-
1
-
-
17744367655
-
In utero gene therapy: Current challenges and perspectives
-
S. N. Waddington, M. G. Kramer, R. Hernandez-Alcoceba et al., "In utero gene therapy: current challenges and perspectives, " Molecular Therapy, vol. 11, no. 5, pp. 661-676, 2005.
-
(2005)
Molecular Therapy
, vol.11
, Issue.5
, pp. 661-676
-
-
Waddington, S.N.1
Kramer, M.G.2
Hernandez-Alcoceba, R.3
-
2
-
-
0035383766
-
Induction of stable prenatal tolerance to galactosidase by in utero gene transfer into preimmune sheep fetuses
-
N. D. Tran, C. D. Porada, G. Almeida-Porada, H. A. Glimp, W. French Anderson, and E. D. Zanjani, "Induction of stable prenatal tolerance to galactosidase by in utero gene transfer into preimmune sheep fetuses, " Blood, vol. 97, no. 11, pp. 3417-3423, 2001.
-
(2001)
Blood
, vol.97
, Issue.11
, pp. 3417-3423
-
-
Tran, N.D.1
Porada, C.D.2
Almeida-Porada, G.3
Glimp, H.A.4
French Anderson, W.5
Zanjani, E.D.6
-
3
-
-
0036682932
-
Complete allogeneic hematopoietic chimerism achieved by a combined strategy of in utero hematopoietic stem cell transplantation and postnatal donor lymphocyte infusion
-
S. Hayashi, W. H. Peranteau, A. F. Shaaban, and A. W. Flake, "Complete allogeneic hematopoietic chimerism achieved by a combined strategy of in utero hematopoietic stem cell transplantation and postnatal donor lymphocyte infusion, " Blood, vol. 100, no. 3, pp. 804-812, 2002.
-
(2002)
Blood
, vol.100
, Issue.3
, pp. 804-812
-
-
Hayashi, S.1
Peranteau, W.H.2
Shaaban, A.F.3
Flake, A.W.4
-
4
-
-
0346336779
-
Neonatal gene transfer with a retroviral vector results in tolerance to human factor IX in mice and dogs
-
J. Zhang, L. Xu, M. E. Haskins, and K. P. Ponder, "Neonatal gene transfer with a retroviral vector results in tolerance to human factor IX in mice and dogs, " Blood, vol. 103, no. 1, pp. 143-151, 2004.
-
(2004)
Blood
, vol.103
, Issue.1
, pp. 143-151
-
-
Zhang, J.1
Xu, L.2
Haskins, M.E.3
Ponder, K.P.4
-
5
-
-
5444227748
-
Permanent phenotypic correction of Hemophilia B in immunocom-petent mice by prenatal gene therapy
-
S. N. Waddington, M. S. Nivsarkar, A. R. Mistry et al., "Permanent phenotypic correction of Hemophilia B in immunocom-petent mice by prenatal gene therapy, " Blood, vol. 104, no. 9, pp. 2714-2721, 2004.
-
(2004)
Blood
, vol.104
, Issue.9
, pp. 2714-2721
-
-
Waddington, S.N.1
Nivsarkar, M.S.2
Mistry, A.R.3
-
6
-
-
0037441596
-
In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor
-
S. N. Waddington, S. M. K. Buckley, M. Nivsarkar et al., "In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor, " Blood, vol. 101, no. 4, pp. 1359-1366, 2003.
-
(2003)
Blood
, vol.101
, Issue.4
, pp. 1359-1366
-
-
Waddington, S.N.1
Buckley, S.M.K.2
Nivsarkar, M.3
-
7
-
-
0142179993
-
A murine locus on chromosome 18 controls NKT cell homeostasis and T cell diferentiation
-
F. Zhang, Z. Liang, N. Matsuki et al., "A murine locus on chromosome 18 controls NKT cell homeostasis and T cell diferentiation, " The Journal of Immunology, vol. 171, no. 9, pp. 4613-4620, 2003.
-
(2003)
The Journal of Immunology
, vol.171
, Issue.9
, pp. 4613-4620
-
-
Zhang, F.1
Liang, Z.2
Matsuki, N.3
-
8
-
-
38849134279
-
Adenovirus serotype 5 hexon mediates liver gene transfer
-
S. N. Waddington, J. H. McVey, D. Bhella et al., "Adenovirus serotype 5 hexon mediates liver gene transfer, " Cell, vol. 132, no. 3, pp. 397-409, 2008.
-
(2008)
Cell
, vol.132
, Issue.3
, pp. 397-409
-
-
Waddington, S.N.1
McVey, J.H.2
Bhella, D.3
-
9
-
-
80053923197
-
Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to diferential targeting of CNS cell types and extensive transduction of the nervous system
-
A. A. Rahim, A. M. S. Wong, K. Hoefer et al., "Intravenous administration of AAV2/9 to the fetal and neonatal mouse leads to diferential targeting of CNS cell types and extensive transduction of the nervous system, " FASEB Journal, vol. 25, no. 10, pp. 3505-3518, 2011.
-
(2011)
FASEB Journal
, vol.25
, Issue.10
, pp. 3505-3518
-
-
Rahim, A.A.1
Wong, A.M.S.2
Hoefer, K.3
-
10
-
-
54949092855
-
Luciferin detection afer intranasal vector delivery is improved by intranasal rather than intraperitoneal luciferin administration
-
S. M. K. Buckley, S. J. Howe, A. A. Rahim et al., "Luciferin detection afer intranasal vector delivery is improved by intranasal rather than intraperitoneal luciferin administration, " Human Gene Therapy, vol. 19, no. 10, pp. 1050-1056, 2008.
-
(2008)
Human Gene Therapy
, vol.19
, Issue.10
, pp. 1050-1056
-
-
Buckley, S.M.K.1
Howe, S.J.2
Rahim, A.A.3
-
11
-
-
34547498762
-
Induction and role of regulatory CD4+CD25+ T cells in tolerance to the transgene product following hepatic in vivo gene transfer
-
O. Cao, E. Dobrzynski, L. Wang et al., "Induction and role of regulatory CD4+CD25+ T cells in tolerance to the transgene product following hepatic in vivo gene transfer, " Blood, vol. 110, no. 4, pp. 1132-1140, 2007.
-
(2007)
Blood
, vol.110
, Issue.4
, pp. 1132-1140
-
-
Cao, O.1
Dobrzynski, E.2
Wang, L.3
-
12
-
-
34248566925
-
Immune response afer neonatal transfer of a human factor IX-expressing retroviral vector in dogs, cats, and mice
-
L. Xu, M. Mei, M. E. Haskins et al., "Immune response afer neonatal transfer of a human factor IX-expressing retroviral vector in dogs, cats, and mice, " Trombosis Research, vol. 120, no. 2, pp. 269-280, 2007.
-
(2007)
Trombosis Research
, vol.120
, Issue.2
, pp. 269-280
-
-
Xu, L.1
Mei, M.2
Haskins, M.E.3
-
13
-
-
84885599195
-
Role of antigen-specifc regulatory CD4+ CD25+ T cells in tolerance induction afer neonatal IP administration of AAV-hF.IX
-
Y. Shi, R. Falahati, J. Zhang, L. Flebbe-Rehwaldt, and K. M. L. Gaensler, "Role of antigen-specifc regulatory CD4+ CD25+ T cells in tolerance induction afer neonatal IP administration of AAV-hF.IX, " Gene Therapy, vol. 20, no. 10, pp. 987-996, 2013.
-
(2013)
Gene Therapy
, vol.20
, Issue.10
, pp. 987-996
-
-
Shi, Y.1
Falahati, R.2
Zhang, J.3
Flebbe-Rehwaldt, L.4
Gaensler, K.M.L.5
-
14
-
-
78751681902
-
Codon optimization of human factor VIII cDNAs leads to high-level expression
-
N. J. Ward, S. M. K. Buckley, S. N. Waddington et al., "Codon optimization of human factor VIII cDNAs leads to high-level expression, " Blood, vol. 117, no. 3, pp. 798-807, 2011.
-
(2011)
Blood
, vol.117
, Issue.3
, pp. 798-807
-
-
Ward, N.J.1
Buckley, S.M.K.2
Waddington, S.N.3
-
15
-
-
38649086367
-
Adenovirus-mediated gene delivery rescues a neonatal lethal murine model of mut methylmalonic acidemia
-
R. J. Chandler and C. P. Venditti, "Adenovirus-mediated gene delivery rescues a neonatal lethal murine model of mut methylmalonic acidemia, " Human Gene Therapy, vol. 19, no. 1, pp. 53-60, 2008.
-
(2008)
Human Gene Therapy
, vol.19
, Issue.1
, pp. 53-60
-
-
Chandler, R.J.1
Venditti, C.P.2
-
16
-
-
77749249680
-
Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN
-
K. D. Foust, X. Wang, V. L. McGovern et al., "Rescue of the spinal muscular atrophy phenotype in a mouse model by early postnatal delivery of SMN, " Nature Biotechnology, vol. 28, no. 3, pp. 271-274, 2010.
-
(2010)
Nature Biotechnology
, vol.28
, Issue.3
, pp. 271-274
-
-
Foust, K.D.1
Wang, X.2
McGovern, V.L.3
-
17
-
-
84902981635
-
Immunological ignorance allows long-term gene expression following perinatal rAAV-mediated gene transfer to murine airways
-
M. S. Carlon, D. Vidovíc, J. Dooley et al., "Immunological ignorance allows long-term gene expression following perinatal rAAV-mediated gene transfer to murine airways, " Human Gene Therapy, vol. 25, no. 6, pp. 517-528, 2014.
-
(2014)
Human Gene Therapy
, vol.25
, Issue.6
, pp. 517-528
-
-
Carlon, M.S.1
Vidovíc, D.2
Dooley, J.3
-
18
-
-
0033941252
-
Development of the murine and human immune system: Diferential Effects of immunotoxicants depend on time of exposure
-
S. D. Holladay and R. J. Smialowicz, "Development of the murine and human immune system: diferential Effects of immunotoxicants depend on time of exposure, " Environmental Health Perspectives, vol. 108, no. 3, pp. 463-473, 2000.
-
(2000)
Environmental Health Perspectives
, vol.108
, Issue.3
, pp. 463-473
-
-
Holladay, S.D.1
Smialowicz, R.J.2
-
19
-
-
84861127509
-
Immunological tolerance during fetal development: From mouse to man
-
J. E. Mold and J. M. McCune, "Immunological tolerance during fetal development: from mouse to man, " Advances in Immunology, vol. 115, pp. 73-111, 2012.
-
(2012)
Advances in Immunology
, vol.115
, pp. 73-111
-
-
Mold, J.E.1
McCune, J.M.2
-
20
-
-
78650352931
-
Fetal and adult hematopoietic stem cells give rise to distinct T cell lineages in humans
-
J. E. Mold, S. Venkatasubrahmanyam, T. D. Burt et al., "Fetal and adult hematopoietic stem cells give rise to distinct T cell lineages in humans, " Science, vol. 330, no. 6011, pp. 1695-1699, 2010.
-
(2010)
Science
, vol.330
, Issue.6011
, pp. 1695-1699
-
-
Mold, J.E.1
Venkatasubrahmanyam, S.2
Burt, T.D.3
-
21
-
-
21044455622
-
Adjuvants and antibody production: Dispelling the myths associated with Freund's complete and other adjuvants
-
H. F. Stills Jr., "Adjuvants and antibody production: dispelling the myths associated with Freund's complete and other adjuvants, " ILAR Journal, vol. 46, no. 3, pp. 280-293, 2005.
-
(2005)
ILAR Journal
, vol.46
, Issue.3
, pp. 280-293
-
-
Stills, H.F.1
-
22
-
-
0033870411
-
Haemoglobin interferes with the ex vivo luciferase luminescence assay: Consequence for detection of luciferase reporter gene expression in vivo
-
M. Colin, S. Moritz, H. Schneider, J. Capeau, C. Coutelle, and M. C. Brahimi-Horn, "Haemoglobin interferes with the ex vivo luciferase luminescence assay: consequence for detection of luciferase reporter gene expression in vivo, " Gene Therapy, vol. 7, no. 15, pp. 1333-1336, 2000.
-
(2000)
Gene Therapy
, vol.7
, Issue.15
, pp. 1333-1336
-
-
Colin, M.1
Moritz, S.2
Schneider, H.3
Capeau, J.4
Coutelle, C.5
Brahimi-Horn, M.C.6
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