Mucopolysaccharidosis: Cardiologic features and effects of enzyme-replacement therapy in 24 children with MPS I, II and VI

Journal of Inherited Metabolic Disease

Volumn 36, Issue 2, 2013, Pages 227-234

  Brands, Marion M M G ^a   Frohn Mulder, Ingrid M ^a   Hagemans, Marloes L C ^a   Hop, Wim C J ^b   Oussoren, Esmee ^a   Helbing, Wim A ^a   Van Der Ploeg, Ans T ^a  

^a SOPHIA CHILDREN S HOSPITAL   (Netherlands)

^b ERASMUS MEDICAL CENTER   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

GALSULFASE; IDURONATE 2 SULFATASE; LARONIDASE;

ADOLESCENT; ADULT; AFRICAN; ARAB; ARTICLE; ASIAN; CAUCASIAN; CHILD; CLINICAL ARTICLE; CONTROLLED STUDY; DIASTOLE; DISEASE SEVERITY; ELECTROCARDIOGRAM; ENZYME REPLACEMENT; ETHNICITY; FEMALE; HEART BUNDLE BRANCH BLOCK; HEART DISEASE; HEART LEFT VENTRICLE HYPERTROPHY; HEART LEFT VENTRICLE MASS; HEART LEFT VENTRICLE VOLUME; HEART RIGHT VENTRICLE HYPERTROPHY; HEART VENTRICLE HYPERTROPHY; HUMAN; HUNTER SYNDROME; HURLER SYNDROME; INFANT; MALE; MAROTEAUX LAMY SYNDROME; MITRAL VALVE REGURGITATION; PR INTERVAL; PRESCHOOL CHILD; QRS COMPLEX; QT PROLONGATION; SCHOOL CHILD; SYSTOLE; TURKISH; VALVULOPLASTY; CARDIOLOGY; ECHOCARDIOGRAPHY; ELECTROCARDIOGRAPHY; MUCOPOLYSACCHARIDOSES; PATHOPHYSIOLOGY; PROCEDURES; PROSPECTIVE STUDY;

ADOLESCENT; CARDIOLOGY; CHILD; CHILD, PRESCHOOL; ECHOCARDIOGRAPHY; ELECTROCARDIOGRAPHY; ENZYME REPLACEMENT THERAPY; FEMALE; HEART DISEASES; HUMANS; INFANT; MALE; MUCOPOLYSACCHARIDOSES; PROSPECTIVE STUDIES;

EID: 84876092434     PISSN: 01418955     EISSN: 15732665     Source Type: Journal    
DOI: 10.1007/s10545-011-9444-z     Document Type: Article

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