-
1
-
-
0028904215
-
Prospects for gene therapy of haemophilia A and B
-
Brownlee GG. Prospects for gene therapy of haemophilia A and B. Br Med Bull, 1995; 51: 91-105.
-
(1995)
Br Med Bull
, vol.51
, pp. 91-105
-
-
Brownlee, G.G.1
-
3
-
-
0030797290
-
Gene therapy for hemophilia A
-
Connelly S, Kaleko M. Gene therapy for hemophilia A. Thromb Haemost, 1997; 78: 31-6.
-
(1997)
Thromb Haemost
, vol.78
, pp. 31-36
-
-
Connelly, S.1
Kaleko, M.2
-
4
-
-
0030611287
-
Viral vector-mediated gene therapy for hemophilia B
-
Eisensmith RC, Woo SL. Viral vector-mediated gene therapy for hemophilia B. Thromb Haemost, 1997; 78: 24-30.
-
(1997)
Thromb Haemost
, vol.78
, pp. 24-30
-
-
Eisensmith, R.C.1
Woo, S.L.2
-
5
-
-
0031698579
-
Problems and prospects in gene therapy for hemophilia
-
Herzog RW, High KA. Problems and prospects in gene therapy for hemophilia. Curr Opin Hematol, 1998; 5: 321-6.
-
(1998)
Curr Opin Hematol
, vol.5
, pp. 321-326
-
-
Herzog, R.W.1
High, K.A.2
-
6
-
-
0027163743
-
Gene therapy of hemophilia B
-
Kurachi K, Yao SN. Gene therapy of hemophilia B. Thromb Haemost, 1993; 70: 193-7.
-
(1993)
Thromb Haemost
, vol.70
, pp. 193-197
-
-
Kurachi, K.1
Yao, S.N.2
-
7
-
-
16944364154
-
Putting muscle to work for gene therapy
-
Miller AD. Putting muscle to work for gene therapy. Nat Med, 1997; 3: 278-9.
-
(1997)
Nat Med
, vol.3
, pp. 278-279
-
-
Miller, A.D.1
-
8
-
-
0029144825
-
Progress towards gene therapy for the hemophilias
-
Thompson AR. Progress towards gene therapy for the hemophilias. Thromb Haemost, 1995; 74: 45-51.
-
(1995)
Thromb Haemost
, vol.74
, pp. 45-51
-
-
Thompson, A.R.1
-
9
-
-
0025039252
-
Gene therapy
-
Verma IM. Gene therapy. Sci Am, 1990; 263(68-72): 81-4.
-
(1990)
Sci Am
, vol.263
, Issue.68-72
, pp. 81-84
-
-
Verma, I.M.1
-
10
-
-
2642705886
-
Human factor IX transgenic sheep produced by transfer of nuclei from transfected fetal fibroblasts
-
Schnieke AE, Kind AJ, Ritchie WA et al. Human factor IX transgenic sheep produced by transfer of nuclei from transfected fetal fibroblasts. Science, 1997; 278: 2130-3.
-
(1997)
Science
, vol.278
, pp. 2130-2133
-
-
Schnieke, A.E.1
Kind, A.J.2
Ritchie, W.A.3
-
11
-
-
0031953132
-
In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides
-
Kren BT, Bandyopadhyay P, Steer CJ. In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides. Nature Med, 1998; 4: 285-90.
-
(1998)
Nature Med
, vol.4
, pp. 285-290
-
-
Kren, B.T.1
Bandyopadhyay, P.2
Steer, C.J.3
-
12
-
-
85003544373
-
Intravenous retroviral vectors expressing human factor VIII results in longterm expression in rabbits of various age groups
-
Abstract
-
Greengard JS, Bodner M, McCormack J et al. Intravenous retroviral vectors expressing human factor VIII results in longterm expression in rabbits of various age groups. Blood, 1998; 92(Suppl. 1): 296a(Abstract).
-
(1998)
Blood
, vol.92
, Issue.1 SUPPL.
-
-
Greengard, J.S.1
Bodner, M.2
McCormack, J.3
-
13
-
-
0002303806
-
Safety and efficacy of a second generation, B-domain deleted recombinant factor VIII (r-VIII SQ) in previously treated patients (PTPs). a four year update
-
Abstract
-
Kessler CM, Spira J, Magill M. Safety and efficacy of a second generation, B-domain deleted recombinant factor VIII (r-VIII SQ) in previously treated patients (PTPs). A four year update. Blood, 1998; 92(Suppl. 1): 555a(Abstract).
-
(1998)
Blood
, vol.92
, Issue.1 SUPPL.
-
-
Kessler, C.M.1
Spira, J.2
Magill, M.3
-
14
-
-
0002303808
-
A four-year update of safety and efficacy of a second generation B-domain deleted factor VIII (R-VIII SQ) in previously untreated hemophilia a patients
-
Abstract
-
Lusher JM, Spira J, Magill M. A four-year update of safety and efficacy of a second generation B-domain deleted factor VIII (R-VIII SQ) in previously untreated hemophilia A patients. Blood, 1998; 92(Suppl. 1): 555a(Abstract).
-
(1998)
Blood
, vol.92
, Issue.1 SUPPL.
-
-
Lusher, J.M.1
Spira, J.2
Magill, M.3
-
15
-
-
0030716959
-
Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors
-
Kafri T, Blomer U, Peterson DA, Gage FH, Verma IM. Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors. Nat Genet, 1997; 17: 314-7.
-
(1997)
Nat Genet
, vol.17
, pp. 314-317
-
-
Kafri, T.1
Blomer, U.2
Peterson, D.A.3
Gage, F.H.4
Verma, I.M.5
-
16
-
-
0032080179
-
Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy
-
Connelly S, Andrews JL, Gallo AM et al. Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy. Blood, 1998; 91: 3273-81.
-
(1998)
Blood
, vol.91
, pp. 3273-3281
-
-
Connelly, S.1
Andrews, J.L.2
Gallo, A.M.3
-
17
-
-
0030809684
-
Complementation of helper-dependent adenoviral vectors: Size effects and titer fluctuations
-
Alemany R, Dai Y, Lou YC et al. Complementation of helper-dependent adenoviral vectors: size effects and titer fluctuations. J Virol Methods, 1997; 68: 147-59.
-
(1997)
J Virol Methods
, vol.68
, pp. 147-159
-
-
Alemany, R.1
Dai, Y.2
Lou, Y.C.3
-
18
-
-
17444372024
-
Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors
-
Snyder RO, Miao CH, Meuse L et al. Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors. Nat Med, 1999; 5: 64-70.
-
(1999)
Nat Med
, vol.5
, pp. 64-70
-
-
Snyder, R.O.1
Miao, C.H.2
Meuse, L.3
-
19
-
-
17444387438
-
Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector
-
Herzog RW, Yang EY, Couto LB et al. Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector. Nat Med, 1999; 5: 56-63.
-
(1999)
Nat Med
, vol.5
, pp. 56-63
-
-
Herzog, R.W.1
Yang, E.Y.2
Couto, L.B.3
-
20
-
-
6744242167
-
An adenoassociated/adenovirus hybrid vector generates high-level human factor VIII in vitro
-
Gnatenko D, Hearing P, Jesty J, Bahou W. An adenoassociated/adenovirus hybrid vector generates high-level human factor VIII in vitro. Blood, 1998; 92(Suppl. 1): 146a.
-
(1998)
Blood
, vol.92
, Issue.1 SUPPL.
-
-
Gnatenko, D.1
Hearing, P.2
Jesty, J.3
Bahou, W.4
|