Stbd1 is highly elevated in skeletal muscle of Pompe disease mice but suppression of its expression does not affect lysosomal glycogen accumulation

Molecular Genetics and Metabolism

Volumn 109, Issue 3, 2013, Pages 312-314

  Yi, Haiqing ^a   Fredrickson, Keri B ^a   Das, Stuti ^a   Kishnani, Priya S ^a   Sun, Baodong ^a  

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

Author keywords

AAV; Lysosomal glycogen; Pompe; shRNA; Stbd1

Indexed keywords

GLYCOGEN; PARVOVIRUS VECTOR; PROTEIN; SHORT HAIRPIN RNA; STARCH BINDING DOMAIN CONTAINING PROTEIN 1; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BIOACCUMULATION; CARBOHYDRATE TRANSPORT; CONTROLLED STUDY; GASTROCNEMIUS MUSCLE; GENE SILENCING; GLYCOGEN STORAGE DISEASE TYPE 2; LYSOSOME; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; QUADRICEPS FEMORIS MUSCLE; SKELETAL MUSCLE; WILD TYPE;

MUS;

EID: 84891372222     PISSN: 10967192     EISSN: 10967206     Source Type: Journal    
DOI: 10.1016/j.ymgme.2013.05.004     Document Type: Article

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