Stable micro-dystrophin gene transfer using an integrating adeno-retroviral hybrid vector ameliorates the dystrophic pathology in mdx mouse muscle

Human Molecular Genetics

Volumn 11, Issue 15, 2002, Pages 1719-1730

  Roberts, Michael L ^a   Wells, Dominic J ^b   Graham, Ian R ^a   Fabb, Stewart A ^a   Hill, Vanessa J ^a   Duisit, Ghislaine ^c   Yuasa, Katsutoshi ^d   Takeda, ShiN'Ichi ^d   Cosset, François Loïc ^e   Dickson, George ^a  

^a UNIVERSITY OF LONDON   (United Kingdom)

^b IMPERIAL COLLEGE SCHOOL OF MEDICINE   (United Kingdom)

^c HÔTEL DIEU   (France)

^d NATIONAL INSTITUTE OF NEUROSCIENCE   (Japan)

^e UNIVERSITÉ DE LYON   (France)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; BETA GALACTOSIDASE; DYSTROPHIN; GENOMIC DNA; GLYCOPROTEIN; RETROVIRUS VECTOR; VIRUS PROTEIN;

ANIMAL CELL; ANIMAL TISSUE; ARTICLE; CELL CULTURE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; GENE SEQUENCE; GENE TRANSFER; MOUSE; MOUSE STRAIN; MUSCLE ATROPHY; MUSCLE CELL; MYOTUBE; NONHUMAN; PHENOTYPE; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; PROTEIN EXPRESSION; REVERSE TRANSCRIPTION; SKELETAL MUSCLE; TIBIALIS ANTERIOR MUSCLE; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS HYBRID; ADENOVIRUS; ANIMAL; DISEASE MODEL; GENE THERAPY; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; LACTOSE OPERON; METABOLISM; PATHOPHYSIOLOGY; RETROVIRUS; TRANSGENIC MOUSE; X CHROMOSOME LINKED MUSCULAR DYSTROPHIC MOUSE;

ADENOVIRIDAE; ANIMALIA; MUS MUSCULUS; RNA VIRUSES; UNIDENTIFIED RETROVIRUS;

ADENOVIRIDAE; ANIMALS; DISEASE MODELS, ANIMAL; DYSTROPHIN; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; LAC OPERON; MICE; MICE, INBRED MDX; MICE, TRANSGENIC; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, DUCHENNE; RETROVIRIDAE; TRANSDUCTION, GENETIC;

EID: 0037098953     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/11.15.1719     Document Type: Article

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