Toward therapy for DYT1 dystonia: Allele-specific silencing of mutant TorsinA

Annals of Neurology

Volumn 53, Issue 6, 2003, Pages 781-787

  Gonzalez Alegre, Pedro ^a   Miller, Victor M ^a   Davidson, Beverly L ^a   Paulson, Henry L ^a,b  

^a UNIVERSITY OF IOWA   (United States)

^b UNIVERSITY OF IOWA HOSPITALS AND CLINICS   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

SMALL NUCLEAR RIBONUCLEOPROTEIN;

ALLELE; ANIMAL CELL; ARTICLE; AUTOSOMAL DOMINANT INHERITANCE; CARBOXY TERMINAL SEQUENCE; DYSTONIA; GENE DELETION; GENE EXPRESSION REGULATION; GENE MUTATION; GENE SILENCING; HETEROZYGOSITY; NEUROLOGIC DISEASE; NONHUMAN; PRIORITY JOURNAL; PROTEIN DEGRADATION; PROTEIN DOMAIN; TISSUE SPECIFICITY;

ALLELES; BLOTTING, WESTERN; CARRIER PROTEINS; CELL CULTURE TECHNIQUES; DYSTONIA; GENE DELETION; GENE SILENCING; GENE THERAPY; HUMANS; MICROSCOPY, FLUORESCENCE; MOLECULAR CHAPERONES; PLASMIDS; POINT MUTATION; RNA, SMALL INTERFERING; TRANSFECTION;

EID: 0038443032     PISSN: 03645134     EISSN: None     Source Type: Journal    
DOI: 10.1002/ana.10548     Document Type: Article

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