Early umbilical cord blood-derived stem cell transplantation does not prevent neurological deterioration in mucopolysaccharidosis type III

JIMD Reports

Volumn 18, Issue , 2015, Pages 63-68

  Welling, Lindsey ^a   Marchal, Jan Pieter ^a   van Hasselt, Peter ^b   van der Ploeg, Ans T ^c   Wijburg, Frits A ^a   Boelens, Jaap Jan ^b  

^a UNIVERSITY OF AMSTERDAM   (Netherlands)

^b UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^c ERASMUS MEDICAL CENTER   (Netherlands)

Author keywords

Central nervous system disease; Developmental quotient; Hematopoietic stem cell transplantation; Lysosomal storage disease; Umbilical cord blood transplantation

Indexed keywords

EID: 85060340912     PISSN: 21928304     EISSN: 21928312     Source Type: Book Series    
DOI: 10.1007/8904_2014_350     Document Type: Chapter

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