A genetic intervention stands a skip away from clinical tests

Science

Volumn 338, Issue 6113, 2012, Pages 1431-1432

  Chamberlain, Jeffrey S ^a  

^a UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ANTISENSE OLIGONUCLEOTIDE; DANTROLENE; DYSTROPHIN; MESSENGER RNA PRECURSOR; RYANODINE RECEPTOR; CALCIUM CHANNEL BLOCKING AGENT; CENTRAL MUSCLE RELAXANT; RNA PRECURSOR;

DISEASE SEVERITY; DRUG; GENETIC ANALYSIS; MUSCLE; PROTEIN; RODENT;

ANTISENSE THERAPY; CALCIUM SIGNALING; CLINICAL TRIAL (TOPIC); DISEASE SEVERITY; DRUG SCREENING; DUCHENNE MUSCULAR DYSTROPHY; EXON SKIPPING; GENE MUTATION; GENETIC ASSOCIATION; GENETIC CODE; HUMAN; IMMUNOFLUORESCENCE; NONHUMAN; PHASE 2 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; PROTEIN SYNTHESIS; RNA SPLICING; SHORT SURVEY; UPREGULATION; ANIMAL; ARTICLE; BIOSYNTHESIS; DISEASE MODEL; EXON; GENE DELETION; GENETICS; METABOLISM; MOUSE;

ANIMALS; CALCIUM CHANNEL BLOCKERS; CLINICAL TRIALS AS TOPIC; DANTROLENE; DISEASE MODELS, ANIMAL; DYSTROPHIN; EXONS; MICE; MUSCLE RELAXANTS, CENTRAL; MUSCULAR DYSTROPHY, DUCHENNE; OLIGONUCLEOTIDES, ANTISENSE; RNA PRECURSORS; RYANODINE RECEPTOR CALCIUM RELEASE CHANNEL; SEQUENCE DELETION;

EID: 84871033293     PISSN: 00368075     EISSN: 10959203     Source Type: Journal    
DOI: 10.1126/science.1233074     Document Type: Short Survey

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