and therapy strategy. Ophthalmologe 98:242-247
    • (2001) Ophthalmologe , vol.98 , pp. 242-247
    • Reichel, M.B.1    Schlichtenbrede, F.2    Paul, D.3    Wiedemann, P.4
  • 17
    • 0035504663 scopus 로고    scopus 로고
    • Gene replacement therapy in the retinal degeneration slow (rds) mouse: The effect on retinal degeneration following partial transduction of the retina
    • Sarra GM, Stephens C, de Alwis M, Bainbridge JW, Smith AJ, Thrasher AJ, Ali RR (2001) Gene replacement therapy in the retinal degeneration slow (rds) mouse: the effect on retinal degeneration following partial transduction of the retina. Hum Mol Genet 10:2353-2361
    • (2001) Hum Mol Genet , vol.10 , pp. 2353-2361
    • Sarra, G.M.1    Stephens, C.2    De Alwis, M.3    Bainbridge, J.W.4    Smith, A.J.5    Thrasher, A.J.6    Ali, R.R.7
  • 19
    • 0034671726 scopus 로고    scopus 로고
    • Age-related macular degeneration. The lipofusion component N-retinyl-N-retinylidene ethanolamine detaches proapoptotic proteins from mitochondria and induces apoptosis in mammalian retinal pigment epithelial cells
    • Suter M, Reme C, Grimm C et al. (2000) Age-related macular degeneration. The lipofusion component N-retinyl-N-retinylidene ethanolamine detaches proapoptotic proteins from mitochondria and induces apoptosis in mammalian retinal pigment epithelial cells. J Biol Chem 275:39625-39630
    • (2000) J Biol Chem , vol.275 , pp. 39625-39630
    • Suter, M.1    Reme, C.2    Grimm, C.3
  • 20
    • 0033653161 scopus 로고    scopus 로고
    • Genetics and phenotypes of RPE65 mutations in inherited retinal degeneration
    • Thompson DA, Gyurus P, Fleischer LL et al. (2000) Genetics and phenotypes of RPE65 mutations in inherited retinal degeneration. Invest Ophthalmol Vis Sci 41:4293-4299
    • (2000) Invest Ophthalmol Vis Sci , vol.41 , pp. 4293-4299
    • Thompson, D.A.1    Gyurus, P.2    Fleischer, L.L.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.