Sickle cell disease: An international survey of results of HLA-identical sibling hematopoietic stem cell transplantation

Blood

Volumn 129, Issue 11, 2017, Pages 1548-1556

  Gluckman, Eliane ^a,b   Cappelli, Barbara ^b   Bernaudin, Francoise ^c   Labopin, Myriam ^d   Volt, Fernanda ^a,b   Carreras, Jeanette ^e   Simões, Belinda Pinto ^f   Ferster, Alina ^g   Dupont, Sophie ^h   De La Fuente, Josu ^i,cs   Dalle, Jean Hugues ^j   Zecca, Marco ^k   Walters, Mark C ^l   Krishnamurti, Lakshmanan ^m   Bhatia, Monica ⁿ   Leung, Kathryn ^o   Yanik, Gregory ^p   Kurtzberg, Joanne ^q   Dhedin, Nathalie ^r   Kuentz, Mathieu ^c   Michel, Gerard ^s,ar   Apperley, Jane ^t   Lutz, Patrick ^u,ax   Neven, Bénédicte ^v   Bertrand, Yves ^w,aq   Vannier, Jean Pierre ^x,av   Ayas, Mouhab ^y   Cavazzana, Marina ^d,v,z   Matthes Martin, Susanne ^aa   Rocha, Vanderson ^a,f,ab   Elayoubi, Hanadi ^a,b   Kenzey, Chantal ^a,b   Bader, Peter ^ac   Locatelli, Franco ^ad,ae   Ruggeri, Annalisa ^a,b,af   Eapen, Mary ^e   Bordon, Victoria ^ag   Labarque, Veerle ^ah   Pereira, Maguy ^ai   Bittencourt, Henrique ^aj   Petersen, Heidi ^ak   Deconninck, Eric ^al   Jubert, Charlotte ^am   Perrin, Jean ^an   Cahn, Jean Yves ^ao   Bruno, Bénédicte ^ap   Bordigoni, Pierre ^as   Mechinaud, Francoise ^at   Vernant, Jean Paul ^au   Stephan, Jean Luis ^aw   Suttorp, Meinolf ^ay   Strahm, Brigitte ^az   Da Cunha, Claudia Bettoni ^ba   Garwer, Birgit ^bb   Rothmayer, Margarete ^bc   Wendelin, Knut ^bd   Graphakos, Stelios ^be   Tbakhi, Abdelghani ^bf   Naeimi, Nooshin ^bg   Zuckerman, Tsila ^bh   Sharon, Pantel Bakst ^bi   Yaniv, Isaac ^bj   Amos, Toren ^bk   Prete, Arcangelo ^bl   Lo Nigro, Luca ^bm   Lanino, Edoardo ^bn   Faraci, Maura ^bn   Ciceri, Fabio ^bo   Marktel, Sarah ^bo   De Simone, Giusy ^bp   Messina, Chiara ^bq   Bartolomeo, Paolo D I ^br   Santarone, Stella ^br   Vallisa, Daniele ^bs   Bertaina, Alice ^ad   Arcese, William ^bt   Foa, Roberto ^bu   Berger, Massimo ^bv   Maximova, Natalia ^bw   Wallet, Sylwia ^bx   Bazuaye, G N ^by   Maschan, Alexei ^bz   De Heredia, Cristina Diaz ^ca   Bieler, C Belendez ^cb   Pato, Julia Ruiz ^cc   Heras, Inmaculata ^cd   Trevor, Reyhana ^ce   Abayomi, Kym ^ce   Thomson, Jackie ^cf   Fasth, Anders ^cg   Frödin, Ulla ^ch   Ljugman, Per ^ci   Ansari, Marc ^cj   Güngör, Tayfun ^ck   Unal, Emel ^cl   Pehlivan, Mustafa ^cm   Anak, Sema ^cn   Ozturk, Gulyuz ^cn   Unal, Ali ^co   Lawson, Sarah ^cp   Keshani, Jagoda ^cq   Drake, Andy ^cr   Wynn, Robert ^ct   Williams, Janet ^cu   Jagsia, Madan ^cv   Leung, Wing ^cw   Abraham, Allistar ^cx   Sahdey, Indria ^cy   Margolis, David ^cz   Eames, Gretchen ^da   Horwitz, Edwin ^db   Cowan, Mortan ^dc   Kapoor, Neena ^dd   Rowley, Scott ^de   Megason, Gail ^df   Rogers, Zora ^dg   Bolaños Meade, Javier ^dh   Hudspeth, Michelle ^di   Rosenthal, Joseph ^dj   Olson, Timothy ^dk   Kassow, Kimberly ^dl   Selby, George ^dm   Haines, Hillary ^dn   Chaudhury, Sonali ^do   more..

^a UNIVERSITÉ PARIS DESCARTES   (France)

^b CENTRE SCIENTIFIQUE DE MONACO   (Monaco)

^c CENTRE HOSPITALIER INTERCOMMUNAL DE CRÉTEIL   (France)

^d ASSISTANCE PUBLIQUE HÔPITAUX DE PARIS   (France)

^e MEDICAL COLLEGE OF WISCONSIN   (United States)

^f UNIVERSITY OF SÃO PAULO   (Brazil)

^g HOP UNIV DES ENFANTS REINE FABIOLA   (Belgium)

^h CLINIQUES UNIVERSITAIRES SAINT LUC   (Belgium)

ⁱ IMPERIAL COLLEGE LONDON   (United Kingdom)

^j HÔPITAL ROBERT DEBRÉ   (France)

^k FONDAZIONE IRCCS POLICLINICO SAN MATTEO   (Italy)

^l CHILDREN S HOSPITAL OAKLAND   (United States)

^m CHILDREN'S HEALTHCARE OF ATLANTA   (United States)

ⁿ NEW YORK PRESBYTERIAN HOSPITAL   (United States)

^o BAYLOR COLLEGE OF MEDICINE   (United States)

^p CHILDREN'S HOSPITAL OF MICHIGAN   (United States)

^q DUKE UNIVERSITY MEDICAL CENTER   (United States)

^r SAINT LOUIS HOSPITAL   (France)

^s AIX MARSEILLE UNIVERSITY   (France)

^t HAMMERSMITH HOSPITAL   (United Kingdom)

^u UNIVERSITY HOSPITAL OF STRASBOURG   (France)

^v HÔPITAL NECKER ENFANTS MALADES   (France)

^w HOSPICES CIVILS DE LYON   (France)

^x UNIVERSITÉ DE ROUEN   (France)

^y KING FAISAL SPECIALIST HOSPITAL AND RESEARCH CENTER   (Saudi Arabia)

^z PARIS DESCARTES SORBONNE PARIS CITÉ UNIVERSITY   (France)

^aa ST ANNA CHILDREN S HOSPITAL   (Austria)

^ab CHURCHILL HOSPITAL   (United Kingdom)

^ac UNIVERSITY HOSPITAL FRANKFURT   (Germany)

^ad BAMBINO GESÙ CHILDREN S HOSPITAL   (Italy)

^ae UNIVERSITY OF PAVIA   (Italy)

^af HÔPITAL SAINT ANTOINE   (France)

^ag GHENT UNIVERSITY HOSPITAL   (Belgium)

^ah UNIVERSITY HOSPITALS LEUVEN   (Belgium)

^ai UNIVERSITY OF LIÈGE   (Belgium)

^aj UNIVERSITY OF MONTREAL   (Canada)

^ak University of Copenhagen   (Denmark)

^al HÔPITAL SAINT JACQUES   (France)

^am HÔPITAL PELLEGRIN   (France)

^an HÔTEL DIEU   (France)

^ao CHU La Tronche and University   (France)

^ap LILLE UNIVERSITY HOSPITAL   (France)

^aq Institute of Pediatric Hematology and Oncology   (France)

^ar TIMONE HOSPITAL   (France)

^as CHU NANCY BRABOIS   (France)

^at HÔTEL DIEU   (France)

^au Hôpital de la Pitié Salpêtrière APHP   (France)

^av HÔPITAL CHARLES NICOLLE   (France)

^aw HÔPITAL NORD   (France)

^ax HÔPITAL DE HAUTEPIERRE   (France)

^ay UNIVERSITY HOSPITAL CARL GUSTAV CARUS   (Germany)

^az UNIVERSITY OF FREIBURG   (Germany)

^ba HANNOVER MEDICAL SCHOOL   (Germany)

^bb Eppendorf University   (Germany)

^bc LUDWIG MAXIMILIANS UNIVERSITY   (Germany)

^bd KLINIKUM NÜRNBERG   (Germany)

^be Pediatric Hospital Saint Sophia   (Greece)

^bf King Hussein Cancer Centre   (Jordan)

^bg TEHRAN UNIVERSITY OF MEDICAL SCIENCES   (Iran)

^bh RAMBAM MEDICAL CENTER   (Israel)

^bi HADASSAH HEBREW UNIVERSITY MEDICAL CENTER   (Israel)

^bj SCHNEIDER CHILDREN S MEDICAL CENTER OF ISRAEL   (Israel)

^bk Edmond and Lily Safra Children s Hospital   (United States)

^bl UNIVERSITY OF BOLOGNA   (Italy)

^bm Ospedale Ferrarotto   (Italy)

^bn G GASLINI INSTITUTE   (Italy)

^bo SAN RAFFAELE HOSPITAL   (Italy)

^bp Ematologia Pediatrica   (Italy)

^bq Clinica di Oncoematologia Pediatrica   (Italy)

^br Ospedale Civile   (Italy)

^bs GUGLIELMO DA SALICETO HOSPITAL   (Italy)

^bt TOR VERGATA UNIVERSITY HOSPITAL   (Italy)

^bu SAPIENZA UNIVERSITY OF ROME   (Italy)

^bv REGINA MARGHERITA CHILDREN S HOSPITAL   (Italy)

^bw INSTITUTE FOR MATERNAL AND CHILD HEALTH IRCCS BURLO GAROFOLO   (Italy)

^bx Malicka University Hospital   (Netherlands)

^by UNIVERSITY OF BENIN   (Nigeria)

^bz Russian Children's Hospital   (Russian Federation)

^ca HOSPITAL UNIVERSITARI VALL D HEBRON   (Spain)

^cb HOSPITAL GENERAL UNIVERSITARIO GREGORIO MARAÑÓN   (Spain)

^cc HOSPITAL INFANTIL UNIVERSITARIO NIÑO JESÚS   (Spain)

^cd HOSPITAL MORALES MESEGUER   (Spain)

^ce Medi Clinic Constantiaberg   (South Africa)

^cf Pretoria Gynaecological Hospital   (South Africa)

^cg SAHLGRENSKA UNIVERSITY HOSPITAL   (Sweden)

^ch LINKÖPING UNIVERSITY HOSPITAL   (Sweden)

^ci KAROLINSKA UNIVERSITY HOSPITAL   (Sweden)

^cj Hopitaux Universitaires Pediatric Department   (Switzerland)

^ck UNIVERSITY CHILDREN S HOSPITAL   (Switzerland)

^cl Cebeci Medical Center   (Turkey)

^cm GAZIANTEP UNIVERSITY   (Turkey)

^cn ISTANBUL UNIVERSITY   (Turkey)

^co ERCIYES UNIVERSITY   (Turkey)

^cp BIRMINGHAM CHILDREN S HOSPITAL   (United Kingdom)

^cq ROYAL FREE HOSPITAL   (United Kingdom)

^cr St George University   (United Kingdom)

^cs ST MARY S HOSPITAL   (United Kingdom)

^ct NATIONAL HEALTH SERVICE   (United Kingdom)

^cu Sheffield Bone Meta Multidisc Team   (United Kingdom)

^cv VANDERBILT UNIVERSITY   (United States)

^cw ST JUDE CHILDREN S RESEARCH HOSPITAL   (United States)

^cx CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

^cy Northwell Health   (United States)

^cz Children's Hospital of Wisconsin   (United States)

^da The Jane and John Justin Neuroscience Center   (United States)

^db NATIONWIDE CHILDREN S HOSPITAL   (United States)

^dc UNIVERSITY OF CALIFORNIA   (United States)

^dd CHILDREN S HOSPITAL LOS ANGELES   (United States)

^de HACKENSACK UNIVERSITY MEDICAL CENTER   (United States)

^df UNIVERSITY OF MISSISSIPPI MEDICAL CENTER   (United States)

^dg CHILDREN S MEDICAL CENTER   (United States)

^dh JOHNS HOPKINS UNIVERSITY   (United States)

^di MEDICAL UNIVERSITY OF SOUTH CAROLINA   (United States)

^dj CITY OF HOPE NATIONAL MEDICAL CENTER   (United States)

^dk CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^dl UNIVERSITY OF NORTH CAROLINA HOSPITALS   (United States)

^dm University of Oklahoma Medical Center   (United States)

^dn UNIVERSITY OF ALABAMA AT BIRMINGHAM   (United States)

^do CHILDREN'S MEMORIAL HOSPITAL   (United States)

more..

Author keywords

[No Author keywords available]

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN A; FLUDARABINE; HLA ANTIGEN; MELPHALAN; METHOTREXATE; MYCOPHENOLATE MOFETIL; OKT 3; TACROLIMUS; THYMOCYTE ANTIBODY;

ADOLESCENT; ADULT; ARTICLE; BLEEDING; BONE MARROW; CHILD; EVENT FREE SURVIVAL; FEMALE; FOLLOW UP; GRAFT FAILURE; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; MAJOR CLINICAL STUDY; MALE; METASTASIS; MYELOABLATIVE CONDITIONING; OVERALL SURVIVAL; PRIORITY JOURNAL; REDUCED INTENSITY CONDITIONING; RETROSPECTIVE STUDY; RISK FACTOR; SIBLING; SICKLE CELL ANEMIA; T CELL DEPLETION; UMBILICAL CORD BLOOD; WHOLE BODY RADIATION; ANEMIA, SICKLE CELL; CLINICAL TRIAL; DISEASE FREE SURVIVAL; GRAFT SURVIVAL; HISTOCOMPATIBILITY; INFANT; MORTALITY; MULTICENTER STUDY; PRESCHOOL CHILD; PROCEDURES; QUESTIONNAIRE; SURVIVAL RATE; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

ADOLESCENT; ANEMIA, SICKLE CELL; CHILD; CHILD, PRESCHOOL; DISEASE-FREE SURVIVAL; FEMALE; GRAFT SURVIVAL; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HISTOCOMPATIBILITY; HLA ANTIGENS; HUMANS; INFANT; MALE; SIBLINGS; SURVEYS AND QUESTIONNAIRES; SURVIVAL RATE; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

EID: 85015934863     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2016-10-745711     Document Type: Article

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