-
1
-
-
0021131380
-
Prospects for human gene therapy
-
Anderson, W.F. 1984. Prospects for human gene therapy. Science 226:401-409.
-
(1984)
Science
, vol.226
, pp. 401-409
-
-
Anderson, W.F.1
-
2
-
-
0025279402
-
Progress toward human gene therapy
-
Miller, A.D. 1990. Progress toward human gene therapy. Blood 76:271-278.
-
(1990)
Blood
, vol.76
, pp. 271-278
-
-
Miller, A.D.1
-
3
-
-
0026430686
-
Gene therapeutics
-
Felgner, P.L. and Rhodes, G. 1991. Gene therapeutics. Nature 349:351-352.
-
(1991)
Nature
, vol.349
, pp. 351-352
-
-
Felgner, P.L.1
Rhodes, G.2
-
4
-
-
0026775132
-
Concepts and strategies for human gene therapy
-
Roemer, K. and Friedmann, T. 1992. Concepts and strategies for human gene therapy. Eur. J. Biochem. 208:211-225.
-
(1992)
Eur. J. Biochem
, vol.208
, pp. 211-225
-
-
Roemer, K.1
Friedmann, T.2
-
5
-
-
0028841615
-
Recent advances in the application of gene therapy to human disease
-
Hannania, E.G., Kavanagh, J., Hortobagyi, G., Giles, R.E., Champlin, R., and Deisseroth, A.B. 1995. Recent advances in the application of gene therapy to human disease. Am. J. Med. 99:537-552.
-
(1995)
Am. J. Med
, vol.99
, pp. 537-552
-
-
Hannania, E.G.1
Kavanagh, J.2
Hortobagyi, G.3
Giles, R.E.4
Champlin, R.5
Deisseroth, A.B.6
-
6
-
-
0027980227
-
Cellular gene therapy: An overview
-
Klein, H.G. 1994. Cellular gene therapy: An overview. J. Clin. Apheres. 9:139-141.
-
(1994)
J. Clin. Apheres
, vol.9
, pp. 139-141
-
-
Klein, H.G.1
-
7
-
-
0026486612
-
Gene therapy via primary myoblasts: Long-term expression of fact IX protein following transplantation in vivo
-
Dai, Y., Roman, M., Naviaux, R.K., and Verman, I.M. 1992. Gene therapy via primary myoblasts: Long-term expression of fact IX protein following transplantation in vivo. Proc. Natl. Acad. Sci. USA 89:10892-10895.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 10892-10895
-
-
Dai, Y.1
Roman, M.2
Naviaux, R.K.3
Verman, I.M.4
-
8
-
-
0028825747
-
Gene therapy for cystic fibrosis: Challenges and future directions
-
Wilson, J.M. 1995. Gene therapy for cystic fibrosis: Challenges and future directions. J. Clin. Invest. 96:2547-2554.
-
(1995)
J. Clin. Invest
, vol.96
, pp. 2547-2554
-
-
Wilson, J.M.1
-
9
-
-
0030026531
-
Gene therapy for cystic fibrosis
-
Rosenfeld, M.A. and Collins, F.S. 1996. Gene therapy for cystic fibrosis. Chest 109:241-252.
-
(1996)
Chest
, vol.109
, pp. 241-252
-
-
Rosenfeld, M.A.1
Collins, F.S.2
-
10
-
-
0029789790
-
Cardiovascular gene therapy: Current concepts
-
Fox, J.C. 1996. Cardiovascular gene therapy: Current concepts. Therapeutic Drug Monitoring 18:410-422.
-
(1996)
Therapeutic Drug Monitoring
, vol.18
, pp. 410-422
-
-
Fox, J.C.1
-
11
-
-
0028009619
-
Gene therapy and the hemophilias
-
Lozier, J.N. and Brinkjous, K.M. 1994. Gene therapy and the hemophilias. JAMA 271:47-51.
-
(1994)
JAMA
, vol.271
, pp. 47-51
-
-
Lozier, J.N.1
Brinkjous, K.M.2
-
12
-
-
0026906987
-
Adenovirus-mediated in vivo gene transfer and expression in normal rat liver
-
Haffe, H.A., Danel, C., Longenecker, G., Metzger, M., Setoguchi, Y., Rosenfeld, M.A., et al. 1992. Adenovirus-mediated in vivo gene transfer and expression in normal rat liver. Nature Genetics 1:372-378.
-
(1992)
Nature Genetics
, vol.1
, pp. 372-378
-
-
Haffe, H.A.1
Danel, C.2
Longenecker, G.3
Metzger, M.4
Setoguchi, Y.5
Rosenfeld, M.A.6
-
13
-
-
0027521773
-
Adenovirus-mediated expression of therapeutic plasma levels of human factor IX in mice
-
Smith, T.A., Mehaffey, M.G., Kayda, D.B., Saunders, J.M., Yei, S., Trapnell, B.C., et al. 1993. Adenovirus-mediated expression of therapeutic plasma levels of human factor IX in mice. Nature Genetics 5:397-402.
-
(1993)
Nature Genetics
, vol.5
, pp. 397-402
-
-
Smith, T.A.1
Mehaffey, M.G.2
Kayda, D.B.3
Saunders, J.M.4
Yei, S.5
Trapnell, B.C.6
-
14
-
-
0027272371
-
Efficient adenoviral-mediated ornithine transcarbamylase expression in deficient mouse and human hepatocytes
-
Morsy, M.A., Alford, E.L., Bett, A., Graham, F.L., Caskey, C.T. 1993. Efficient adenoviral-mediated ornithine transcarbamylase expression in deficient mouse and human hepatocytes. J. Clin. Invest. 92:1580-1586.
-
(1993)
J. Clin. Invest
, vol.92
, pp. 1580-1586
-
-
Morsy, M.A.1
Alford, E.L.2
Bett, A.3
Graham, F.L.4
Caskey, C.T.5
-
15
-
-
0027409026
-
Adenovirus-mediated transfer of low density lipoprotein receptor gene acutely accelerates cholersterol clearance in normal mice
-
Herz, J. and Gerard, R.D. 1993. Adenovirus-mediated transfer of low density lipoprotein receptor gene acutely accelerates cholersterol clearance in normal mice. Proc. Natl. Acad. Sci. USA 90:2812-2816.
-
(1993)
Proc. Natl. Acad. Sci. USA
, vol.90
, pp. 2812-2816
-
-
Herz, J.1
Gerard, R.D.2
-
16
-
-
0027723616
-
Adenovirus-mediated correction of the genetic defect in hepatocytes from patients with familial hypercholesterolemia
-
Kozarsky, K., Grossman, M., and Wilson, J.M. 1993. Adenovirus-mediated correction of the genetic defect in hepatocytes from patients with familial hypercholesterolemia. Somatic Cell Molec. Gen. 19:449-458.
-
(1993)
Somatic Cell Molec. Gen
, vol.19
, pp. 449-458
-
-
Kozarsky, K.1
Grossman, M.2
Wilson, J.M.3
-
17
-
-
0027258140
-
Hypercholesterolemia in low density lipoprotein receptor knockout mice and its reversal by adenovirus-mediated gene delivery
-
Ishibashi, S., Brown, M.S., Goldstein, J.L., Gerard, R.D., Hammer, R.E., and Herz, J. 1993. Hypercholesterolemia in low density lipoprotein receptor knockout mice and its reversal by adenovirus-mediated gene delivery. J. Clin. Invest. 92:883-893.
-
(1993)
J. Clin. Invest
, vol.92
, pp. 883-893
-
-
Ishibashi, S.1
Brown, M.S.2
Goldstein, J.L.3
Gerard, R.D.4
Hammer, R.E.5
Herz, J.6
-
18
-
-
0029988465
-
Effective treatment of familial hypercholesterolaemia in the mouse model using adenovirus-mediated transfer of the VLDL receptor gene
-
Kozarsky, K.F., Jooss, K., Donahee, M., Strauss, J.F. III, and Wilson, J.M. 1996. Effective treatment of familial hypercholesterolaemia in the mouse model using adenovirus-mediated transfer of the VLDL receptor gene. Nature Genetics 13:54-62.
-
(1996)
Nature Genetics
, vol.13
, pp. 54-62
-
-
Kozarsky, K.F.1
Jooss, K.2
Donahee, M.3
Strauss, J.4
Wilson, J.M.5
-
19
-
-
0030042794
-
Prolonged metabolic correction in adult ornithine transcarbamylase-deficient mice with adenoviral vectors
-
Ye, X., Robinson, M.B., Batshaw, M.L., Furth, E.E., Smith, I., and Wilson, J.M. 1996. Prolonged metabolic correction in adult ornithine transcarbamylase-deficient mice with adenoviral vectors. J. Biol. Chem. 271:3639-3646.
-
(1996)
J. Biol. Chem
, vol.271
, pp. 3639-3646
-
-
Ye, X.1
Robinson, M.B.2
Batshaw, M.L.3
Furth, E.E.4
Smith, I.5
Wilson, J.M.6
-
20
-
-
0028328261
-
Cellular immunity to viral antigens limits E1-deleted adenoviruses for gene therapy
-
Yang, Y., Nunes, F.A., Berencsi, K., Furth, E.E., Gonczol, E., and Wilson, J.M. 1994. Cellular immunity to viral antigens limits E1-deleted adenoviruses for gene therapy. Proc. Natl. Acad. Sci. USA 91:4407-4411.
-
(1994)
Proc. Natl. Acad. Sci. USA
, vol.91
, pp. 4407-4411
-
-
Yang, Y.1
Nunes, F.A.2
Berencsi, K.3
Furth, E.E.4
Gonczol, E.5
Wilson, J.M.6
-
21
-
-
0029028989
-
Clearance of adenovirus-infected hepatocytes by MHC class I-restricted CD4+ CTLs in vivo
-
Yang, Y. and Wilson, J.M. 1995. Clearance of adenovirus-infected hepatocytes by MHC class I-restricted CD4+ CTLs in vivo. J. Immunol. 155:2564-2570.
-
(1995)
J. Immunol
, vol.155
, pp. 2564-2570
-
-
Yang, Y.1
Wilson, J.M.2
-
22
-
-
0028484704
-
MHC class I-restricted cytotoxic T lymphocytes to viral antigens destroy hepatocytes in mice infected with E1-deleted recombinant adenoviruses
-
Yang, Y., Ertle, H.C., and Wilson, J.M. 1995. MHC class I-restricted cytotoxic T lymphocytes to viral antigens destroy hepatocytes in mice infected with E1-deleted recombinant adenoviruses. Immunity 1:433-442.
-
(1995)
Immunity
, vol.1
, pp. 433-442
-
-
Yang, Y.1
Ertle, H.C.2
Wilson, J.M.3
-
23
-
-
0028937785
-
Cellular and humoral immune responses to viral antigens create barriers to lung-directed gene therapy with recombinant adenoviruses
-
Yang, Y., Li, Q., Ertl, H.C., and Wilson, J.M. 1995. Cellular and humoral immune responses to viral antigens create barriers to lung-directed gene therapy with recombinant adenoviruses. J. Virol. 69:2004-2015.
-
(1995)
J. Virol
, vol.69
, pp. 2004-2015
-
-
Yang, Y.1
Li, Q.2
Ertl, H.C.3
Wilson, J.M.4
-
24
-
-
0025949806
-
Retroviral-mediated gene transfer in hepatocytes in vivo
-
Ferry, N., Duplessis, O., Houssin, D., Danos, O., and Heard, J.-M. 1991. Retroviral-mediated gene transfer in hepatocytes in vivo. Proc. Natl. Acad. Sci. USA 88:8377-8381.
-
(1991)
Proc. Natl. Acad. Sci. USA
, vol.88
, pp. 8377-8381
-
-
Ferry, N.1
Duplessis, O.2
Houssin, D.3
Danos, O.4
Heard, J.-M.5
-
25
-
-
0027748178
-
Hepatic gene therapy: Efficient retroviral-mediated gene transfer into rat hepatocytes in vivo
-
Kolodka, T.M., Finegold, M., and Woo, S.L.C. 1993. Hepatic gene therapy: Efficient retroviral-mediated gene transfer into rat hepatocytes in vivo. Somatic Cell Molec. Gen. 19:491-497.
-
(1993)
Somatic Cell Molec. Gen
, vol.19
, pp. 491-497
-
-
Kolodka, T.M.1
Finegold, M.2
Woo, S.L.C.3
-
26
-
-
0027174251
-
Direct retroviral-mediated transfer of a dystrophin minigene into mdx mouse muscle in vivo
-
Dunckley, M.G., Wells, D.J., Welsh, F.S., and Dickson, G. 1993. Direct retroviral-mediated transfer of a dystrophin minigene into mdx mouse muscle in vivo. Human Molecular Genetics 2:717-723.
-
(1993)
Human Molecular Genetics
, vol.2
, pp. 717-723
-
-
Dunckley, M.G.1
Wells, D.J.2
Welsh, F.S.3
Dickson, G.4
-
27
-
-
0027418929
-
In vivo regional delivery of retrovirally mediated foreign genes to rat liver cells: Need for partial hepatectomy for succcessful foreign gene expression
-
Moscioni, A.D., Rozga, J., Neuzil, D.F., Overell, R.W., Holt, J.T., and Demetriou, A.A. 1993. In vivo regional delivery of retrovirally mediated foreign genes to rat liver cells: Need for partial hepatectomy for succcessful foreign gene expression. Surgery 113:304-311.
-
(1993)
Surgery
, vol.113
, pp. 304-311
-
-
Moscioni, A.D.1
Rozga, J.2
Neuzil, D.F.3
Overell, R.W.4
Holt, J.T.5
Demetriou, A.A.6
-
28
-
-
0027748178
-
Hepatic gene therapy: Efficient retroviral-mediated gene transfer into rat hepatocytes in vivo
-
Kolodka, T.M., Finegold, M., and Woo, S.L.C. 1993. Hepatic gene therapy: Efficient retroviral-mediated gene transfer into rat hepatocytes in vivo. Somatic Cell Molec. Gen. 19:491-497.
-
(1993)
Somatic Cell Molec. Gen
, vol.19
, pp. 491-497
-
-
Kolodka, T.M.1
Finegold, M.2
Woo, S.L.C.3
-
29
-
-
0028351719
-
Intrathecal gene therapy for malignant leptomeningeal neoplasia
-
Ram, Z., Walbridge, S., Oshiro, E.M., Viola, J.J., Chiang, Y., Mueller, S.N., et al. 1994. Intrathecal gene therapy for malignant leptomeningeal neoplasia. Cancer Res. 54:2141-2145.
-
(1994)
Cancer Res
, vol.54
, pp. 2141-2145
-
-
Ram, Z.1
Walbridge, S.2
Oshiro, E.M.3
Viola, J.J.4
Chiang, Y.5
Mueller, S.N.6
-
30
-
-
0025610750
-
Gene delivery to glioma cells in rat brain by grafting of a retrovirus packaging cell line
-
Short, M.P., Choi, B.C., Lee, J.K., Malick, A., Breakefield, X.O., and Martuza, R.L. 1990. Gene delivery to glioma cells in rat brain by grafting of a retrovirus packaging cell line. J. Neurosci. Res. 27:427-433.
-
(1990)
J. Neurosci. Res
, vol.27
, pp. 427-433
-
-
Short, M.P.1
Choi, B.C.2
Lee, J.K.3
Malick, A.4
Breakefield, X.O.5
Martuza, R.L.6
-
31
-
-
0026772206
-
In vivo gene transfer with retroviral vector-producer cells for treatment of experimental brain tumors
-
Culver, K.W., Ram, Z., Walbridge, S., Ishii, H., Oldfield, E.H., and Blaese, R.M. In vivo gene transfer with retroviral vector-producer cells for treatment of experimental brain tumors. Science 256:1550-1552.
-
Science
, vol.256
, pp. 1550-1552
-
-
Culver, K.W.1
Ram, Z.2
Walbridge, S.3
Ishii, H.4
Oldfield, E.H.5
Blaese, R.M.6
-
32
-
-
0027217637
-
An experimental model of retrovirus gene therapy for malignant brain tumors
-
Takamiya, Y., Short, M.P., Moolten, F.L., Fleet, C., Mineta, T., Breakefield, X.O., and Martuza, R.L. 1993. An experimental model of retrovirus gene therapy for malignant brain tumors. J. Neurosurg. 79:104-110.
-
(1993)
J. Neurosurg
, vol.79
, pp. 104-110
-
-
Takamiya, Y.1
Short, M.P.2
Moolten, F.L.3
Fleet, C.4
Mineta, T.5
Breakefield, X.O.6
Martuza, R.L.7
-
33
-
-
0027531548
-
In situ retroviral-mediated gene transfer for the treatment of brain tumors in rats
-
Ram, Z., Culver, K.W., Walbridge, S., Blaese, R.M., and Odfield, E.H. 1993. In situ retroviral-mediated gene transfer for the treatment of brain tumors in rats. Cancer Res. 53:83-88.
-
(1993)
Cancer Res
, vol.53
, pp. 83-88
-
-
Ram, Z.1
Culver, K.W.2
Walbridge, S.3
Blaese, R.M.4
Odfield, E.H.5
-
34
-
-
0027317796
-
Toxicity studies of retroviral-mediated gene transfer for the treatment of brain tumors
-
Ram, Z., Culver, K.W., Walbridge, S., Frank, J.A., Blaese, R.M., and Oldfield, E.H. 1993. Toxicity studies of retroviral-mediated gene transfer for the treatment of brain tumors. J. Neurosurg. 79:400-407.
-
(1993)
J. Neurosurg
, vol.79
, pp. 400-407
-
-
Ram, Z.1
Culver, K.W.2
Walbridge, S.3
Frank, J.A.4
Blaese, R.M.5
Oldfield, E.H.6
-
37
-
-
0029997197
-
Retroviral vector producer cell killing in human serum in mediated by natural antibody and complement: Strategies for evading the humoral immune response
-
Rollins, S.A., Birks, C.W., Setter, E., Squinto, S.P., and Rother, R.P. 1996. Retroviral vector producer cell killing in human serum in mediated by natural antibody and complement: Strategies for evading the humoral immune response. Human Gene Therapy 7:619-626.
-
(1996)
Human Gene Therapy
, vol.7
, pp. 619-626
-
-
Rollins, S.A.1
Birks, C.W.2
Setter, E.3
Squinto, S.P.4
Rother, R.P.5
-
38
-
-
0027236954
-
Production of high-titer helper-free retroviruses by transient transfection
-
Pear, W.S., Nolan, G.P., Scott, M.L., and Baltimore, D. 1993. Production of high-titer helper-free retroviruses by transient transfection. Proc. Natl. Acad. Sci. USA 90:8392-8396.
-
(1993)
Proc. Natl. Acad. Sci. USA
, vol.90
, pp. 8392-8396
-
-
Pear, W.S.1
Nolan, G.P.2
Scott, M.L.3
Baltimore, D.4
-
39
-
-
0028577834
-
Virofection: A new procedure to achieve stable expression of genes transferred into early embryos
-
Flamant, F., Demeneix, B., Benoist, C., Markossian-Belin, S., and Samarut, J. 1994. Virofection: A new procedure to achieve stable expression of genes transferred into early embryos. Int. J. Dev. Biol. 38:751-757.
-
(1994)
Int. J. Dev. Biol
, vol.38
, pp. 751-757
-
-
Flamant, F.1
Demeneix, B.2
Benoist, C.3
Markossian-Belin, S.4
Samarut, J.5
-
40
-
-
0029149328
-
Enhanced transduction efficiency of retroviral vectors coprecipitated with calcium phosphate
-
Morling, F.J. and Russell, S.J. 1995. Enhanced transduction efficiency of retroviral vectors coprecipitated with calcium phosphate. Gene Therapy 2:504-508.
-
(1995)
Gene Therapy
, vol.2
, pp. 504-508
-
-
Morling, F.J.1
Russell, S.J.2
-
41
-
-
0029132243
-
Virofection: A one-step procedure for using replication-defective retrovirus vectors
-
Flamant F. and Samarut, J. 1995. Virofection: A one-step procedure for using replication-defective retrovirus vectors. Virology 211:234-240.
-
(1995)
Virology
, vol.211
, pp. 234-240
-
-
Flamant, F.1
Samarut, J.2
-
42
-
-
0028097848
-
Kat: A high efficiency retroviral transduction system for primary human T lymphocytes
-
Finer, M.H., Dull, T.J., Qin, L., Farson, D., and Roberts, M.R. 1994. kat: A high efficiency retroviral transduction system for primary human T lymphocytes. Blood 83:43-50.
-
(1994)
Blood
, vol.83
, pp. 43-50
-
-
Finer, M.H.1
Dull, T.J.2
Qin, L.3
Farson, D.4
Roberts, M.R.5
-
43
-
-
0029920928
-
Plasmoviruses: Nonviral/viral vectors for gene therapy
-
Noguiez-Hellin, P., Robert-Le Meur, M., Salzmann, J.-L., and Klatzmann, D. 1996. Plasmoviruses: Nonviral/viral vectors for gene therapy. Proc. Natl. Acad. Sci. USA 93:4175-1780.
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
, pp. 4175-4780
-
-
Noguiez-Hellin, P.1
Robert-Le Meur, M.2
Salzmann, J.-L.3
Klatzmann, D.4
-
44
-
-
0028559768
-
An efficient and flexible system for-construction of adenovirus vectors with insertions or deletions in early regions 1 and 3
-
Bett AJ., Haddara W., Prevec L., Graham FL. An efficient and flexible system for-construction of adenovirus vectors with insertions or deletions in early regions 1 and 3. Proc Natl Acad Sci USA 91:8802-6 (1994).
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 8802-8806
-
-
Bett, A.J.1
Haddara, W.2
Prevec, L.3
Graham, F.L.4
-
45
-
-
0028324325
-
High-efficiency gene transfer employing adenovirus-polylysine-DNA complexes
-
Curiel, D.T. 1994. High-efficiency gene transfer employing adenovirus-polylysine-DNA complexes. Natural Immunity 13:141-164.
-
(1994)
Natural Immunity
, vol.13
, pp. 141-164
-
-
Curiel, D.T.1
-
46
-
-
0029823797
-
A novel adenovirus-adeno-associated virus hybrid vector that displays efficient rescue and delivery of the AAV genome
-
Fisher, K.J., Kelley, W.M., Burda, J.F., and Wilson, J.M. 1996. A novel adenovirus-adeno-associated virus hybrid vector that displays efficient rescue and delivery of the AAV genome. Human Gene Therapy 7:2079-2087.
-
(1996)
Human Gene Therapy
, vol.7
, pp. 2079-2087
-
-
Fisher, K.J.1
Kelley, W.M.2
Burda, J.F.3
Wilson, J.M.4
-
47
-
-
0021894711
-
Isolation from cats of an endogenous type C virus with a novel envelope
-
Haapala, D.K., Robey, W.G., Oroszlan, S.D., and Tsai, W.P. 1985. Isolation from cats of an endogenous type C virus with a novel envelope. J. Virology 53:827-833.
-
(1985)
J. Virology
, vol.53
, pp. 827-833
-
-
Haapala, D.K.1
Robey, W.G.2
Oroszlan, S.D.3
Tsai, W.P.4
|