메뉴 건너뛰기




Volumn 100, Issue 1, 2015, Pages 17-22

Criteria for evaluating response and outcome in clinical trials for children with juvenile myelomonocytic leukemia

(27)  Niemeyer, Charlotte M a   Loh, Mignon L b   Cseh, Annamaria a   Cooper, Todd c   Dvorak, Christopher C d   Chan, Rebecca e   Xicoy, Blanca f   Germing, Ulrich g   Kojima, Seiji h   Manabe, Atsushi i   Dworzak, Michael j   De Moerloose, Barbara k   Starý, Jan l   Smith, Owen P m   Masetti, Riccardo n   Catala, Albert o   Bergstraesser, Eva p   Ussowicz, Marek q   Fabri, Oskana r   Baruchel, André s   more..


Author keywords

[No Author keywords available]

Indexed keywords

K RAS PROTEIN; PROTEIN TYROSINE PHOSPHATASE SHP 2;

EID: 84920147335     PISSN: 03906078     EISSN: 15928721     Source Type: Journal    
DOI: 10.3324/haematol.2014.109892     Document Type: Article
Times cited : (39)

References (33)
  • 1
    • 39749133834 scopus 로고    scopus 로고
    • Paediatric myelodysplastic syndromes and juvenile myelomonocytic leukaemia: Molecular classification and treatment options
    • Niemeyer CM, Kratz CP. Paediatric myelodysplastic syndromes and juvenile myelomonocytic leukaemia: molecular classification and treatment options. Br J Haematol. 2008;140 (6):610-24.
    • (2008) Br J Haematol , vol.140 , Issue.6 , pp. 610-624
    • Niemeyer, C.M.1    Kratz, C.P.2
  • 2
    • 79951979515 scopus 로고    scopus 로고
    • Recent advances in the pathogenesis and treatment of juvenile myelomonocytic leukaemia
    • Loh ML. Recent advances in the pathogenesis and treatment of juvenile myelomonocytic leukaemia. Br J Haematol. 2011; 152(6):677-87.
    • (2011) Br J Haematol , vol.152 , Issue.6 , pp. 677-687
    • Loh, M.L.1
  • 3
    • 0028069002 scopus 로고
    • The chronic myeloid leukaemias: Guidelines for distinguishing chronic granulocytic, atypical chronic myeloid, and chronic myelomonocytic leukaemia. Proposals by the French-American- British Cooperative Leukaemia Group
    • Bennett JM, Catovsky D, Daniel MT, Flandrin G, Galton DA, Gralnick H, et al. The chronic myeloid leukaemias: guidelines for distinguishing chronic granulocytic, atypical chronic myeloid, and chronic myelomonocytic leukaemia. Proposals by the French-American- British Cooperative Leukaemia Group. Br J Haematol. 1994; 87(4):746-54.
    • (1994) Br J Haematol , vol.87 , Issue.4 , pp. 746-754
    • Bennett, J.M.1    Catovsky, D.2    Daniel, M.T.3    Flandrin, G.4    Galton, D.A.5    Gralnick, H.6
  • 4
    • 0030977399 scopus 로고    scopus 로고
    • Chronic myelomonocytic leukemia in childhood: A retrospective analysis of 110 cases. European Working Group on Myelodysplastic Syndromes in Childhood (EWOG-MDS)
    • Niemeyer CM, Arico M, Basso G, Biondi A, Cantu RA, Creutzig U, et al. Chronic myelomonocytic leukemia in childhood: a retrospective analysis of 110 cases. European Working Group on Myelodysplastic Syndromes in Childhood (EWOG-MDS). Blood. 1997;89(10):3534-43.
    • (1997) Blood , vol.89 , Issue.10 , pp. 3534-3543
    • Niemeyer, C.M.1    Arico, M.2    Basso, G.3    Biondi, A.4    Cantu, R.A.5    Creutzig, U.6
  • 5
    • 0038278866 scopus 로고    scopus 로고
    • Somatic PTPN11 mutations in juvenile myelomonocytic leukemia, myelodysplastic syndromes and acute myeloid leukemia
    • Tartaglia M, Niemeyer CM, Fragale A, Song X, Buechner J, Jung A, et al. Somatic PTPN11 mutations in juvenile myelomonocytic leukemia, myelodysplastic syndromes and acute myeloid leukemia. Nat Genet. 2003; 34(2):148-50.
    • (2003) Nat Genet , vol.34 , Issue.2 , pp. 148-150
    • Tartaglia, M.1    Niemeyer, C.M.2    Fragale, A.3    Song, X.4    Buechner, J.5    Jung, A.6
  • 6
    • 24744455046 scopus 로고    scopus 로고
    • The mutational spectrum of PTPN11 in juvenile myelomonocytic leukemia and Noonan syndrome/myeloproliferative disease
    • Kratz CP, Niemeyer CM, Castleberry RP, Cetin M, Bergsträsser E, Emanuel PD, et al. The mutational spectrum of PTPN11 in juvenile myelomonocytic leukemia and Noonan syndrome/myeloproliferative disease. Blood. 2005;106(6):2183-5.
    • (2005) Blood , vol.106 , Issue.6 , pp. 2183-2185
    • Kratz, C.P.1    Niemeyer, C.M.2    Castleberry, R.P.3    Cetin, M.4    Bergsträsser, E.5    Emanuel, P.D.6
  • 7
    • 0028344097 scopus 로고
    • Mutations of the N-ras gene in juvenile chronic myelogenous leukemia
    • Miyauchi J, Asada M, Sasaki M, Tsunematsu Y, Kojima S, Mizutani S. Mutations of the N-ras gene in juvenile chronic myelogenous leukemia. Blood. 1994;83(8):2248-54.
    • (1994) Blood , vol.83 , Issue.8 , pp. 2248-2254
    • Miyauchi, J.1    Asada, M.2    Sasaki, M.3    Tsunematsu, Y.4    Kojima, S.5    Mizutani, S.6
  • 8
    • 0032125716 scopus 로고    scopus 로고
    • Mutations of the NF1 gene in children with juvenile myelomonocytic leukemia without clinical evidence of neurofibromatosis, type1
    • Side LE, Emanuel PD, Taylor B, Franklin J, Thompson P, Castleberry RP, et al. Mutations of the NF1 gene in children with juvenile myelomonocytic leukemia without clinical evidence of neurofibromatosis, type1. Blood. 1998;92(1):267-72.
    • (1998) Blood , vol.92 , Issue.1 , pp. 267-272
    • Side, L.E.1    Emanuel, P.D.2    Taylor, B.3    Franklin, J.4    Thompson, P.5    Castleberry, R.P.6
  • 9
    • 0032896457 scopus 로고    scopus 로고
    • Ras mutations and clonality analysis in children with juvenile myelomonocytic leukemia (JMML)
    • Flotho C, Valcamonica S, Mach-Pascual S, Schmahl G, Corral L, Ritterbach J, et al. Ras mutations and clonality analysis in children with juvenile myelomonocytic leukemia (JMML). Leukemia. 1999;13(1):32-7.
    • (1999) Leukemia , vol.13 , Issue.1 , pp. 32-37
    • Flotho, C.1    Valcamonica, S.2    Mach-Pascual, S.3    Schmahl, G.4    Corral, L.5    Ritterbach, J.6
  • 10
    • 70349249988 scopus 로고    scopus 로고
    • Mutations in CBL occur frequently in juvenile myelomonocytic leukemia
    • Loh ML, Sakai DS, Flotho C, Kang M, Fliegauf M, Archambeault S, et al. Mutations in CBL occur frequently in juvenile myelomonocytic leukemia. Blood. 2009; 114(9):1859-63.
    • (2009) Blood , vol.114 , Issue.9 , pp. 1859-1863
    • Loh, M.L.1    Sakai, D.S.2    Flotho, C.3    Kang, M.4    Fliegauf, M.5    Archambeault, S.6
  • 11
    • 84984935016 scopus 로고    scopus 로고
    • Germline CBL mutations cause developmental abnormalities and predispose to juvenile myelomonocytic leukemia
    • Niemeyer CM, Kang MW, Shin DH, Furlan I, Erlacher M, Bunin NJ, et al. Germline CBL mutations cause developmental abnormalities and predispose to juvenile myelomonocytic leukemia. Nat Genet. 2010;42(9):794-800.
    • (2010) Nat Genet , vol.42 , Issue.9 , pp. 794-800
    • Niemeyer, C.M.1    Kang, M.W.2    Shin, D.H.3    Furlan, I.4    Erlacher, M.5    Bunin, N.J.6
  • 13
    • 19944428598 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation (HSCT) in children with juvenile myelomonocytic leukemia (JMML): Results of the EWOG-MDS/EBMT trial
    • Locatelli F, Nöllke P, Zecca M, Korthof E, Lanino E, Peters C, et al. Hematopoietic stem cell transplantation (HSCT) in children with juvenile myelomonocytic leukemia (JMML): results of the EWOG-MDS/EBMT trial. Blood. 2005;105(1):410-9.
    • (2005) Blood , vol.105 , Issue.1 , pp. 410-419
    • Locatelli, F.1    Nöllke, P.2    Zecca, M.3    Korthof, E.4    Lanino, E.5    Peters, C.6
  • 14
    • 54849415692 scopus 로고    scopus 로고
    • A conditioning regimen of busulfan, fludarabine, and melphalan for allogeneic stem cell transplantation in children with juvenile myelomonocytic leukemia
    • Yabe M, Sako M, Yabe H, Osugi Y, Kurosawa H, Nara T, et al. A conditioning regimen of busulfan, fludarabine, and melphalan for allogeneic stem cell transplantation in children with juvenile myelomonocytic leukemia. Pediatr Transplant. 2008; 12(8):862-7.
    • (2008) Pediatr Transplant , vol.12 , Issue.8 , pp. 862-867
    • Yabe, M.1    Sako, M.2    Yabe, H.3    Osugi, Y.4    Kurosawa, H.5    Nara, T.6
  • 15
    • 84887600939 scopus 로고    scopus 로고
    • Analysis of risk factors influencing outcomes after cord blood transplantation in children with juvenile myelomonocytic leukemia: A EUROCORD, EBMT, EWOG-MDS, CIBMTR study
    • Locatelli F, Crotta A, Ruggeri A, Eapen M, Wagner JE, Macmillan ML, et al. Analysis of risk factors influencing outcomes after cord blood transplantation in children with juvenile myelomonocytic leukemia: a EUROCORD, EBMT, EWOG-MDS, CIBMTR study. Blood. 2013;122(12):2135-41.
    • (2013) Blood , vol.122 , Issue.12 , pp. 2135-2141
    • Locatelli, F.1    Crotta, A.2    Ruggeri, A.3    Eapen, M.4    Wagner, J.E.5    Macmillan, M.L.6
  • 16
    • 0028138595 scopus 로고
    • A pilot study of isotretinoin in the treatment of juvenile chronic myelogenous leukemia
    • Castleberry RP, Emanuel PD, Zuckerman KS, Cohn S, Strauss L, Byrd RL, et al. A pilot study of isotretinoin in the treatment of juvenile chronic myelogenous leukemia. N Engl J Med. 1994;331(25):1680-4.
    • (1994) N Engl J Med , vol.331 , Issue.25 , pp. 1680-1684
    • Castleberry, R.P.1    Emanuel, P.D.2    Zuckerman, K.S.3    Cohn, S.4    Strauss, L.5    Byrd, R.L.6
  • 18
    • 23844478260 scopus 로고    scopus 로고
    • Little response to zoledronic acid in a child of juvenile myelomonocytic leukemia (JMML) harboring the PTPN11 mutation
    • Shimada H, Shima H, Shimasaki N, Yoshihara H, Mori T, Takahashi T. Little response to zoledronic acid in a child of juvenile myelomonocytic leukemia (JMML) harboring the PTPN11 mutation. Ann Oncol. 2005;16(8):1400.
    • (2005) Ann Oncol , vol.16 , Issue.8 , pp. 1400
    • Shimada, H.1    Shima, H.2    Shimasaki, N.3    Yoshihara, H.4    Mori, T.5    Takahashi, T.6
  • 19
    • 63849095591 scopus 로고    scopus 로고
    • Intriguing response to azacitidine in a patient with juvenile myelomonocytic leukemia and monosomy 7
    • Furlan I, Batz C, Flotho C, Mohr B, Lübbert M, Suttorp M, et al. Intriguing response to azacitidine in a patient with juvenile myelomonocytic leukemia and monosomy 7. Blood. 2009;113(12):2867-8.
    • (2009) Blood , vol.113 , Issue.12 , pp. 2867-2868
    • Furlan, I.1    Batz, C.2    Flotho, C.3    Mohr, B.4    Lübbert, M.5    Suttorp, M.6
  • 22
    • 84873844410 scopus 로고    scopus 로고
    • Sustained MEK inhibition abrogates myeloproliferative disease in Nf1 mutant mice
    • Chang T, Krisman K, Theobald EH; Xu J, Akutagawa J, Lauchle JO, et al. Sustained MEK inhibition abrogates myeloproliferative disease in Nf1 mutant mice. J Clin Invest. 2013;123(1):335-9.
    • (2013) J Clin Invest , vol.123 , Issue.1 , pp. 335-339
    • Chang, T.1    Krisman, K.2    Theobald, E.H.3    Xu, J.4    Akutagawa, J.5    Lauchle, J.O.6
  • 23
    • 84900426322 scopus 로고    scopus 로고
    • PI3K p110delta uniquely promotes gain-of-function Shp2-induced GMCSF hypersensitivity in a model of JMML
    • Goodwin CB, Li XJ, Mali RS, Chan G, Kang M, Liu Z et al. PI3K p110delta uniquely promotes gain-of-function Shp2-induced GMCSF hypersensitivity in a model of JMML. Blood. 2014;23(18):2838-42.
    • (2014) Blood , vol.23 , Issue.18 , pp. 2838-2842
    • Goodwin, C.B.1    Li, X.J.2    Mali, R.S.3    Chan, G.4    Kang, M.5    Liu, Z.6
  • 24
    • 0034554786 scopus 로고    scopus 로고
    • Report of an international working group to standardize response criteria for myelodysplastic syndromes
    • Cheson BD, Bennett JM, Kantarjian H, Pinto A, Schiffer CA, Nimer SD, et al. Report of an international working group to standardize response criteria for myelodysplastic syndromes. Blood. 2000;96(12):3671-4.
    • (2000) Blood , vol.96 , Issue.12 , pp. 3671-3674
    • Cheson, B.D.1    Bennett, J.M.2    Kantarjian, H.3    Pinto, A.4    Schiffer, C.A.5    Nimer, S.D.6
  • 25
    • 33745968917 scopus 로고    scopus 로고
    • Clinical application and proposal for modification of the International Working Group (IWG) response criteria in myelodysplasia
    • Cheson BD, Greenberg PL, Bennett JM, Lowenberg B, Wijermans PW, Nimer SD, et al. Clinical application and proposal for modification of the International Working Group (IWG) response criteria in myelodysplasia. Blood. 2006;108(2):419-25.
    • (2006) Blood , vol.108 , Issue.2 , pp. 419-425
    • Cheson, B.D.1    Greenberg, P.L.2    Bennett, J.M.3    Lowenberg, B.4    Wijermans, P.W.5    Nimer, S.D.6
  • 26
    • 35148867031 scopus 로고    scopus 로고
    • Nonhematopoietic stem cell transplantation treatment of juvenile myelomonocytic leukemia: A retrospective analysis and definition of response criteria
    • Bergstraesser E, Hasle H, Rogge T, Fischer A, Zimmermann M, Noellke P, et al. Nonhematopoietic stem cell transplantation treatment of juvenile myelomonocytic leukemia: a retrospective analysis and definition of response criteria. Pediatr Blood Cancer. 2007;49(5):629-33.
    • (2007) Pediatr Blood Cancer , vol.49 , Issue.5 , pp. 629-633
    • Bergstraesser, E.1    Hasle, H.2    Rogge, T.3    Fischer, A.4    Zimmermann, M.5    Noellke, P.6
  • 27
    • 58549090093 scopus 로고    scopus 로고
    • Juvenile myelomonocytic leukemia: A report from the 2nd International JMML Symposium
    • Chan RJ, Cooper T, Kratz CP, Weiss B, Loh ML. Juvenile myelomonocytic leukemia: a report from the 2nd International JMML Symposium. Leuk Res. 2009;33(3):355-62.
    • (2009) Leuk Res , vol.33 , Issue.3 , pp. 355-362
    • Chan, R.J.1    Cooper, T.2    Kratz, C.P.3    Weiss, B.4    Loh, M.L.5
  • 28
    • 84877084272 scopus 로고    scopus 로고
    • Predictive factors of response and survival among chronic myelomonocytic leukemia patients treated with azacitidine
    • Ades L, Sekeres MA, Wolfromm A, Teichman ML, Tiu RV, Itzykson R, et al. Predictive factors of response and survival among chronic myelomonocytic leukemia patients treated with azacitidine. Leuk Res. 2013;37(6):609-13.
    • (2013) Leuk Res , vol.37 , Issue.6 , pp. 609-613
    • Ades, L.1    Sekeres, M.A.2    Wolfromm, A.3    Teichman, M.L.4    Tiu, R.V.5    Itzykson, R.6
  • 29
    • 33846939564 scopus 로고    scopus 로고
    • Activity of decitabine, a hypomethylating agent, in chronic myelomonocytic leukemia
    • Aribi A, Borthakur G, Ravandi F, Shan J, Davisson J, Cortes J, et al. Activity of decitabine, a hypomethylating agent, in chronic myelomonocytic leukemia. Cancer. 2007;109(4):713-7.
    • (2007) Cancer , vol.109 , Issue.4 , pp. 713-717
    • Aribi, A.1    Borthakur, G.2    Ravandi, F.3    Shan, J.4    Davisson, J.5    Cortes, J.6
  • 30
    • 10144240361 scopus 로고    scopus 로고
    • A randomized trial of hydroxyurea versus VP16 in adult chronic myelomonocytic leukemia. Groupe Francais des Myelodysplasies and European CMML Group
    • Wattel E, Guerci A, Hecquet B, Economopoulos T, Copplestone A, Mahé B, et al. A randomized trial of hydroxyurea versus VP16 in adult chronic myelomonocytic leukemia. Groupe Francais des Myelodysplasies and European CMML Group. Blood. 1996;88(7):2480-7.
    • (1996) Blood , vol.88 , Issue.7 , pp. 2480-2487
    • Wattel, E.1    Guerci, A.2    Hecquet, B.3    Economopoulos, T.4    Copplestone, A.5    Mahé, B.6
  • 31
    • 0036319096 scopus 로고    scopus 로고
    • Spleen size: How well do linear ultrasound measurements correlate with three-dimensional CT volume assessments?
    • Lamb PM, Lund A, Kanagasabay RR, Martin A, Webb JA, Reznek RH, et al. Spleen size: how well do linear ultrasound measurements correlate with three-dimensional CT volume assessments? Br J Radiol. 2002; 75(895):573-7.
    • (2002) Br J Radiol , vol.75 , Issue.895 , pp. 573-577
    • Lamb, P.M.1    Lund, A.2    Kanagasabay, R.R.3    Martin, A.4    Webb, J.A.5    Reznek, R.H.6
  • 32
    • 84881020319 scopus 로고    scopus 로고
    • Exome sequencing identifies secondary mutations of SETBP1 and JAK3 in juvenile myelomonocytic leukemia
    • Sakaguchi H, Okuno Y, Muramatsu, Yoshida K, Shiraishi Y, Takahashi M, et al. Exome sequencing identifies secondary mutations of SETBP1 and JAK3 in juvenile myelomonocytic leukemia. Nat Genet. 2013;45(8):937-41.
    • (2013) Nat Genet , vol.45 , Issue.8 , pp. 937-941
    • Sakaguchi, H.1    Okuno, Y.2    Muramatsu, Y.K.3    Shiraishi, Y.4    Takahashi, M.5
  • 33
    • 20044376886 scopus 로고    scopus 로고
    • Chimaerism analyses and subsequent immunological intervention after stem cell transplantation in patients with juvenile myelomonocytic leukaemia
    • Yoshimi A, Niemeyer CM, Bohmer V, Duffner U, Strahm B, Kreyenberg H, et al. Chimaerism analyses and subsequent immunological intervention after stem cell transplantation in patients with juvenile myelomonocytic leukaemia. Br J Haematol. 2005;129(4):542-9.
    • (2005) Br J Haematol , vol.129 , Issue.4 , pp. 542-549
    • Yoshimi, A.1    Niemeyer, C.M.2    Bohmer, V.3    Duffner, U.4    Strahm, B.5    Kreyenberg, H.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.