Generation of a gene-corrected isogenic control iPSC line from cystic fibrosis patient-specific iPSCs homozygous for p.Phe508del mutation mediated by TALENs and ssODN

Stem Cell Research

Volumn 23, Issue , 2017, Pages 95-97

  Merkert, Sylvia ^a,b   Bednarski, Christien ^c   Göhring, Gudrun ^a   Cathomen, Toni ^c   Martin, Ulrich ^a,b  

^a HANNOVER MEDICAL SCHOOL   (Germany)

^b Biomedical Research in Endstage and Obstructive Lung Disease (BREATH)   (Germany)

^c UNIVERSITY OF FREIBURG   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; OLIGONUCLEOTIDE; PHENYLALANINE; TRANSCRIPTION ACTIVATOR LIKE EFFECTOR NUCLEASE; OLIGODEOXYRIBONUCLEOTIDE;

ALLELE; AMINO ACID SEQUENCE; ANIMAL CELL; ARTICLE; CFTR GENE; CYSTIC FIBROSIS; GENE; GENE MUTATION; HOMOZYGOSITY; HUMAN; HUMAN CELL; IMMUNOFLUORESCENCE; IMMUNOHISTOCHEMISTRY; INDUCED PLURIPOTENT STEM CELL; MOUSE; NONHUMAN; PRIORITY JOURNAL; CELL LINE; GENETICS; HOMOZYGOTE; MALE; METABOLISM; MUTATION; NUCLEOTIDE SEQUENCE; PATHOLOGY;

BASE SEQUENCE; CELL LINE; CYSTIC FIBROSIS; HOMOZYGOTE; HUMANS; INDUCED PLURIPOTENT STEM CELLS; MALE; MUTATION; OLIGODEOXYRIBONUCLEOTIDES; TRANSCRIPTION ACTIVATOR-LIKE EFFECTOR NUCLEASES;

EID: 85023621630     PISSN: 18735061     EISSN: 18767753     Source Type: Journal    
DOI: 10.1016/j.scr.2017.07.010     Document Type: Article

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