Long-Term functional outcomes of children with hurler syndrome treated with unrelated umbilical cord blood transplantation

JIMD Reports

Volumn 20, Issue , 2015, Pages 77-86

  Coletti, Hannah Y ^a   Aldenhoven, Mieke ^b   Yelin, Karina ^a   Poe, Michele D ^c   Kurtzberg, Joanne ^d   Escolar, Maria L ^c  

^a UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY MEDICAL CENTER UTRECHT   (Netherlands)

^c CHILDREN S HOSPITAL OF PITTSBURGH   (United States)

^d DUKE UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

Enzyme replacement therapy; Hematopoietic stem cell transplantation; Hurler syndrome; Umbilical cord blood transplantation; Unaffected child

Indexed keywords

EID: 84995917139     PISSN: 21928304     EISSN: 21928312     Source Type: Book Series    
DOI: 10.1007/8904_2014_395     Document Type: Chapter

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