Response to androgen therapy in patients with dyskeratosis congenita

British Journal of Haematology

Volumn 165, Issue 3, 2014, Pages 349-357

  Khincha, Payal P ^a,b   Wentzensen, Ingrid M ^a,c   Giri, Neelam ^a   Alter, Blanche P ^a   Savage, Sharon A ^a  

^a NATIONAL CANCER INSTITUTE   (United States)

^b CHILDREN'S NATIONAL MEDICAL CENTER   (United States)

^c JOHNS HOPKINS HOSPITAL   (United States)

Author keywords

Androgen; Dyskeratosis congenita; Telomere

Indexed keywords

ANDROGEN; LIVER ENZYME; THYROGLOBULIN;

ACNE; ADOLESCENT; ADULT; AGED; ANDROGEN THERAPY; ARTICLE; BEHAVIOR DISORDER; BONE MARROW DEPRESSION; BONE MARROW DISEASE; CANCER SUSCEPTIBILITY; CHILD; CLINICAL ARTICLE; COHORT ANALYSIS; CONTROLLED STUDY; DISORDERS OF LIPID METABOLISM; DYSKERATOSIS CONGENITA; ENDOCRINE FUNCTION; ERYTHROCYTE TRANSFUSION; FANCONI ANEMIA; FEMALE; GENE MUTATION; GONADAL DISEASE; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HYPERBILIRUBINEMIA; HYPERTRANSAMINASEMIA; LIVER ADENOMA; LIVER CELL CARCINOMA; LIVER FUNCTION; LIVER TOXICITY; MALE; MYELODYSPLASTIC SYNDROME; OBSERVATIONAL STUDY; PREPUBERTY; PRIAPISM; PRIORITY JOURNAL; PROSPECTIVE STUDY; PURPURA; RETROSPECTIVE STUDY; TELOMERE; THROMBOCYTE TRANSFUSION; TREATMENT RESPONSE;

ANDROGEN; DYSKERATOSIS CONGENITA; TELOMERE;

ADOLESCENT; ADULT; AGED; ANDROGENS; CHILD; CHILD, PRESCHOOL; COHORT STUDIES; DYSKERATOSIS CONGENITA; FEMALE; HUMANS; INFANT; MALE; MIDDLE AGED; PROSPECTIVE STUDIES; RETROSPECTIVE STUDIES; TELOMERE; YOUNG ADULT;

EID: 84898458091     PISSN: 00071048     EISSN: 13652141     Source Type: Journal    
DOI: 10.1111/bjh.12748     Document Type: Article

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