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Volumn 16, Issue 4, 2015, Pages 348-349
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Clinical translation of TALENS: Treating SCID-X1 by gene editing in iPSCs
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Author keywords
[No Author keywords available]
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Indexed keywords
TRANSCRIPTION ACTIVATOR LIKE EFFECTOR NUCLEASE;
VIRUS VECTOR;
ZINC FINGER NUCLEASE;
ADENOSINE DEAMINASE DEFICIENCY;
ADOPTIVE TRANSFER;
CARCINOGENESIS;
CELL DIFFERENTIATION;
CELL POPULATION;
DNA MODIFICATION;
EXON;
GENE EXPRESSION;
GENE MUTATION;
HOMOLOGOUS RECOMBINATION;
HUMAN;
NATURAL KILLER CELL;
NONHUMAN;
PLURIPOTENT STEM CELL;
PRE T LYMPHOCYTE;
PRIORITY JOURNAL;
RNA EDITING;
SHORT SURVEY;
STEM CELL GENE THERAPY;
TARGETED GENE REPAIR;
TRANSGENE;
X LINKED SEVERE COMBINED IMMUNODEFICIENCY;
ADOPTIVE IMMUNOTHERAPY;
GENE THERAPY;
PHYSIOLOGY;
PROCEDURES;
REGENERATION;
REGENERATIVE MEDICINE;
X-LINKED COMBINED IMMUNODEFICIENCY DISEASES;
GENETIC THERAPY;
HUMANS;
IMMUNOTHERAPY, ADOPTIVE;
INDUCED PLURIPOTENT STEM CELLS;
KILLER CELLS, NATURAL;
PRECURSOR CELLS, T-LYMPHOID;
REGENERATION;
REGENERATIVE MEDICINE;
X-LINKED COMBINED IMMUNODEFICIENCY DISEASES;
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EID: 84926137677
PISSN: 19345909
EISSN: 18759777
Source Type: Journal
DOI: 10.1016/j.stem.2015.03.009 Document Type: Short Survey |
Times cited : (9)
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References (9)
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