Natural history of Sanfilippo syndrome type A

Journal of Inherited Metabolic Disease

Volumn 37, Issue 3, 2014, Pages 431-437

  Buhrman, Dakota ^a   Thakkar, Kavita ^a   Poe, Michele ^a   Escolar, Maria L ^a  

^a CHILDREN S HOSPITAL OF PITTSBURGH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADAPTIVE BEHAVIOR; ADOLESCENT; AGGRESSION; ARTICLE; BEHAVIOR CHANGE; CHEWING DIFFICULTY; CHILD; CHILD REARING; CLINICAL ARTICLE; CONTROLLED STUDY; EVALUATION STUDY; FACE DEFORMITY; FEMALE; GROWTH; HEAD AND NECK DISEASE; HEARING IMPAIRMENT; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEPATOMEGALY; HUMAN; HYPERACTIVITY; INFANT; LANGUAGE; LANGUAGE DELAY; MALE; MASTICATION; MOTOR PERFORMANCE; RETROSPECTIVE STUDY; SANFILIPPO SYNDROME; SANFILIPPO SYNDROME TYPE A; SLEEP DISORDER; SPEECH; SPEECH DELAY; TERATOLOGY; TONGUE DISEASE; TOOTH MALFORMATION; COGNITION; HEARING LOSS; MUCOPOLYSACCHARIDOSIS III; PRESCHOOL CHILD; PSYCHOLOGY;

ADAPTATION, PSYCHOLOGICAL; ADOLESCENT; CHILD; CHILD, PRESCHOOL; COGNITION; FEMALE; HEARING LOSS; HUMANS; INFANT; MALE; MUCOPOLYSACCHARIDOSIS III; RETROSPECTIVE STUDIES;

EID: 84904209461     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-013-9661-8     Document Type: Article

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