-
1
-
-
84870778464
-
Involvement of patient organisations in research and development of orphan drugs for rare diseases in Europe
-
COI: 1:STN:280:DC%2BC3s3ntFyntA%3D%3D, PID: 23293582
-
Mavris M, Le CY. Involvement of patient organisations in research and development of orphan drugs for rare diseases in Europe. Mol Syndromol. 2012;3(5):237–43.
-
(2012)
Mol Syndromol
, vol.3
, Issue.5
, pp. 237-243
-
-
Mavris, M.1
Le, C.Y.2
-
2
-
-
84875271754
-
Sustaining innovation and improvement in the treatment of childhood cancer: lessons from high-income countries
-
PID: 23434338
-
Pritchard-Jones K, Pieters R, Reaman GH, Hjorth L, Downie P, Calaminus G, et al. Sustaining innovation and improvement in the treatment of childhood cancer: lessons from high-income countries. Lancet Oncol. 2013;14(3):e95–103.
-
(2013)
Lancet Oncol
, vol.14
, Issue.3
, pp. e95-e103
-
-
Pritchard-Jones, K.1
Pieters, R.2
Reaman, G.H.3
Hjorth, L.4
Downie, P.5
Calaminus, G.6
-
3
-
-
84899968324
-
EUROPLAN: a project to support the development of national plans on rare diseases in Europe
-
COI: 1:STN:280:DC%2BC2cvivFertQ%3D%3D, PID: 24503588
-
Taruscio D, Gentile AE, De SM, Ferrelli RM, de la Posada PM, Hens M, et al. EUROPLAN: a project to support the development of national plans on rare diseases in Europe. Public Health Genomics. 2013;16(6):278–87.
-
(2013)
Public Health Genomics
, vol.16
, Issue.6
, pp. 278-287
-
-
Taruscio, D.1
Gentile, A.E.2
De, S.M.3
Ferrelli, R.M.4
de la Posada, P.M.5
Hens, M.6
-
4
-
-
84925482440
-
-
2014. Accessed 10 June 2014
-
Orphanet. About rare diseases. 2014. http://www.orpha.net/consor/cgi-bin/Education_AboutRareDiseases.php?lng=EN. Accessed 10 June 2014.
-
Orphanet. About rare diseases.
-
-
-
5
-
-
84899445465
-
A population-based registry as a source of health indicators for rare diseases: the ten-year experience of the Veneto Region’s rare diseases registry
-
PID: 24646171
-
Mazzucato M, Visona Dalla PL, Manea S, Minichiello C, Facchin P. A population-based registry as a source of health indicators for rare diseases: the ten-year experience of the Veneto Region’s rare diseases registry. Orphanet J Rare Dis. 2014;9:37.
-
(2014)
Orphanet J Rare Dis
, vol.9
, pp. 37
-
-
Mazzucato, M.1
Visona Dalla, P.L.2
Manea, S.3
Minichiello, C.4
Facchin, P.5
-
6
-
-
84873079257
-
Orphan drugs: the regulatory environment
-
PID: 22981668
-
Franco P. Orphan drugs: the regulatory environment. Drug Discov Today. 2013;18(3–4):163–72.
-
(2013)
Drug Discov Today
, vol.18
, Issue.3-4
, pp. 163-172
-
-
Franco, P.1
-
7
-
-
84925487573
-
-
Rare diseases: understanding this public health priority. 2005. Accessed 10 June 2014
-
European Organisation for Rare Diseases. Rare diseases: understanding this public health priority. 2005. http://www.eurordis.org/IMG/pdf/princeps_document-EN.pdf. Accessed 10 June 2014.
-
European Organisation for Rare Diseases.
-
-
-
8
-
-
84925492236
-
-
Orphan drugs in the United States of America. 2014. Accessed 13 June 2014
-
EURORDIS Rare Diseases Europe. Orphan drugs in the United States of America. 2014. http://www.orpha.net/consor/cgi-bin/Education_AboutOrphanDrugs.php?lng=EN&stapage=ST_EDUCATION_EDUCATION_ABOUTORPHANDRUGS_USA. Accessed 13 June 2014.
-
EURORDIS Rare Diseases Europe.
-
-
-
12
-
-
84925492236
-
-
National alliances for rare diseases. 2014. Accessed 13 June 2014
-
EURORDIS Rare Diseases Europe. National alliances for rare diseases. 2014. http://www.eurordis.org/content/national-alliances-rare-diseases. Accessed 13 June 2014.
-
EURORDIS Rare Diseases Europe.
-
-
-
15
-
-
84925516091
-
-
Rare diseases in Taiwan. 2014. Accessed 10 June 2014
-
Taiwan Foundation for Rare Disorders. Rare diseases in Taiwan. 2014. http://www.tfrd.org.tw/english/rare/cont.php?kind_id=16&top1=About%20rare%20diseases&top2=Rare%20Diseases%20in%20Taiwan. Accessed 10 June 2014.
-
Taiwan Foundation for Rare Disorders.
-
-
-
16
-
-
84925483798
-
-
, Taiwan Foundation for Rare Diseases. 2014
-
Rare Disease and Orphan Drug Act, Taiwan Foundation for Rare Diseases. 2014.
-
Rare Disease and Orphan Drug Act
-
-
-
17
-
-
84925479036
-
-
About the JPA. 2014. Accessed 10 June 2014
-
Japan Patients Association. About the JPA. 2014. http://www.nanbyo.jp. Accessed 10 June 2014.
-
Japan Patients Association.
-
-
-
18
-
-
84925479035
-
-
Accessed 22 Nov 2014
-
History Geiser Fundacion. http://www.fundaciongeiser.org/geiser/historia/?lang=en. Accessed 22 Nov 2014.
-
History Geiser Fundacion.
-
-
-
20
-
-
84908153966
-
A call for action to improve access to care and treatment for patients with rare diseases in the Asia-Pacific region
-
Soon S, Lopes G, Lim HW, Wong-Rieger D, et al. A call for action to improve access to care and treatment for patients with rare diseases in the Asia-Pacific region. Orphanet J Rare Dis. 2014; 9(1):137.
-
(2014)
Orphanet J Rare Dis
, vol.9
, Issue.1
, pp. 137
-
-
Soon, S.1
Lopes, G.2
Lim, H.W.3
Wong-Rieger, D.4
-
24
-
-
84925479031
-
-
Malaysian Rare Disorders Society. 2014. Accessed 22 Nov 2014
-
Malaysian Rare Disorders Society. Malaysian Rare Disorders Society. 2014. http://www.mrds.org.my. Accessed 22 Nov 2014.
-
Malaysian Rare Disorders Society.
-
-
-
25
-
-
84925479030
-
-
Who we are. 2012. Accessed 13 June 2014
-
Philippine Society for Orphan Disorders. Who we are. 2012. http://www.psod.org.ph/about-us/who-we-are/. Accessed 13 June 2014.
-
Philippine Society for Orphan Disorders.
-
-
-
26
-
-
84925486167
-
-
New Zealand Organisation for Rare Disorders (NZORD). 2013. Accessed 10 June 2014
-
New Zealand Organisation for Rare Disorders. New Zealand Organisation for Rare Disorders (NZORD). 2013. http://www.nzord.org.nz/. Accessed 10 June 2014.
-
New Zealand Organisation for Rare Disorders.
-
-
|