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Volumn 23, Issue 4, 2011, Pages 337-339

Gene therapy for retinal dystrophies: Twenty years in the making

Author keywords

[No Author keywords available]

Indexed keywords

LENTIVIRUS VECTOR; PARVOVIRUS VECTOR;

EID: 84860109511     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2012.2506     Document Type: Note
Times cited : (8)

References (15)
  • 5
    • 0035182556 scopus 로고    scopus 로고
    • In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector; efficient long-term transduction of cornealendothelium and retinal pigment epithelium
    • DOI 10.1038/sj.gt.3301574
    • Bainbridge, J. W., Stephens, C., Parsley, K., et al. (2001). In vivo gene transfer to the mouse eye using an HIV-based lentiviral vector: Efficient long-term transduction of corneal endothelium and retinal pigment epithelium. Gene Ther. 8, 1665-1668. (Pubitemid 33085588)
    • (2001) Gene Therapy , vol.8 , Issue.21 , pp. 1665-1668
    • Bainbridge, J.W.B.1    Stephens, C.2    Parsley, K.3    Demaison, C.4    Halfyard, A.5    Thrasher, A.J.6    Ali, R.R.7
  • 8
    • 84860198103 scopus 로고    scopus 로고
    • Dextran and protamine-based solid lipid nanoparticles as potential vectors for the treatment of X-linked juvenile retinoschisis
    • (this issue)
    • Delgado, D., Del Pozo-Rodríguez, A., Solinís, M. A., et al. (2012). Dextran and protamine-based solid lipid nanoparticles as potential vectors for the treatment of X-linked juvenile retinoschisis. Hum. Gene Ther. (this issue).
    • (2012) Hum. Gene Ther.
    • Delgado, D.1    Del Pozo-Rodríguez, A.2    Solinís, M.A.3
  • 9
    • 84879275641 scopus 로고    scopus 로고
    • Gene therapy for retinitis pigmentosa caused by MFRP mutations: Human phenotype and preliminary proof of concept
    • (this issue)
    • Dinculescu, A., Estreicher, J., Zenteno, J. C., et al. (2012). Gene therapy for retinitis pigmentosa caused by MFRP mutations: Human phenotype and preliminary proof of concept. Hum. Gene Ther. (this issue).
    • (2012) Hum. Gene Ther.
    • Dinculescu, A.1    Estreicher, J.2    Zenteno, J.C.3
  • 10
    • 54949104686 scopus 로고    scopus 로고
    • Phase i trial of Leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: Short-term results
    • Hauswirth, W., Aleman, T. S., Kaushal, S., et al. (2008). Phase I trial of Leber congenital amaurosis due to RPE65 mutations by ocular subretinal injection of adeno-associated virus gene vector: Short-term results. Hum. Gene Ther. 19, 979-990.
    • (2008) Hum. Gene Ther. , vol.19 , pp. 979-990
    • Hauswirth, W.1    Aleman, T.S.2    Kaushal, S.3
  • 13
    • 84860198102 scopus 로고    scopus 로고
    • Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice
    • (this issue)
    • Mao, H., Gorbatyuk, M. S., Rossmiller, B., et al. (2012). Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice. Hum. Gene Ther. (this issue).
    • (2012) Hum. Gene Ther.
    • Mao, H.1    Gorbatyuk, M.S.2    Rossmiller, B.3
  • 14
    • 79953314650 scopus 로고    scopus 로고
    • Suppression and replacement gene therapy for autosomal dominant disease in a murine model of dominant retinitis pigmentosa
    • Millington-Ward, S., Chadderton, N., O'Reilly, M., et al. (2011). Suppression and replacement gene therapy for autosomal dominant disease in a murine model of dominant retinitis pigmentosa. Mol Ther 19, 642-649.
    • (2011) Mol Ther , vol.19 , pp. 642-649
    • Millington-Ward, S.1    Chadderton, N.2    O'Reilly, M.3
  • 15
    • 84856974535 scopus 로고    scopus 로고
    • Gene supplementation therapy for recessive forms of inherited retinal dystrophies
    • Smith, A. J., Bainbridge, J. W., and Ali, R. R. (2012). Gene supplementation therapy for recessive forms of inherited retinal dystrophies. Gene Ther. 19, 154-161.
    • (2012) Gene Ther. , vol.19 , pp. 154-161
    • Smith, A.J.1    Bainbridge, J.W.2    Ali, R.R.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.