Complete restoration of multiple dystrophin isoforms in genetically corrected Duchenne muscular dystrophy patient–derived cardiomyocytes

Molecular Therapy Methods and Clinical Development

Volumn 1, Issue , 2014, Pages 1-

  Zatti, Susi ^a,b   Martewicz, Sebastian ^a,b   Serena, Elena ^a,b   Uno, Narumi ^c   Giobbe, Giovanni ^a,b   Kazuki, Yasuhiro ^c   Oshimura, Mitsuo ^c   Elvassore, Nicola ^a,b  

^a UNIVERSITY OF PADOVA   (Italy)

^b VENETIAN INSTITUTE OF MOLECULAR MEDICINE   (Italy)

^c TOTTORI UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA ACTININ; CONNEXIN 43; DYSTROPHIN; F ACTIN; ISOPROTEIN; MESSENGER RNA; VENTRICULAR MYOSIN;

AMPLICON; ANIMAL CELL; ARTICLE; CARDIAC MUSCLE CELL; CELL ADHESION; CELL DIFFERENTIATION; CELL LINEAGE; CELL MATURATION; CELL STIMULATION; CELLULAR DISTRIBUTION; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; EMBRYO; EXON; EXON SKIPPING; GENE ACTIVATION; HEART TISSUE; HUMAN; HUMAN ARTIFICIAL CHROMOSOME; HUMAN CELL; HUMAN TISSUE; IMMUNOFLUORESCENCE; INDUCED PLURIPOTENT STEM CELL; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SARCOMERE;

EID: 85015693946     PISSN: None     EISSN: 23290501     Source Type: Journal    
DOI: 10.1038/mtm.2013.1     Document Type: Article

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