Adenovirus-mediated gene delivery rescues a neonatal lethal murine model of mut0 methylmalonic acidemia

Human Gene Therapy

Volumn 19, Issue 1, 2008, Pages 53-60

  Chandler, Randy J ^a   Venditti, Charles P ^a  

^a NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

METHYLMALONIC ACID; METHYLMALONYL COENZYME A MUTASE;

ACIDEMIA; ADENOVIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; AUTOSOMAL DISORDER; CELL THERAPY; CITRIC ACID CYCLE; CONTROLLED STUDY; CYTOMEGALOVIRUS; GENE; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; LIVER; METABOLIC DISORDER; METHYLMALONIC ACIDEMIA; MOUSE; MUT GENE; MUTATION; NONHUMAN; VIRAL GENE DELIVERY SYSTEM; WESTERN BLOTTING;

ADENOVIRIDAE; ANIMALS; ANIMALS, NEWBORN; DISEASE MODELS, ANIMAL; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; METABOLISM, INBORN ERRORS; METHYLMALONIC ACID; METHYLMALONYL-COA MUTASE; MICE; MICE, TRANSGENIC; MUTATION; PHENOTYPE;

ADENOVIRIDAE; CYTOMEGALOVIRUS; MURINAE; MUS;

EID: 38649086367     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2007.0118     Document Type: Article

References (37)

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