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Volumn 32, Issue SUPPL. 1, 2009, Pages

Continuous infusion of enzyme replacement therapy is inferior to weekly infusions in MPS I dogs

Author keywords

[No Author keywords available]

Indexed keywords

GLYCOSAMINOGLYCAN; LEVO IDURONIDASE; RECOMBINANT PROTEIN;

EID: 84881013011     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-009-1198-5     Document Type: Article
Times cited : (4)

References (12)
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  • 2
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    • Immune tolerance improves the efficacy of enzyme replacement therapy in the canine model of mucopolysaccharidosis I
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  • 4
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    • A dose-optimization trial of laronidase (Aldurazyme) in patients with mucopolysaccharidosis I
    • doi:10.1016/j.ymgme.2008.10.009
    • Giugliani R, Rojas VM, Martins AM, et al (2009) A dose-optimization trial of laronidase (Aldurazyme) in patients with mucopolysaccharidosis I. Mol Genet Metab 96: 13-19. doi:10.1016/j.ymgme.2008.10.009
    • (2009) Mol Genet Metab , vol.96 , pp. 13-19
    • Giugliani, R.1    Rojas, V.M.2    Martins, A.M.3
  • 5
    • 16844379992 scopus 로고    scopus 로고
    • Pharmacokinetic profile of recombinant human N-acetylgalactosamine 4-sulphatase enzyme replacement therapy in patients with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome): A phase I/II study
    • doi:10.1080/08035320510028139
    • Harmatz P, Kramer WG, Hopwood JJ, et al (2005) Pharmacokinetic profile of recombinant human N-acetylgalactosamine 4-sulphatase enzyme replacement therapy in patients with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome): a phase I/II study. Acta Paediatr Suppl 94: 61-68. doi:10.1080/08035320510028139
    • (2005) Acta Paediatr Suppl , vol.94 , pp. 61-68
    • Harmatz, P.1    Kramer, W.G.2    Hopwood, J.J.3
  • 6
    • 38049185089 scopus 로고    scopus 로고
    • Comparison of continuous subcutaneous insulin infusion (CSII) and multiple daily infusions (MDI) in paediatric Type 1 diabetes: A multicentre matched-pair cohort analysis over 3 years
    • Jakisch BI, Wagner VM, Heidtmann B, et al (2008) Comparison of continuous subcutaneous insulin infusion (CSII) and multiple daily infusions (MDI) in paediatric Type 1 diabetes: a multicentre matched-pair cohort analysis over 3 years. Diabet Med 25: 80-85.
    • (2008) Diabet Med , vol.25 , pp. 80-85
    • Jakisch, B.I.1    Wagner, V.M.2    Heidtmann, B.3
  • 7
    • 0028449393 scopus 로고
    • Overexpression of the human lysosomal enzyme alpha-L-iduronidase in Chinese hamster ovary cells
    • DOI 10.1006/prep.1994.1035
    • Kakkis ED, Matynia A, Jonas AJ, et al (1994) Overexpression of the human lysosomal enzyme a-L-iduronidase in Chinese hamster ovary cells. Protein Expr Purif 5 : 225-232. doi:10.1006/prep.1994.1035 (Pubitemid 2097008)
    • (1994) Protein Expression and Purification , vol.5 , Issue.3 , pp. 225-232
    • Kakkis, E.D.1    Matynia, A.2    Jonas, A.J.3    Neufeld, E.F.4
  • 9
    • 0035905889 scopus 로고    scopus 로고
    • Enzymer-eplacement therapy in mucopolysaccharisosis I
    • doi:10.1056/NEJM200101183440304
    • Kakkis ED, Muenzer J, Tiller GE, et al (2001) Enzymer-eplacement therapy in mucopolysaccharisosis I. N Engl J Med 344: 182-188. doi:10.1056/ NEJM200101183440304
    • (2001) N Engl J Med , vol.344 , pp. 182-188
    • Kakkis, E.D.1    Muenzer, J.2    Tiller, G.E.3
  • 11
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    • A phase II/III clinical study of enzyme replacement therapy with idursulfase in mucopolysaccharidosis II (Hunter syndrome)
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  • 12
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    • Wraith JE, Beck M, Lane R, et al (2007) Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human a-Liduronidase (laronidase). Pediatrics 120: e37-e46. doi:10.1542/peds.2006-2156 (Pubitemid 47036214)
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* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.