Enzyme therapy for Pompe disease: From science to industrial enterprise

European Journal of Pediatrics, Supplement

Volumn 161, Issue 1, 2002, Pages S106-S111

  Reuser, Arnold J J ^a   Van Den Hout, Hannerieke ^b   Bijvoet, Agnes G A ^a   Kroos, Marian A ^a   Verbeet, Martin P ^c   Van Der Ploeg, Ans T ^b  

^a ERASMUS UNIVERSITY ROTTERDAM   (Netherlands)

^b SOPHIA CHILDREN S HOSPITAL   (Netherlands)

^c LEIDEN UNIVERSITY   (Netherlands)

Author keywords

Acid maltase deficiency; Enzyme therapy; Glycogenosis; Lysosomal storage disease; Transgene technology

Indexed keywords

GLUCAN 1,4 ALPHA GLUCOSIDASE; RECOMBINANT ENZYME;

BIRTH; CARDIOMEGALY; CHO CELL; CLINICAL FEATURE; CLINICAL TRIAL; CONFERENCE PAPER; DRUG EFFICACY; DRUG SYNTHESIS; ENZYME ACTIVITY; ENZYME REPLACEMENT; ERYTHEMA; FEVER; FLUSHING; GLYCOGEN STORAGE DISEASE TYPE 2; HISTORY; HUMAN; MALAISE; METABOLIC DISORDER; METHODOLOGY; MILK; MOLECULAR CLONING; MUSCLE WEAKNESS; MYOPATHY; NONHUMAN; ONSET AGE; PRIORITY JOURNAL; RABBIT; SCIENCE; SIDE EFFECT; SWEATING; TACHYCARDIA; TECHNOLOGY; TRANSGENIC ANIMAL; TREATMENT OUTCOME;

ALPHA-GLUCOSIDASES; ANIMALS; ANIMALS, GENETICALLY MODIFIED; CRICETINAE; CRICETULUS; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; RABBITS;

EID: 0036390045     PISSN: 09439676     EISSN: None     Source Type: Journal    
DOI: 10.1007/bf02680006     Document Type: Article

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