Modeling the early phenotype at the neuromuscular junction of spinal muscular atrophy using patient-derived iPSCs

Stem Cell Reports

Volumn 4, Issue 4, 2015, Pages 561-568

  Yoshida, Michiko ^a,b   Kitaoka, Shiho ^d   Egawa, Naohiro ^a,c   Yamane, Mayu ^a   Ikeda, Ryunosuke ^a   Tsukita, Kayoko ^a   Amano, Naoki ^a   Watanabe, Akira ^a   Morimoto, Masafumi ^b   Takahashi, Jun ^a   Hosoi, Hajime ^b   Nakahata, Tatsutoshi ^a   Inoue, Haruhisa ^a,c   Saito, Megumu K ^a  

^a KYOTO UNIVERSITY   (Japan)

^b KYOTO PREFECTURAL UNIVERSITY OF MEDICINE   (Japan)

^c JAPAN SCIENCE AND TECHNOLOGY AGENCY   (Japan)

^d KOBE UNIVERSITY   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; CHOLINERGIC RECEPTOR; MORPHOLINO OLIGONUCLEOTIDE; VALPROIC ACID;

ARTICLE; CELL DIFFERENTIATION; CONTROLLED STUDY; GENE; GENETIC TRANSCRIPTION; HUMAN; HUMAN CELL; MOTONEURON; NEUROMUSCULAR SYNAPSE; PHENOTYPE; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; SPINAL MUSCULAR ATROPHY; SURVIVAL OF MOTOR NEURON 1 GENE; ANIMAL; CELL CULTURE TECHNIQUE; CELL LINE; COCULTURE; CYTOLOGY; DRUG EFFECTS; GENETICS; HEREDITARY SPINAL MUSCULAR ATROPHY; INDUCED PLURIPOTENT STEM CELL; METABOLISM; MOUSE; NEUROMUSCULAR JUNCTION; PATHOLOGY;

ANIMALS; CELL CULTURE TECHNIQUES; CELL DIFFERENTIATION; CELL LINE; COCULTURE TECHNIQUES; HUMANS; INDUCED PLURIPOTENT STEM CELLS; MICE; MORPHOLINOS; MOTOR NEURONS; MUSCULAR ATROPHY, SPINAL; NEUROMUSCULAR JUNCTION; PHENOTYPE; SPINAL MUSCULAR ATROPHIES OF CHILDHOOD; VALPROIC ACID;

EID: 84933677989     PISSN: 22136711     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.stemcr.2015.02.010     Document Type: Article

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