U1 snRNA as an effective vector for stable expression of antisense molecules and for the inhibition of the splicing reaction

Methods in Molecular Biology

Volumn 867, Issue , 2012, Pages 239-257

  Martone, Julie ^a   De Angelis, Fernanda Gabriella ^a   Bozzoni, Irene ^a  

^a SAPIENZA UNIVERSITY OF ROME   (Italy)

Author keywords

Duchenne muscular dystrophy; Fibroblast reprogramming; Lentivirus; Luciferase constructs for exon skipping; U1 snRNA

Indexed keywords

COMPLEMENTARY RNA; DYSTROPHIN; FIREFLY LUCIFERASE; SMALL NUCLEAR RNA; U1 SMALL NUCLEAR RNA;

ANIMAL; ARTICLE; CELL CULTURE; DUCHENNE MUSCULAR DYSTROPHY; EXON; FIBROBLAST; GENE THERAPY; GENE VECTOR; GENETICS; HELA CELL; HUMAN; LENTIVIRINAE; METABOLISM; METHODOLOGY; MOLECULAR CLONING; MOUSE; MYOBLAST; RNA SPLICING;

ANIMALS; CELLS, CULTURED; CLONING, MOLECULAR; DYSTROPHIN; EXONS; FIBROBLASTS; GENE THERAPY; GENETIC VECTORS; HELA CELLS; HUMANS; LENTIVIRUS; LUCIFERASES, FIREFLY; MICE; MUSCULAR DYSTROPHY, DUCHENNE; MYOBLASTS; RNA SPLICING; RNA, ANTISENSE; RNA, SMALL NUCLEAR;

ANIMALIA; LENTIVIRUS; MUS;

EID: 84859834957     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-61779-767-5_16     Document Type: Article

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