MIR-16 rescues F508del-CFTR function in native cystic fibrosis epithelial cells

Gene Therapy

Volumn 22, Issue 11, 2015, Pages 908-916

  Kumar, P ^a   Bhattacharyya, S ^a   Peters, K W ^b   Glover, M L ^b   Sen, A ^c   Cox, R T ^c   Kundu, S ^a   Caohuy, H ^a   Frizzell, R A ^b   Pollard, H B ^a   Biswas, R ^a  

^a Uniformed Services University of the Health Sciences and the Walter Reed National Military Medical Center   (United States)

^b UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^c UNIFORMED SERVICES UNIVERSITY OF THE HEALTH SCIENCES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GLYCERALDEHYDE 3 PHOSPHATE DEHYDROGENASE; HEAT SHOCK PROTEIN 90; HISTONE DEACETYLASE 6; HISTONE DEACETYLASE 7; INTERLEUKIN 8; MESSENGER RNA; MICRORNA; MICRORNA 1; MICRORNA 16; MICRORNA 302A; UNCLASSIFIED DRUG; CFTR PROTEIN, HUMAN; MIRN16 MICRORNA, HUMAN;

ARTICLE; CELL MEMBRANE; CELLULAR DISTRIBUTION; CHLORIDE CONDUCTANCE; CHLORIDE TRANSPORT; CONTROLLED STUDY; CYSTIC FIBROSIS; CYTOPLASM; ENDOPLASMIC RETICULUM; GENE OVEREXPRESSION; HOMOZYGOTE; HUMAN; HUMAN CELL; HUMAN CELL CULTURE; LUNG ALVEOLUS EPITHELIUM CELL; LUNG FIBROSIS; MESSENGER RNA SYNTHESIS; PRIMARY CELL CULTURE; PRIORITY JOURNAL; PROMOTER REGION; PROTEIN LOCALIZATION; BIOSYNTHESIS; CELL CULTURE; CELL LINE; EPITHELIUM CELL; GENE THERAPY; GENETICS; METABOLISM; MUTATION; PATHOLOGY; PROCEDURES; RESPIRATORY TRACT MUCOSA;

CELL LINE; CELLS, CULTURED; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; EPITHELIAL CELLS; GENETIC THERAPY; HUMANS; MICRORNAS; MUTATION; RESPIRATORY MUCOSA; RNA, MESSENGER;

EID: 84947036329     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2015.56     Document Type: Article

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