Haematopoietic stem cell transplantation for sickle cell disease – current practice and new approaches

British Journal of Haematology

Volumn 174, Issue 4, 2016, Pages 515-525

  Arnold, Staci D ^a   Bhatia, Monica ^b   Horan, John ^a   Krishnamurti, Lakshmanan ^a  

^a CHILDREN'S HEALTHCARE OF ATLANTA   (United States)

^b Department of Medicine   (United States)

Author keywords

SCT; sickle cell disease; Transplantation

Indexed keywords

ABATACEPT; HEMOGLOBIN BETA CHAIN;

AUTOLOGOUS GENE EDITING; BONE MARROW; CD34 SELECTION; CHRONIC GRAFT VERSUS HOST DISEASE; CLINICAL EFFECTIVENESS; COMPARATIVE EFFECTIVENESS; DONOR; DONOR SELECTION; GENE THERAPY; GENETIC PROCEDURES; GONAD FUNCTION; HAPLOIDENTICAL RELATED DONOR; HBB GENE; HEALTH CARE COST; HEALTH CARE QUALITY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; MATCHED SIBLING DONOR; MEDICAL PRACTICE; MULTICENTER STUDY (TOPIC); PATIENT SAFETY; PHASE 2 CLINICAL TRIAL (TOPIC); PREIMPLANTATION GENETIC DIAGNOSIS; PRIORITY JOURNAL; QUALITY OF LIFE; RANDOMIZED CONTROLLED TRIAL (TOPIC); REVIEW; SICKLE CELL ANEMIA; UMBILICAL CORD BLOOD; UNRELATED DONORS;

EID: 84982893702     PISSN: 00071048     EISSN: 13652141     Source Type: Journal    
DOI: 10.1111/bjh.14167     Document Type: Review

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