The natural course and the impact of therapies of cardiac involvement in the mucopolysaccharidoses

Cardiology in the Young

Volumn 19, Issue 2, 2009, Pages 170-178

  Fesslová, Vlasta ^a   Corti, Paola ^b   Sersale, Giovanna ^b   Rovelli, Attilio ^b   Russo, Pierluigi ^c   Mannarino, Savina ^d   Butera, Gianfranco ^a   Parini, Rossella ^b  

^a IRCCS POLICLINICO SAN DONATO   (Italy)

^b UNIVERSITY OF MILANO BICOCCA   (Italy)

^c SAN GERARDO HOSPITAL   (Italy)

^d FONDAZIONE IRCCS POLICLINICO SAN MATTEO   (Italy)

Author keywords

Cardiac anomalies; Echocardiography; Enzyme replacement therapy; Haematopoietic stem cell transplantation; Lysosomal storage disorders

Indexed keywords

ADOLESCENT; AGE DISTRIBUTION; AORTA VALVE DISEASE; ARTICLE; CHILD; CONTROLLED STUDY; DISEASE CLASSIFICATION; DISEASE COURSE; DISEASE SEVERITY; ECHOCARDIOGRAPHY; ENZYME REPLACEMENT; FEMALE; HEART DISEASE; HEART LEFT VENTRICLE HYPERTROPHY; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN; HUNTER SYNDROME; HURLER SYNDROME; INFANT; MAJOR CLINICAL STUDY; MALE; MAROTEAUX LAMY SYNDROME; MITRAL VALVE DISEASE; MORQUIO SYNDROME; ONSET AGE; SANFILIPPO SYNDROME; SCORING SYSTEM; ADULT; COMPARATIVE STUDY; DOPPLER ECHOCARDIOGRAPHY; ECHOGRAPHY; FOLLOW UP; METHODOLOGY; MIDDLE AGED; MUCOPOLYSACCHARIDOSIS; PRESCHOOL CHILD; RETROSPECTIVE STUDY; TIME; TREATMENT OUTCOME;

ADOLESCENT; ADULT; CHILD; CHILD, PRESCHOOL; ECHOCARDIOGRAPHY, DOPPLER; FEMALE; FOLLOW-UP STUDIES; HEART DISEASES; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; INFANT; MALE; MIDDLE AGED; MUCOPOLYSACCHARIDOSES; RETROSPECTIVE STUDIES; TIME FACTORS; TREATMENT OUTCOME; YOUNG ADULT;

EID: 66149099295     PISSN: 10479511     EISSN: 14671107     Source Type: Journal    
DOI: 10.1017/S1047951109003576     Document Type: Article

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