SMN-targeted therapeutics for spinal muscular atrophy: Are we SMArt enough yet?

Journal of Clinical Investigation

Volumn 124, Issue 2, 2014, Pages 487-490

  Swoboda, Kathryn J ^a  

^a UNIVERSITY OF UTAH SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANIMALS; FEMALE; MALE; NEUROMUSCULAR JUNCTION; SURVIVAL OF MOTOR NEURON 1 PROTEIN;

EID: 84893877851     PISSN: 00219738     EISSN: 15588238     Source Type: Journal    
DOI: 10.1172/JCI74142     Document Type: Review

References (22)

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